KR20230035584A - Dwarf 개방 판독 프레임을 위한 아데노-관련 바이러스 벡터 - Google Patents

Dwarf 개방 판독 프레임을 위한 아데노-관련 바이러스 벡터 Download PDF

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KR20230035584A
KR20230035584A KR1020237001979A KR20237001979A KR20230035584A KR 20230035584 A KR20230035584 A KR 20230035584A KR 1020237001979 A KR1020237001979 A KR 1020237001979A KR 20237001979 A KR20237001979 A KR 20237001979A KR 20230035584 A KR20230035584 A KR 20230035584A
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seq
dworf
polypeptide
raav
promoter
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에릭 엔. 올슨
론다 에스. 바셀-두비
벤자민 알. 넬슨
캐서린 에이. 마카레위치
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더 보드 오브 리젠츠 오브 더 유니버시티 오브 텍사스 시스템
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KR1020237001979A 2020-07-07 2021-07-06 Dwarf 개방 판독 프레임을 위한 아데노-관련 바이러스 벡터 Withdrawn KR20230035584A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063048743P 2020-07-07 2020-07-07
US63/048,743 2020-07-07
PCT/US2021/040428 WO2022010834A1 (en) 2020-07-07 2021-07-06 Adeno-associated virus vector for dwarf open reading frame

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KR20230035584A true KR20230035584A (ko) 2023-03-14

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KR1020237001979A Withdrawn KR20230035584A (ko) 2020-07-07 2021-07-06 Dwarf 개방 판독 프레임을 위한 아데노-관련 바이러스 벡터

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US (1) US20230241249A1 (https=)
EP (1) EP4179083A4 (https=)
JP (1) JP2023534647A (https=)
KR (1) KR20230035584A (https=)
CN (1) CN115885043A (https=)
AU (1) AU2021306697A1 (https=)
BR (1) BR112022026997A2 (https=)
CA (1) CA3183844A1 (https=)
IL (1) IL299638A (https=)
MX (1) MX2023000318A (https=)
WO (1) WO2022010834A1 (https=)

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WO2021142267A1 (en) 2020-01-08 2021-07-15 Scarpmap Llc Methods and computing system for processing ultrasound image to determine health of subdermal tissue
AU2022307365A1 (en) 2021-07-08 2024-02-01 Tenaya Therapeutics, Inc. Optimized expression cassettes for gene therapy

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CN1856576B (zh) * 2003-09-30 2011-05-04 宾夕法尼亚州立大学托管会 腺伴随病毒(aav)进化支、序列、含有这些序列的载体及它们的应用
US10570183B2 (en) * 2016-04-19 2020-02-25 The Board Of Regents Of The University Of Texas System Use of a small native peptide activator of SERCA pump for treatment of heart failure and other disorders characterized by cytosolic calcium overload
WO2018026766A1 (en) * 2016-08-01 2018-02-08 The Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College Compositions and methods for treating cardiac injury
US20190382732A1 (en) * 2017-02-24 2019-12-19 The Board Of Regents Of The University Of Texas System Compositions and methods relating to myomixer-promoted muscle cell fusion
US20180326022A1 (en) * 2017-04-21 2018-11-15 The Trustees Of The University Of Pennsylvania Compositions and methods for improving heart function and treating heart failure
IL297391A (en) * 2020-04-20 2022-12-01 Tenaya Therapeutics Inc An adeno-associated virus with an engineered capsid

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BR112022026997A2 (pt) 2023-03-07
CA3183844A1 (en) 2022-01-13
AU2021306697A1 (en) 2023-02-09
US20230241249A1 (en) 2023-08-03
EP4179083A1 (en) 2023-05-17
IL299638A (en) 2023-03-01
EP4179083A4 (en) 2024-08-28
JP2023534647A (ja) 2023-08-10
MX2023000318A (es) 2023-02-09
CN115885043A (zh) 2023-03-31
WO2022010834A1 (en) 2022-01-13

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