JPWO2022017363A5 - - Google Patents

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Publication number
JPWO2022017363A5
JPWO2022017363A5 JP2023512465A JP2023512465A JPWO2022017363A5 JP WO2022017363 A5 JPWO2022017363 A5 JP WO2022017363A5 JP 2023512465 A JP2023512465 A JP 2023512465A JP 2023512465 A JP2023512465 A JP 2023512465A JP WO2022017363 A5 JPWO2022017363 A5 JP WO2022017363A5
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JP
Japan
Prior art keywords
seq
sequence
rpe65
promoter
coding sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023512465A
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English (en)
Japanese (ja)
Other versions
JP2023535232A (ja
JP2023535232A5 (https=
Publication date
Priority claimed from CN202010704946.1A external-priority patent/CN113952471A/zh
Application filed filed Critical
Priority claimed from PCT/CN2021/107284 external-priority patent/WO2022017363A1/en
Publication of JP2023535232A publication Critical patent/JP2023535232A/ja
Publication of JPWO2022017363A5 publication Critical patent/JPWO2022017363A5/ja
Publication of JP2023535232A5 publication Critical patent/JP2023535232A5/ja
Withdrawn legal-status Critical Current

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JP2023512465A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Withdrawn JP2023535232A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
CN202010704946.1 2020-07-21
CN202010704946.1A CN113952471A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
CN202110378979.6 2021-04-08
CN202110378979 2021-04-08
PCT/CN2021/107284 WO2022017363A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of ocular diseases

Publications (3)

Publication Number Publication Date
JP2023535232A JP2023535232A (ja) 2023-08-16
JPWO2022017363A5 true JPWO2022017363A5 (https=) 2024-07-26
JP2023535232A5 JP2023535232A5 (https=) 2024-07-26

Family

ID=79728991

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512465A Withdrawn JP2023535232A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230321280A1 (https=)
EP (1) EP4185335A1 (https=)
JP (1) JP2023535232A (https=)
CN (1) CN116368228A (https=)
AU (1) AU2021314400A1 (https=)
CA (1) CA3186818A1 (https=)
WO (1) WO2022017363A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2023187822A1 (en) * 2022-03-28 2023-10-05 Indian Institute Of Technology Kanpur A system for an ocular gene therapy and a process for preparing thereof
WO2024077089A2 (en) * 2022-10-04 2024-04-11 Siren Biotechnology, Inc. Modified cpg dinucleotides for recombinant viral vector production

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB201502137D0 (en) * 2015-02-09 2015-03-25 Ucl Business Plc Treatment
US20180161405A1 (en) * 2015-06-04 2018-06-14 INSERM (Institut National de la Santé et de la Recherche Médicale) Improved methods for treating ocular diseases by gene therapy
KR20200036912A (ko) * 2017-07-31 2020-04-07 리플렉션 바이오테크놀러지스 리미티드 안과 질환을 위한 세포 모델 및 치료요법
CN111118017B (zh) * 2018-11-01 2023-10-03 上海朗昇生物科技有限公司 治疗Leber先天性黑蒙症的载体及其应用

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