JPWO2023108129A5 - - Google Patents

Info

Publication number
JPWO2023108129A5
JPWO2023108129A5 JP2024534532A JP2024534532A JPWO2023108129A5 JP WO2023108129 A5 JPWO2023108129 A5 JP WO2023108129A5 JP 2024534532 A JP2024534532 A JP 2024534532A JP 2024534532 A JP2024534532 A JP 2024534532A JP WO2023108129 A5 JPWO2023108129 A5 JP WO2023108129A5
Authority
JP
Japan
Prior art keywords
vector
tnnc1
polynucleotide
promoter
pharmaceutical composition
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024534532A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024545507A5 (https=
JP2024545507A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081282 external-priority patent/WO2023108129A1/en
Publication of JP2024545507A publication Critical patent/JP2024545507A/ja
Publication of JP2024545507A5 publication Critical patent/JP2024545507A5/ja
Publication of JPWO2023108129A5 publication Critical patent/JPWO2023108129A5/ja
Pending legal-status Critical Current

Links

JP2024534532A 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療 Pending JP2024545507A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163288255P 2021-12-10 2021-12-10
US63/288,255 2021-12-10
PCT/US2022/081282 WO2023108129A1 (en) 2021-12-10 2022-12-09 Troponin c (tnnc1) gene therapy using aav vector

Publications (3)

Publication Number Publication Date
JP2024545507A JP2024545507A (ja) 2024-12-09
JP2024545507A5 JP2024545507A5 (https=) 2025-10-29
JPWO2023108129A5 true JPWO2023108129A5 (https=) 2025-10-29

Family

ID=86731323

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024534532A Pending JP2024545507A (ja) 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療

Country Status (6)

Country Link
US (1) US20240335566A1 (https=)
EP (1) EP4444893A4 (https=)
JP (1) JP2024545507A (https=)
CN (1) CN118613591A (https=)
CA (1) CA3240616A1 (https=)
WO (1) WO2023108129A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3021572A1 (en) 2016-04-20 2017-10-26 Centro De Investigaciones Energeticas, Medioambientales Y Tecnologicas Compositions and methods for enhanced gene expression of pklr
EP3697452A4 (en) 2017-10-16 2021-11-24 Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, O.A., M.P. LENTIVIRAL VECTORS FOR ADMINISTRATION OF PKLR TO TREAT PYRUVATE KINASE DEFECTS
BR112020020841A2 (pt) 2018-04-11 2021-01-19 Fundacion Para La Investigacion Biomedica Del Hospital Infantil Universitario Nino Jesus Composições e métodos para transplante de célulastronco

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP5553547B2 (ja) * 2009-07-14 2014-07-16 俊一 梶岡 トロポニン含有医薬組成物
AU2012258525B2 (en) * 2011-05-26 2017-02-23 University Of Washington Cell and gene based methods to improve cardiac function
EP2792742A1 (en) * 2013-04-17 2014-10-22 Universitätsklinikum Hamburg-Eppendorf (UKE) Gene-therapy vectors for treating cardiomyopathy
CA3057899A1 (en) * 2017-03-27 2018-10-04 Vrije Universiteit Brussel Diaphragm-specific nucleic acid regulatory elements and methods and use thereof
CN114450411A (zh) * 2019-04-01 2022-05-06 特纳亚治疗股份有限公司 具有工程化衣壳的腺相关病毒
AR126660A1 (es) * 2021-07-28 2023-11-01 Univ Brussel Vrije Mejorando la eficacia de la terapia génica dirigida a músculos

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