JPWO2021174036A5 - - Google Patents
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- Publication number
- JPWO2021174036A5 JPWO2021174036A5 JP2022551593A JP2022551593A JPWO2021174036A5 JP WO2021174036 A5 JPWO2021174036 A5 JP WO2021174036A5 JP 2022551593 A JP2022551593 A JP 2022551593A JP 2022551593 A JP2022551593 A JP 2022551593A JP WO2021174036 A5 JPWO2021174036 A5 JP WO2021174036A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- modified
- optionally
- internucleoside linkage
- sugar moiety
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202062983555P | 2020-02-28 | 2020-02-28 | |
| US62/983,555 | 2020-02-28 | ||
| US202063085111P | 2020-09-29 | 2020-09-29 | |
| US63/085,111 | 2020-09-29 | ||
| PCT/US2021/019960 WO2021174036A1 (en) | 2020-02-28 | 2021-02-26 | Compounds and methods for modulating scn1a expression |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023515974A JP2023515974A (ja) | 2023-04-17 |
| JP2023515974A5 JP2023515974A5 (https=) | 2024-03-05 |
| JPWO2021174036A5 true JPWO2021174036A5 (https=) | 2024-03-05 |
Family
ID=77491960
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022551593A Pending JP2023515974A (ja) | 2020-02-28 | 2021-02-26 | Ｓｃｎ１ａ発現を調節するための化合物及び方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20230043648A1 (https=) |
| EP (1) | EP4110919A4 (https=) |
| JP (1) | JP2023515974A (https=) |
| TW (1) | TW202140788A (https=) |
| UY (1) | UY39104A (https=) |
| WO (1) | WO2021174036A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP7507093B2 (ja) * | 2018-03-21 | 2024-06-27 | リジェネロン・ファーマシューティカルズ・インコーポレイテッド | １７β－水酸化ステロイド脱水素酵素１３型（ＨＳＤ１７Ｂ１３）ｉＲＮＡ組成物およびその使用方法 |
| EP4392562A4 (en) * | 2021-08-27 | 2025-09-24 | Ionis Pharmaceuticals Inc | COMPOUNDS AND METHODS FOR MODULATING SCN1A EXPRESSION |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP6453212B2 (ja) * | 2012-07-13 | 2019-01-16 | ウェイブ ライフ サイエンシズ リミテッドＷａｖｅ Ｌｉｆｅ Ｓｃｉｅｎｃｅｓ Ｌｔｄ． | キラル制御 |
| ES2935658T3 (es) * | 2016-07-15 | 2023-03-09 | Ionis Pharmaceuticals Inc | Compuestos y métodos para la modulación de SMN2 |
| SG11202001590RA (en) * | 2017-08-25 | 2020-03-30 | Stoke Therapeutics Inc | Antisense oligomers for treatment of conditions and diseases |
| US10758629B2 (en) * | 2018-05-29 | 2020-09-01 | Sarepta Therapeutics, Inc. | Exon skipping oligomer conjugates for muscular dystrophy |
| BR112021003224A2 (pt) * | 2018-08-20 | 2021-07-20 | Rogcon, Inc. | oligonucleotídeos antissentido direcionados a scn2a para o tratamento de encefalopatias por scn1a |
| BR112022010882A2 (pt) * | 2019-12-06 | 2022-10-04 | Stoke Therapeutics Inc | Oligômeros antissenso para tratamento de condições e doenças |
-
2021
- 2021-02-26 WO PCT/US2021/019960 patent/WO2021174036A1/en not_active Ceased
- 2021-02-26 TW TW110107122A patent/TW202140788A/zh unknown
- 2021-02-26 EP EP21760424.8A patent/EP4110919A4/en active Pending
- 2021-02-26 US US17/802,324 patent/US20230043648A1/en active Pending
- 2021-02-26 JP JP2022551593A patent/JP2023515974A/ja active Pending
- 2021-03-01 UY UY0001039104A patent/UY39104A/es unknown
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