JPWO2020168222A5 - - Google Patents

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Publication number
JPWO2020168222A5
JPWO2020168222A5 JP2021547189A JP2021547189A JPWO2020168222A5 JP WO2020168222 A5 JPWO2020168222 A5 JP WO2020168222A5 JP 2021547189 A JP2021547189 A JP 2021547189A JP 2021547189 A JP2021547189 A JP 2021547189A JP WO2020168222 A5 JPWO2020168222 A5 JP WO2020168222A5
Authority
JP
Japan
Prior art keywords
protein
nucleic acid
dna
acid sequence
rep
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021547189A
Other languages
English (en)
Japanese (ja)
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JP2022520803A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/018332 external-priority patent/WO2020168222A1/en
Publication of JP2022520803A publication Critical patent/JP2022520803A/ja
Publication of JPWO2020168222A5 publication Critical patent/JPWO2020168222A5/ja
Priority to JP2024064717A priority Critical patent/JP2024083567A/ja
Pending legal-status Critical Current

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JP2021547189A 2019-02-15 2020-02-14 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 Pending JP2022520803A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024064717A JP2024083567A (ja) 2019-02-15 2024-04-12 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962806076P 2019-02-15 2019-02-15
US62/806,076 2019-02-15
PCT/US2020/018332 WO2020168222A1 (en) 2019-02-15 2020-02-14 Modulation of rep protein activity in closed-ended dna (cedna) production

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024064717A Division JP2024083567A (ja) 2019-02-15 2024-04-12 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節

Publications (2)

Publication Number Publication Date
JP2022520803A JP2022520803A (ja) 2022-04-01
JPWO2020168222A5 true JPWO2020168222A5 (ru) 2023-02-22

Family

ID=72045641

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021547189A Pending JP2022520803A (ja) 2019-02-15 2020-02-14 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節
JP2024064717A Pending JP2024083567A (ja) 2019-02-15 2024-04-12 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024064717A Pending JP2024083567A (ja) 2019-02-15 2024-04-12 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節

Country Status (11)

Country Link
US (1) US20220127625A1 (ru)
EP (1) EP3924491A4 (ru)
JP (2) JP2022520803A (ru)
KR (1) KR20210127935A (ru)
CN (1) CN113454232A (ru)
AU (1) AU2020221312A1 (ru)
CA (1) CA3129321A1 (ru)
IL (1) IL285415A (ru)
MA (1) MA54958A (ru)
SG (1) SG11202106491VA (ru)
WO (1) WO2020168222A1 (ru)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
TW202112807A (zh) * 2019-06-10 2021-04-01 美商霍蒙拉奇醫藥公司 用於arsa基因轉移之腺相關病毒組成物及其使用方法
EP4189098A1 (en) 2020-07-27 2023-06-07 Anjarium Biosciences AG Compositions of dna molecules, methods of making therefor, and methods of use thereof
EP4267197A1 (en) * 2020-12-23 2023-11-01 Vivet Therapeutics Minimal bile acid inducible promoters for gene therapy
US20240182925A1 (en) * 2021-03-16 2024-06-06 Wisconsin Alumni Research Foundation Insulin gene therapy to treat diabetes
KR20240049821A (ko) * 2021-08-23 2024-04-17 바이오버라티브 테라퓨틱스 인크. 바큘로바이러스 발현 시스템
CN114703203A (zh) * 2022-02-11 2022-07-05 上海渤因生物科技有限公司 杆状病毒载体及其用途

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DK3023500T3 (da) * 2006-06-21 2020-04-20 Uniqure Ip Bv Insektceller til fremstilling af AAV-vektorer
EP2500434A1 (en) * 2011-03-12 2012-09-19 Association Institut de Myologie Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery
MX2016011585A (es) * 2014-03-10 2016-11-29 Uniqure Ip Bv Vectores aav mejorados adicionales producidos en celulas de insecto.
KR102336362B1 (ko) * 2016-03-03 2021-12-08 보이저 테라퓨틱스, 인크. 비-바이러스 유전자 전달을 위한 폐쇄형-말단 선형 듀플렉스 dna
KR20200035130A (ko) * 2017-08-09 2020-04-01 바이오버라티브 테라퓨틱스 인크. 핵산 분자 및 이의 용도

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