JPWO2022018518A5 - - Google Patents

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Publication number
JPWO2022018518A5
JPWO2022018518A5 JP2023512665A JP2023512665A JPWO2022018518A5 JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5 JP 2023512665 A JP2023512665 A JP 2023512665A JP 2023512665 A JP2023512665 A JP 2023512665A JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5
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JP
Japan
Prior art keywords
sequence
promoter
seq
aav
identity
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Pending
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JP2023512665A
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English (en)
Japanese (ja)
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JP2023542279A (ja
JP2023542279A5 (https=
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Priority claimed from CN202010705069.XA external-priority patent/CN113952472A/zh
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Publication of JP2023542279A publication Critical patent/JP2023542279A/ja
Publication of JPWO2022018518A5 publication Critical patent/JPWO2022018518A5/ja
Publication of JP2023542279A5 publication Critical patent/JP2023542279A5/ja
Pending legal-status Critical Current

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JP2023512665A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Pending JP2023542279A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
CN202010705069.XA CN113952472A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
PCT/IB2021/000509 WO2022018518A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of eye diseases

Publications (3)

Publication Number Publication Date
JP2023542279A JP2023542279A (ja) 2023-10-06
JPWO2022018518A5 true JPWO2022018518A5 (https=) 2024-07-26
JP2023542279A5 JP2023542279A5 (https=) 2024-07-26

Family

ID=79459955

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512665A Pending JP2023542279A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230321281A1 (https=)
EP (1) EP4185319A4 (https=)
JP (1) JP2023542279A (https=)
CN (2) CN113952472A (https=)
AU (1) AU2021312379A1 (https=)
CA (1) CA3186826A1 (https=)
WO (1) WO2022018518A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11345930B2 (en) * 2020-09-02 2022-05-31 4D Molecular Therapeutics Inc. Codon optimized RPGRORF15 genes and uses thereof

Family Cites Families (14)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA2507036A1 (en) * 2002-12-02 2004-06-17 Genvec, Inc. Materials and methods for treating ocular-related disorders
EP2872183B1 (en) * 2012-07-11 2018-09-26 The Trustees Of The University Of Pennsylvania Aav-mediated gene therapy for rpgr x-linked retinal degeneration
JP5971661B2 (ja) * 2012-09-19 2016-08-17 国立大学法人 東京大学 神経活動依存的プロモータ活性を有するdna、及びこれを含むベクター
EP3030665B9 (en) * 2013-08-05 2023-10-04 Academisch Ziekenhuis Leiden H.O.D.N. Leids Universitair Medisch Centrum Recombinant aav-crumbs homologue composition and methods for treating lca-8 and progressive rp
AU2014359136B2 (en) * 2013-12-06 2020-06-25 Centre Hospitalier Universitaire De Montpellier Methods and pharmaceutical compositions for expressing a polynucleotide of interest in the retinal pigment epithelium of a subject
CA2945965C (en) 2014-04-15 2022-11-01 Applied Genetic Technologies Corporation Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (rpgr)
IL248102B (en) * 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
US20160346359A1 (en) * 2015-05-01 2016-12-01 Spark Therapeutics, Inc. Adeno-associated Virus-Mediated CRISPR-Cas9 Treatment of Ocular Disease
GB201516066D0 (en) * 2015-09-10 2015-10-28 Young & Co Llp D Treatment of retinitis pigmentosa
EP3827812B1 (en) * 2016-07-29 2025-10-29 The Regents of the University of California Adeno-associated virus virions with variant capsid and methods of use thereof
WO2019006182A1 (en) * 2017-06-30 2019-01-03 The Regents Of The University Of California VIRIONS OF ADENO-ASSOCIATED VIRUSES OF CAPSID VARIANTS AND METHODS OF USE THEREOF
MX2020007876A (es) * 2018-01-31 2020-12-03 Res Inst Nationwide Childrens Hospital Terapia genica para la distrofia muscular de cinturas tipo 2c.
TW202028225A (zh) * 2018-09-21 2020-08-01 英商夜星克有限公司 用於治療色素性視網膜炎之組合物及方法
EP4087617A4 (en) * 2020-01-10 2024-05-01 Solid Biosciences Inc. VIRAL VECTOR FOR COMBINATION THERAPY

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