JPWO2020218419A5 - - Google Patents

Download PDF

Info

Publication number
JPWO2020218419A5
JPWO2020218419A5 JP2021516202A JP2021516202A JPWO2020218419A5 JP WO2020218419 A5 JPWO2020218419 A5 JP WO2020218419A5 JP 2021516202 A JP2021516202 A JP 2021516202A JP 2021516202 A JP2021516202 A JP 2021516202A JP WO2020218419 A5 JPWO2020218419 A5 JP WO2020218419A5
Authority
JP
Japan
Prior art keywords
seq
amino acid
peptide
acid sequence
aav
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2021516202A
Other languages
English (en)
Japanese (ja)
Other versions
JP7524166B2 (ja
JPWO2020218419A1 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/JP2020/017495 external-priority patent/WO2020218419A1/ja
Publication of JPWO2020218419A1 publication Critical patent/JPWO2020218419A1/ja
Publication of JPWO2020218419A5 publication Critical patent/JPWO2020218419A5/ja
Application granted granted Critical
Publication of JP7524166B2 publication Critical patent/JP7524166B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2021516202A 2019-04-24 2020-04-23 脳に指向性を有するaav変異体 Active JP7524166B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
JP2019082417 2019-04-24
JP2019082417 2019-04-24
PCT/JP2020/017495 WO2020218419A1 (ja) 2019-04-24 2020-04-23 脳に指向性を有するaav変異体

Publications (3)

Publication Number Publication Date
JPWO2020218419A1 JPWO2020218419A1 (https=) 2020-10-29
JPWO2020218419A5 true JPWO2020218419A5 (https=) 2023-01-05
JP7524166B2 JP7524166B2 (ja) 2024-07-29

Family

ID=72942142

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021516202A Active JP7524166B2 (ja) 2019-04-24 2020-04-23 脳に指向性を有するaav変異体

Country Status (10)

Country Link
US (1) US12421526B2 (https=)
EP (1) EP3960755A4 (https=)
JP (1) JP7524166B2 (https=)
KR (1) KR102917057B1 (https=)
CN (1) CN113748122B (https=)
AU (1) AU2020263757B2 (https=)
BR (1) BR112021017603A2 (https=)
CA (1) CA3132447A1 (https=)
IL (1) IL286212A (https=)
WO (1) WO2020218419A1 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3575398A4 (en) * 2017-01-30 2020-11-11 Nippon Medical School Foundation ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT
CN115960177B (zh) * 2022-10-09 2023-07-07 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN116789739B (zh) * 2022-12-08 2024-01-26 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN116284262B (zh) * 2023-02-13 2026-03-17 和元生物技术(上海)股份有限公司 高效感染ht-22细胞的腺相关病毒突变体
CN116693633B (zh) * 2023-02-21 2023-12-22 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN121569040A (zh) 2023-07-27 2026-02-24 宝生物工程株式会社 脑趋向性aav突变体
CN121816425A (zh) * 2023-09-11 2026-04-07 学校法人顺天堂 能够感染内耳的aav变体

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE19827457C1 (de) * 1998-06-19 2000-03-02 Medigene Ag Strukturprotein von AAV, seine Herstellung und Verwendung
EP2176283B1 (en) 2007-07-14 2016-11-02 University of Iowa Research Foundation Methods and compositions for treating brain diseases
WO2010114143A1 (ja) * 2009-03-30 2010-10-07 国立大学法人岡山大学 特異的プロモーターの活性を上昇させるシステム及び該システムを保持したベクター
CN105755044A (zh) 2011-04-22 2016-07-13 加利福尼亚大学董事会 具有变异衣壳的腺相关病毒病毒体及其使用方法
WO2013014764A1 (ja) 2011-07-27 2013-01-31 三菱電機株式会社 通信システム、通信装置および通信方法
US9938541B2 (en) 2012-12-25 2018-04-10 Takara Bio Inc. AAV variant
HK1222673A1 (zh) 2013-07-12 2017-07-07 The Children's Hospital Of Philadelphia Aav载体和用於抗aav(腺相关病毒)中和抗体的检测
GB201403684D0 (en) 2014-03-03 2014-04-16 King S College London Vector
CA2942289C (en) * 2014-03-10 2024-05-21 Uniqure Ip B.V. Further improved aav vectors produced in insect cells
DE102014207498A1 (de) 2014-04-17 2015-10-22 Universitätsklinikum Hamburg-Eppendorf Viraler Vektor für den zielgerichteten Gentransfer in Gehirn und Rückenmark
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
EP3890017B1 (en) 2018-12-04 2025-08-13 Ningbo Sunny Opotech Co., Ltd. Photosensitive assembly, photographic module, manufacturing method for photographic assembly, and electronic device

Similar Documents

Publication Publication Date Title
JPWO2020218419A5 (https=)
JP2022530633A5 (https=)
JP2022530544A5 (https=)
CN116390934A (zh) 功能性aav衣壳的高通量工程化
JP2023076606A5 (https=)
CN101511373B (zh) 用于基因治疗的修饰的因子ⅷ和因子ⅸ基因和载体
CA2329060A1 (en) Aav5 vector and uses thereof
JP2022078208A5 (https=)
JP2014239686A5 (https=)
JP2020508667A5 (https=)
JP2020505936A5 (https=)
JP2017536116A5 (https=)
JP2003505032A5 (https=)
CN111808175B (zh) 重组腺相关病毒颗粒及其应用
JP2014012022A5 (https=)
JP2003505033A5 (https=)
IL317938A (en) Recombinant viral vectors with altered tropism and their uses for the targeted introduction of genetic material into human cells
JP2020510429A5 (https=)
JP2024051082A5 (https=)
JP2005512569A5 (https=)
JP2011101646A5 (https=)
CA2349838A1 (en) Adeno-associated virus serotype 1 nucleic acid sequences, vectors and host cells containing same
JP2005525086A5 (https=)
JP2023524577A5 (https=)
JP2004513616A5 (https=)