JP7708436B2 - 核酸を細胞に送達するための組成物および方法 - Google Patents

核酸を細胞に送達するための組成物および方法

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Publication number
JP7708436B2
JP7708436B2 JP2022513157A JP2022513157A JP7708436B2 JP 7708436 B2 JP7708436 B2 JP 7708436B2 JP 2022513157 A JP2022513157 A JP 2022513157A JP 2022513157 A JP2022513157 A JP 2022513157A JP 7708436 B2 JP7708436 B2 JP 7708436B2
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Prior art keywords
cells
nucleic acid
composition
sequence
seq
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JP2022513157A
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Japanese (ja)
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JPWO2021042060A5 (https=
JP2022546699A5 (https=
JP2022546699A (ja
Inventor
エリアス キジャーノ，
ピーター グレイザー，
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Yale University
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Yale University
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Priority claimed from PCT/US2019/048962 external-priority patent/WO2020047353A1/en
Priority claimed from PCT/US2019/048953 external-priority patent/WO2020047344A1/en
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Publication of JP2022546699A publication Critical patent/JP2022546699A/ja
Publication of JPWO2021042060A5 publication Critical patent/JPWO2021042060A5/ja
Publication of JP2022546699A5 publication Critical patent/JP2022546699A5/ja
Priority to JP2025069544A priority Critical patent/JP2025111590A/ja
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    • A61K47/50—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates
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JP2022513157A 2019-08-30 2020-08-31 核酸を細胞に送達するための組成物および方法 Active JP7708436B2 (ja)

Priority Applications (1)

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JP2025069544A JP2025111590A (ja) 2019-08-30 2025-04-21 核酸を細胞に送達するための組成物および方法

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
USPCT/US2019/048953 2019-08-30
PCT/US2019/048962 WO2020047353A1 (en) 2018-08-31 2019-08-30 Compositions and methods for enhancing triplex and nuclease-based gene editing
PCT/US2019/048953 WO2020047344A1 (en) 2018-08-31 2019-08-30 Compositions and methods for enhancing donor oligonucleotide-based gene editing
USPCT/US2019/048962 2019-08-30
US201962944281P 2019-12-05 2019-12-05
US62/944,281 2019-12-05
PCT/US2020/048823 WO2021042060A1 (en) 2019-08-30 2020-08-31 Compositions and methods for delivery of nucleic acids to cells

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JP2022546699A JP2022546699A (ja) 2022-11-07
JPWO2021042060A5 JPWO2021042060A5 (https=) 2023-09-08
JP2022546699A5 JP2022546699A5 (https=) 2023-09-08
JP7708436B2 true JP7708436B2 (ja) 2025-07-15

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