JPWO2022010834A5 - - Google Patents

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Publication number
JPWO2022010834A5
JPWO2022010834A5 JP2023501075A JP2023501075A JPWO2022010834A5 JP WO2022010834 A5 JPWO2022010834 A5 JP WO2022010834A5 JP 2023501075 A JP2023501075 A JP 2023501075A JP 2023501075 A JP2023501075 A JP 2023501075A JP WO2022010834 A5 JPWO2022010834 A5 JP WO2022010834A5
Authority
JP
Japan
Prior art keywords
seq
pharmaceutical composition
polypeptide
dworf
raav virion
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023501075A
Other languages
English (en)
Japanese (ja)
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JP2023534647A5 (https=
JP2023534647A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/040428 external-priority patent/WO2022010834A1/en
Publication of JP2023534647A publication Critical patent/JP2023534647A/ja
Publication of JP2023534647A5 publication Critical patent/JP2023534647A5/ja
Publication of JPWO2022010834A5 publication Critical patent/JPWO2022010834A5/ja
Pending legal-status Critical Current

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JP2023501075A 2020-07-07 2021-07-06 Dwarfオープンリーディングフレームのためのアデノ随伴ウイルスベクター Pending JP2023534647A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063048743P 2020-07-07 2020-07-07
US63/048,743 2020-07-07
PCT/US2021/040428 WO2022010834A1 (en) 2020-07-07 2021-07-06 Adeno-associated virus vector for dwarf open reading frame

Publications (3)

Publication Number Publication Date
JP2023534647A JP2023534647A (ja) 2023-08-10
JP2023534647A5 JP2023534647A5 (https=) 2024-07-10
JPWO2022010834A5 true JPWO2022010834A5 (https=) 2024-07-10

Family

ID=79552029

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023501075A Pending JP2023534647A (ja) 2020-07-07 2021-07-06 Dwarfオープンリーディングフレームのためのアデノ随伴ウイルスベクター

Country Status (11)

Country Link
US (1) US20230241249A1 (https=)
EP (1) EP4179083A4 (https=)
JP (1) JP2023534647A (https=)
KR (1) KR20230035584A (https=)
CN (1) CN115885043A (https=)
AU (1) AU2021306697A1 (https=)
BR (1) BR112022026997A2 (https=)
CA (1) CA3183844A1 (https=)
IL (1) IL299638A (https=)
MX (1) MX2023000318A (https=)
WO (1) WO2022010834A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2021142267A1 (en) 2020-01-08 2021-07-15 Scarpmap Llc Methods and computing system for processing ultrasound image to determine health of subdermal tissue
AU2022307365A1 (en) 2021-07-08 2024-02-01 Tenaya Therapeutics, Inc. Optimized expression cassettes for gene therapy

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN1856576B (zh) * 2003-09-30 2011-05-04 宾夕法尼亚州立大学托管会 腺伴随病毒(aav)进化支、序列、含有这些序列的载体及它们的应用
US10570183B2 (en) * 2016-04-19 2020-02-25 The Board Of Regents Of The University Of Texas System Use of a small native peptide activator of SERCA pump for treatment of heart failure and other disorders characterized by cytosolic calcium overload
WO2018026766A1 (en) * 2016-08-01 2018-02-08 The Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College Compositions and methods for treating cardiac injury
US20190382732A1 (en) * 2017-02-24 2019-12-19 The Board Of Regents Of The University Of Texas System Compositions and methods relating to myomixer-promoted muscle cell fusion
US20180326022A1 (en) * 2017-04-21 2018-11-15 The Trustees Of The University Of Pennsylvania Compositions and methods for improving heart function and treating heart failure
IL297391A (en) * 2020-04-20 2022-12-01 Tenaya Therapeutics Inc An adeno-associated virus with an engineered capsid

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