JPWO2020004675A5 - - Google Patents

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Publication number
JPWO2020004675A5
JPWO2020004675A5 JP2020527712A JP2020527712A JPWO2020004675A5 JP WO2020004675 A5 JPWO2020004675 A5 JP WO2020004675A5 JP 2020527712 A JP2020527712 A JP 2020527712A JP 2020527712 A JP2020527712 A JP 2020527712A JP WO2020004675 A5 JPWO2020004675 A5 JP WO2020004675A5
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Japan
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pharmaceutical composition
treatment
week
composition according
weeks
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JP2020527712A
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English (en)
Japanese (ja)
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JPWO2020004675A1 (ja
JP7345466B2 (ja
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Priority claimed from PCT/JP2019/026393 external-priority patent/WO2020004675A1/ja
Publication of JPWO2020004675A1 publication Critical patent/JPWO2020004675A1/ja
Publication of JPWO2020004675A5 publication Critical patent/JPWO2020004675A5/ja
Priority to JP2023143451A priority Critical patent/JP7595719B2/ja
Application granted granted Critical
Publication of JP7345466B2 publication Critical patent/JP7345466B2/ja
Priority to JP2024205093A priority patent/JP2025028961A/ja
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JP2020527712A 2018-06-26 2019-06-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用 Active JP7345466B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023143451A JP7595719B2 (ja) 2018-06-26 2023-09-05 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用
JP2024205093A JP2025028961A (ja) 2018-06-26 2024-11-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862690270P 2018-06-26 2018-06-26
US62/690,270 2018-06-26
US201862739386P 2018-10-01 2018-10-01
US62/739,386 2018-10-01
PCT/JP2019/026393 WO2020004675A1 (ja) 2018-06-26 2019-06-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023143451A Division JP7595719B2 (ja) 2018-06-26 2023-09-05 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用

Publications (3)

Publication Number Publication Date
JPWO2020004675A1 JPWO2020004675A1 (ja) 2021-07-15
JPWO2020004675A5 true JPWO2020004675A5 (enExample) 2022-03-03
JP7345466B2 JP7345466B2 (ja) 2023-09-15

Family

ID=68987235

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2020527712A Active JP7345466B2 (ja) 2018-06-26 2019-06-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用
JP2023143451A Active JP7595719B2 (ja) 2018-06-26 2023-09-05 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用
JP2024205093A Pending JP2025028961A (ja) 2018-06-26 2024-11-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2023143451A Active JP7595719B2 (ja) 2018-06-26 2023-09-05 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用
JP2024205093A Pending JP2025028961A (ja) 2018-06-26 2024-11-26 アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用

Country Status (21)

Country Link
US (2) US20210261963A1 (enExample)
EP (1) EP3815696A4 (enExample)
JP (3) JP7345466B2 (enExample)
KR (1) KR20210023988A (enExample)
CN (1) CN112399849A (enExample)
AU (2) AU2019293687B2 (enExample)
BR (1) BR112020026542A2 (enExample)
CA (1) CA3101321A1 (enExample)
CL (1) CL2020003367A1 (enExample)
CO (1) CO2020015685A2 (enExample)
EC (1) ECSP20083454A (enExample)
IL (1) IL279692A (enExample)
MX (2) MX2020013880A (enExample)
MY (1) MY209148A (enExample)
NZ (1) NZ770540A (enExample)
PE (1) PE20210630A1 (enExample)
PH (1) PH12020552078A1 (enExample)
SG (1) SG11202011554PA (enExample)
TW (1) TW202035692A (enExample)
WO (1) WO2020004675A1 (enExample)
ZA (1) ZA202007682B (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN113748209A (zh) 2019-02-27 2021-12-03 斯托克制药公司 用于治疗病况和疾病的反义寡聚体
AU2021270720A1 (en) 2020-05-11 2022-12-08 Stoke Therapeutics, Inc. OPA1 antisense oligomers for treatment of conditions and diseases
IL307937A (en) 2021-04-30 2023-12-01 Sarepta Therapeutics Inc Treatment methods for muscular dystrophy
JP2025509438A (ja) 2022-03-17 2025-04-11 サレプタ セラピューティクス, インコーポレイテッド ホスホロジアミデートモルホリノオリゴマーコンジュゲート
AU2024222908A1 (en) * 2023-02-14 2025-09-04 Stoke Therapeutics, Inc. Antisense oligomer formulations
US20240368596A1 (en) * 2023-05-05 2024-11-07 Biomarin Pharmaceutical Inc. Dystrophin exon skipping oligonucleotides

Family Cites Families (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE69033986T2 (de) 1989-12-20 2003-03-13 Antivirals Inc., Portland Ungeladene, auf Morpholin basierende Polymere mit Chiralen, Phosphor enthaltenden Brücken zwischen den Untereinheiten
EP2530155B1 (en) 2002-11-25 2016-03-16 Masafumi Matsuo ENA nucleic acid drugs modifying splicing in mRNA precursor
SI2206781T1 (sl) 2004-06-28 2016-05-31 The University Of Western Australia Protismiselni oligonukleotidi za induciranje preskakovanja eksona in postopki njihove uporabe
WO2006038608A1 (ja) 2004-10-05 2006-04-13 Nippon Shinyaku Co., Ltd. オリゴ二本鎖rna及び医薬組成物
US20090069260A1 (en) 2005-05-30 2009-03-12 Nippon Shinyaku Co., Ltd Method for producing a nucleic-acid-containing complex preparation
CA2884340C (en) 2007-11-15 2017-07-25 Sarepta Therapeutics, Inc. Method of synthesis of morpholino oligomers
US8084601B2 (en) 2008-09-11 2011-12-27 Royal Holloway And Bedford New College Royal Holloway, University Of London Oligomers
EP2762567B1 (en) 2008-10-24 2016-07-13 Sarepta Therapeutics, Inc. Multiple exon skipping compositions for DMD
TWI541024B (zh) * 2010-09-01 2016-07-11 日本新藥股份有限公司 反義核酸
ES2907250T3 (es) * 2012-01-27 2022-04-22 Biomarin Tech Bv Oligonucleótidos de modulación de ARN con características mejoradas para el tratamiento de la distrofia muscular de Duchenne y de Becker
KR20230074606A (ko) * 2013-03-14 2023-05-30 사렙타 쎄러퓨틱스 인코퍼레이티드 근육 이영양증의 치료를 위한 엑손 스키핑 조성물
NZ732507A (en) 2013-03-15 2018-08-31 Sarepta Therapeutics Inc Improved compositions for treating muscular dystrophy
CN105228999B (zh) * 2013-05-24 2021-03-02 味之素株式会社 吗啉代寡核苷酸的制备方法
WO2017059131A1 (en) * 2015-09-30 2017-04-06 Sarepta Therapeutics, Inc. Methods for treating muscular dystrophy
FR3044926B1 (fr) * 2015-12-09 2020-01-31 Genethon Outils de therapie genique efficaces pour le saut de l'exon 53 de la dystrophine

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