JPWO2020163337A5 - - Google Patents

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JPWO2020163337A5
JPWO2020163337A5 JP2021545384A JP2021545384A JPWO2020163337A5 JP WO2020163337 A5 JPWO2020163337 A5 JP WO2020163337A5 JP 2021545384 A JP2021545384 A JP 2021545384A JP 2021545384 A JP2021545384 A JP 2021545384A JP WO2020163337 A5 JPWO2020163337 A5 JP WO2020163337A5
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pharmaceutical composition
halogen
alkyl
optionally substituted
syndrome
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JP2021545384A
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JP2022519131A5 (https=
JP7633169B2 (ja
JP2022519131A (ja
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JP2021545384A 2019-02-04 2020-02-04 グルコシルセラミドシンターゼ(gcs)阻害剤を使用した繊毛病の処置 Active JP7633169B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962800993P 2019-02-04 2019-02-04
US62/800,993 2019-02-04
US201962851430P 2019-05-22 2019-05-22
US62/851,430 2019-05-22
PCT/US2020/016588 WO2020163337A1 (en) 2019-02-04 2020-02-04 Treatment of ciliopathies using inhibitors of glucosylceramide synthase (gcs)

Publications (4)

Publication Number Publication Date
JP2022519131A JP2022519131A (ja) 2022-03-18
JP2022519131A5 JP2022519131A5 (https=) 2023-02-10
JPWO2020163337A5 true JPWO2020163337A5 (https=) 2023-02-10
JP7633169B2 JP7633169B2 (ja) 2025-02-19

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JP2021545384A Active JP7633169B2 (ja) 2019-02-04 2020-02-04 グルコシルセラミドシンターゼ(gcs)阻害剤を使用した繊毛病の処置

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US (1) US12527776B2 (https=)
EP (1) EP3920912B1 (https=)
JP (1) JP7633169B2 (https=)
CN (1) CN114040762A (https=)
AU (1) AU2020218185B2 (https=)
ES (1) ES3040555T3 (https=)
HU (1) HUE072626T2 (https=)
PL (1) PL3920912T3 (https=)
PT (1) PT3920912T (https=)
WO (1) WO2020163337A1 (https=)

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CN114040762A (zh) 2019-02-04 2022-02-11 建新公司 使用葡糖神经酰胺合酶(gcs)的抑制剂治疗纤毛疾病
TW202142236A (zh) 2020-02-03 2021-11-16 美商健臻公司 用於治療與溶體儲積症相關的神經症狀之方法
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WO2022169004A1 (ko) * 2021-02-05 2022-08-11 연세대학교 산학협력단 신규한 fabp4 억제제를 유효성분으로 포함하는 섬모형성 촉진용 조성물
EP4201403A1 (en) 2021-12-21 2023-06-28 Som Innovation Biotech, S.L. Compounds tirapazamine and quazinone for use in the treatment of gm2 gangliosidoses
CN115350278A (zh) * 2022-07-11 2022-11-18 清华大学 提高细胞内鞘脂类物质含量的试剂在制备纤毛异常相关疾病药物中的用途
CN120417900A (zh) 2022-12-01 2025-08-01 建新公司 文鲁司他与cyp3a4的强或中度抑制剂的组合
WO2025178019A1 (ja) * 2024-02-19 2025-08-28 国立大学法人大阪大学 繊毛病治療用医薬組成物
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