KR102502091B9 - β-사르코글리칸 및 마이크로RNA-29의 아데노-관련 바이러스 벡터 전달 및 근이영양증의 처리 - Google Patents

β-사르코글리칸 및 마이크로RNA-29의 아데노-관련 바이러스 벡터 전달 및 근이영양증의 처리

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KR102502091B9
KR102502091B9 KR1020187032688A KR20187032688A KR102502091B9 KR 102502091 B9 KR102502091 B9 KR 102502091B9 KR 1020187032688 A KR1020187032688 A KR 1020187032688A KR 20187032688 A KR20187032688 A KR 20187032688A KR 102502091 B9 KR102502091 B9 KR 102502091B9
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sarcoglycan
microrna
adeno
treatment
viral vector
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KR1020187032688A
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KR20180137511A (ko
KR102502091B1 (ko
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루이스 로디노-클라파크
제리 알. 멘델
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더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈
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KR1020187032688A 2016-04-15 2017-06-20 β-사르코글리칸 및 마이크로RNA-29의 아데노-관련 바이러스 벡터 전달 및 근이영양증의 처리 KR102502091B1 (ko)

Applications Claiming Priority (5)

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US201662323333P 2016-04-15 2016-04-15
US62/323,333 2016-04-15
US201662433548P 2016-12-13 2016-12-13
US62/433,548 2016-12-13
PCT/US2017/027583 WO2017180976A1 (en) 2016-04-15 2017-04-14 Adeno-associated virus vector delivery of b-sarcoglycan and microrna-29 and the treatment of muscular dystrophy

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KR20180137511A KR20180137511A (ko) 2018-12-27
KR102502091B1 KR102502091B1 (ko) 2023-02-20
KR102502091B9 true KR102502091B9 (ko) 2023-04-17

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US (2) US11358993B2 (ko)
EP (1) EP3442600B1 (ko)
JP (2) JP7079733B2 (ko)
KR (1) KR102502091B1 (ko)
CN (2) CN117384964A (ko)
AU (2) AU2017250756B2 (ko)
BR (1) BR112018071167A2 (ko)
CA (1) CA3021057A1 (ko)
CO (1) CO2018012082A2 (ko)
IL (1) IL262262B2 (ko)
MA (1) MA44681A (ko)
MX (2) MX2018012605A (ko)
MY (1) MY195439A (ko)
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