JPWO2022094180A5 - - Google Patents

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Publication number
JPWO2022094180A5
JPWO2022094180A5 JP2023526506A JP2023526506A JPWO2022094180A5 JP WO2022094180 A5 JPWO2022094180 A5 JP WO2022094180A5 JP 2023526506 A JP2023526506 A JP 2023526506A JP 2023526506 A JP2023526506 A JP 2023526506A JP WO2022094180 A5 JPWO2022094180 A5 JP WO2022094180A5
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JP
Japan
Prior art keywords
seq
capsid
deamidated
nucleic acid
acid sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023526506A
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English (en)
Japanese (ja)
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JP2023550581A5 (https=
JP2023550581A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/057201 external-priority patent/WO2022094180A1/en
Publication of JP2023550581A publication Critical patent/JP2023550581A/ja
Publication of JPWO2022094180A5 publication Critical patent/JPWO2022094180A5/ja
Publication of JP2023550581A5 publication Critical patent/JP2023550581A5/ja
Withdrawn legal-status Critical Current

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JP2023526506A 2020-10-29 2021-10-29 Aavカプシド及びそれを含有する組成物 Withdrawn JP2023550581A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063107030P 2020-10-29 2020-10-29
US63/107,030 2020-10-29
US202163214530P 2021-06-24 2021-06-24
US63/214,530 2021-06-24
PCT/US2021/057201 WO2022094180A1 (en) 2020-10-29 2021-10-29 Aav capsids and compositions containing same

Publications (3)

Publication Number Publication Date
JP2023550581A JP2023550581A (ja) 2023-12-04
JPWO2022094180A5 true JPWO2022094180A5 (https=) 2024-11-07
JP2023550581A5 JP2023550581A5 (https=) 2024-11-07

Family

ID=78851102

Family Applications (1)

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JP2023526506A Withdrawn JP2023550581A (ja) 2020-10-29 2021-10-29 Aavカプシド及びそれを含有する組成物

Country Status (9)

Country Link
US (1) US20230407333A1 (https=)
EP (1) EP4236975A1 (https=)
JP (1) JP2023550581A (https=)
CN (1) CN117042787A (https=)
AU (1) AU2021369793A1 (https=)
CA (1) CA3196499A1 (https=)
MX (1) MX2023005113A (https=)
TW (1) TW202233844A (https=)
WO (1) WO2022094180A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20240376496A1 (en) * 2021-09-03 2024-11-14 Biomarin Pharmaceutical Inc. Aav capsid compositions and methods for delivery
WO2023220476A2 (en) * 2022-05-13 2023-11-16 The Broad Institute, Inc. Adeno-associated viral vectors and uses thereof
WO2024015966A2 (en) * 2022-07-15 2024-01-18 The Trustees Of The University Of Pennsylvania Recombinant aav having aav clade d and clade e capsids and compositions containing same
WO2024077089A2 (en) * 2022-10-04 2024-04-11 Siren Biotechnology, Inc. Modified cpg dinucleotides for recombinant viral vector production
WO2025212884A1 (en) * 2024-04-05 2025-10-09 University Of Massachusetts Discovery of novel aav capsid proteins through directed evolution of the vp1u region

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