JPWO2020168222A5 - - Google Patents
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- Publication number
- JPWO2020168222A5 JPWO2020168222A5 JP2021547189A JP2021547189A JPWO2020168222A5 JP WO2020168222 A5 JPWO2020168222 A5 JP WO2020168222A5 JP 2021547189 A JP2021547189 A JP 2021547189A JP 2021547189 A JP2021547189 A JP 2021547189A JP WO2020168222 A5 JPWO2020168222 A5 JP WO2020168222A5
- Authority
- JP
- Japan
- Prior art keywords
- protein
- nucleic acid
- dna
- acid sequence
- rep
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
JP2024064717A JP2024083567A (ja) | 2019-02-15 | 2024-04-12 | 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 |
Applications Claiming Priority (3)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US201962806076P | 2019-02-15 | 2019-02-15 | |
US62/806,076 | 2019-02-15 | ||
PCT/US2020/018332 WO2020168222A1 (en) | 2019-02-15 | 2020-02-14 | Modulation of rep protein activity in closed-ended dna (cedna) production |
Related Child Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
JP2024064717A Division JP2024083567A (ja) | 2019-02-15 | 2024-04-12 | 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 |
Publications (2)
Publication Number | Publication Date |
---|---|
JP2022520803A JP2022520803A (ja) | 2022-04-01 |
JPWO2020168222A5 true JPWO2020168222A5 (ru) | 2023-02-22 |
Family
ID=72045641
Family Applications (2)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
JP2021547189A Pending JP2022520803A (ja) | 2019-02-15 | 2020-02-14 | 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 |
JP2024064717A Pending JP2024083567A (ja) | 2019-02-15 | 2024-04-12 | 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 |
Family Applications After (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
JP2024064717A Pending JP2024083567A (ja) | 2019-02-15 | 2024-04-12 | 閉端DNA(ceDNA)の産生におけるREPタンパク質活性の調節 |
Country Status (11)
Country | Link |
---|---|
US (1) | US20220127625A1 (ru) |
EP (1) | EP3924491A4 (ru) |
JP (2) | JP2022520803A (ru) |
KR (1) | KR20210127935A (ru) |
CN (1) | CN113454232A (ru) |
AU (1) | AU2020221312A1 (ru) |
CA (1) | CA3129321A1 (ru) |
IL (1) | IL285415A (ru) |
MA (1) | MA54958A (ru) |
SG (1) | SG11202106491VA (ru) |
WO (1) | WO2020168222A1 (ru) |
Families Citing this family (6)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
TW202112807A (zh) * | 2019-06-10 | 2021-04-01 | 美商霍蒙拉奇醫藥公司 | 用於arsa基因轉移之腺相關病毒組成物及其使用方法 |
EP4189098A1 (en) | 2020-07-27 | 2023-06-07 | Anjarium Biosciences AG | Compositions of dna molecules, methods of making therefor, and methods of use thereof |
EP4267197A1 (en) * | 2020-12-23 | 2023-11-01 | Vivet Therapeutics | Minimal bile acid inducible promoters for gene therapy |
US20240182925A1 (en) * | 2021-03-16 | 2024-06-06 | Wisconsin Alumni Research Foundation | Insulin gene therapy to treat diabetes |
KR20240049821A (ko) * | 2021-08-23 | 2024-04-17 | 바이오버라티브 테라퓨틱스 인크. | 바큘로바이러스 발현 시스템 |
CN114703203A (zh) * | 2022-02-11 | 2022-07-05 | 上海渤因生物科技有限公司 | 杆状病毒载体及其用途 |
Family Cites Families (5)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
DK3023500T3 (da) * | 2006-06-21 | 2020-04-20 | Uniqure Ip Bv | Insektceller til fremstilling af AAV-vektorer |
EP2500434A1 (en) * | 2011-03-12 | 2012-09-19 | Association Institut de Myologie | Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery |
MX2016011585A (es) * | 2014-03-10 | 2016-11-29 | Uniqure Ip Bv | Vectores aav mejorados adicionales producidos en celulas de insecto. |
KR102336362B1 (ko) * | 2016-03-03 | 2021-12-08 | 보이저 테라퓨틱스, 인크. | 비-바이러스 유전자 전달을 위한 폐쇄형-말단 선형 듀플렉스 dna |
KR20200035130A (ko) * | 2017-08-09 | 2020-04-01 | 바이오버라티브 테라퓨틱스 인크. | 핵산 분자 및 이의 용도 |
-
2020
- 2020-02-14 JP JP2021547189A patent/JP2022520803A/ja active Pending
- 2020-02-14 SG SG11202106491VA patent/SG11202106491VA/en unknown
- 2020-02-14 AU AU2020221312A patent/AU2020221312A1/en active Pending
- 2020-02-14 EP EP20756257.0A patent/EP3924491A4/en active Pending
- 2020-02-14 CN CN202080014548.5A patent/CN113454232A/zh active Pending
- 2020-02-14 MA MA054958A patent/MA54958A/fr unknown
- 2020-02-14 WO PCT/US2020/018332 patent/WO2020168222A1/en active Search and Examination
- 2020-02-14 KR KR1020217025576A patent/KR20210127935A/ko unknown
- 2020-02-14 CA CA3129321A patent/CA3129321A1/en active Pending
- 2020-02-14 US US17/430,341 patent/US20220127625A1/en active Pending
-
2021
- 2021-08-05 IL IL285415A patent/IL285415A/en unknown
-
2024
- 2024-04-12 JP JP2024064717A patent/JP2024083567A/ja active Pending
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