JPWO2020005974A5 - - Google Patents
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- Publication number
- JPWO2020005974A5 JPWO2020005974A5 JP2020572414A JP2020572414A JPWO2020005974A5 JP WO2020005974 A5 JPWO2020005974 A5 JP WO2020005974A5 JP 2020572414 A JP2020572414 A JP 2020572414A JP 2020572414 A JP2020572414 A JP 2020572414A JP WO2020005974 A5 JPWO2020005974 A5 JP WO2020005974A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- vector
- nucleic acid
- single nucleic
- clrn1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023135405A JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862689660P | 2018-06-25 | 2018-06-25 | |
| US62/689,660 | 2018-06-25 | ||
| PCT/US2019/039030 WO2020005974A1 (en) | 2018-06-25 | 2019-06-25 | Methods of treating clrn1-associated hearing loss and/or vision loss |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Division JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021529519A JP2021529519A (ja) | 2021-11-04 |
| JPWO2020005974A5 true JPWO2020005974A5 (https=) | 2022-06-24 |
| JP2021529519A5 JP2021529519A5 (https=) | 2022-06-24 |
Family
ID=68985009
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020572414A Pending JP2021529519A (ja) | 2018-06-25 | 2019-06-25 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20210277417A1 (https=) |
| EP (1) | EP3824090A4 (https=) |
| JP (3) | JP2021529519A (https=) |
| KR (1) | KR20210057720A (https=) |
| CN (1) | CN112639107B (https=) |
| AU (2) | AU2019294603B2 (https=) |
| BR (1) | BR112020026606A2 (https=) |
| CA (1) | CA3104330A1 (https=) |
| CL (1) | CL2020003346A1 (https=) |
| EA (1) | EA202190114A1 (https=) |
| IL (1) | IL279551A (https=) |
| MX (1) | MX2020013628A (https=) |
| SG (1) | SG11202012710WA (https=) |
| WO (1) | WO2020005974A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230340038A1 (en) * | 2020-09-14 | 2023-10-26 | President And Fellows Of Harvard College | Recombinant adeno associated virus (raav) encoding gjb2 and uses thereof |
| MX2023007800A (es) * | 2020-12-29 | 2023-07-11 | Akouos Inc | Composiciones y metodos para tratar la perdida de audicion y/o la perdida de vision asociada a clrn1. |
| CA3233522A1 (en) * | 2021-09-30 | 2023-04-06 | Katherine Diane GRIBBLE | Gene therapy delivery compositions and methods for treating hearing loss |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8980952B2 (en) * | 2002-03-20 | 2015-03-17 | University Of Maryland, Baltimore | Methods for treating brain swelling with a compound that blocks a non-selective cation channel |
| KR20080016786A (ko) * | 2005-02-03 | 2008-02-22 | 주식회사 바이오텍 아이 | 당뇨병 치료용 조성물 및 당뇨병 치료 방법 |
| JP2009511014A (ja) * | 2005-10-05 | 2009-03-19 | ベイヒル セラピューティクス インコーポレーティッド | 自己免疫疾患の処置のための組成物および方法 |
| US20090215178A1 (en) * | 2008-02-22 | 2009-08-27 | Zequn Tang | Methods to enhance the stability and homogeneity of transgene expression in clonal cell lines |
| WO2011061937A1 (en) * | 2009-11-19 | 2011-05-26 | Immuno Tec Laboratory Co., Ltd. | Methods for producing antibody-producing cells that produce desired polypeptides |
| RU2658490C2 (ru) * | 2012-03-27 | 2018-06-21 | Кьюрвак Аг | Искусственные молекулы нуклеиновых кислот для улучшенной экспрессии белков или пептидов |
| CN102978284A (zh) * | 2012-11-19 | 2013-03-20 | 金子兵 | 一种筛查各类眼科遗传性疾病的基因芯片及其制备和使用方法 |
| ES2697249T3 (es) * | 2013-03-11 | 2019-01-22 | Fond Telethon | miR-204 y miR-211 y usos de los mismos |
| CA2909733C (en) * | 2013-04-18 | 2023-10-17 | Fondazione Telethon | Effective delivery of large genes by dual aav vectors |
| WO2016073900A1 (en) * | 2014-11-06 | 2016-05-12 | Case Western Reserve University | Compositions and methods of treating usher syndrome iii |
| CN107921118B (zh) * | 2015-06-12 | 2022-11-08 | 葛兰素史密丝克莱恩生物有限公司 | 腺病毒多核苷酸和多肽 |
| SG11201804814YA (en) * | 2015-12-11 | 2018-07-30 | Massachusetts Eye & Ear Infirmary | Materials and methods for delivering nucleic acids to cochlear and vestibular cells |
| JP2019530737A (ja) * | 2016-08-23 | 2019-10-24 | アコーオス インコーポレイテッド | ヒト対象において非加齢性聴力障害を治療するための組成物および方法 |
-
2019
- 2019-06-25 SG SG11202012710WA patent/SG11202012710WA/en unknown
- 2019-06-25 WO PCT/US2019/039030 patent/WO2020005974A1/en not_active Ceased
- 2019-06-25 CN CN201980055197.XA patent/CN112639107B/zh active Active
- 2019-06-25 JP JP2020572414A patent/JP2021529519A/ja active Pending
- 2019-06-25 CA CA3104330A patent/CA3104330A1/en active Pending
- 2019-06-25 AU AU2019294603A patent/AU2019294603B2/en active Active
- 2019-06-25 EP EP19827048.0A patent/EP3824090A4/en active Pending
- 2019-06-25 KR KR1020217002300A patent/KR20210057720A/ko not_active Ceased
- 2019-06-25 EA EA202190114A patent/EA202190114A1/ru unknown
- 2019-06-25 BR BR112020026606-0A patent/BR112020026606A2/pt unknown
- 2019-06-25 US US17/253,658 patent/US20210277417A1/en active Pending
- 2019-06-25 MX MX2020013628A patent/MX2020013628A/es unknown
-
2020
- 2020-12-17 IL IL279551A patent/IL279551A/en unknown
- 2020-12-22 CL CL2020003346A patent/CL2020003346A1/es unknown
-
2023
- 2023-08-23 JP JP2023135405A patent/JP2023153320A/ja active Pending
-
2025
- 2025-07-03 JP JP2025112689A patent/JP2025156349A/ja active Pending
-
2026
- 2026-02-24 AU AU2026201371A patent/AU2026201371A1/en active Pending
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