JP7397488B2 - Ｓｏｄ１二重発現ベクターおよびその使用 - Google Patents
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| WO2012145624A2 (en) | 2011-04-21 | 2012-10-26 | University Of Massachusetts | Raav-based compositions and methods for treating alpha-1 anti-trypsin deficiencies |
| JP6756700B2 (ja) | 2014-03-18 | 2020-09-16 | ユニバーシティ オブ マサチューセッツ | 筋萎縮性側索硬化症を処置するためのｒＡＡＶベースの組成物および方法 |
| AU2018264996A1 (en) | 2017-05-09 | 2019-12-05 | University Of Massachusetts | Methods of treating Amyotrophic Lateral Sclerosis (ALS) |
| CN118006607A (zh) | 2017-09-22 | 2024-05-10 | 马萨诸塞大学 | Sod1双表达载体及其用途 |
| AR123524A1 (es) * | 2020-09-16 | 2022-12-14 | Biogen Ma Inc | Composiciones y métodos para tratar la esclerosis lateral amiotrófica (ela) con aav-mir-sod1 |
| EP4291654A2 (en) | 2021-02-12 | 2023-12-20 | Alnylam Pharmaceuticals, Inc. | Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases |
| US20250101424A1 (en) * | 2023-09-25 | 2025-03-27 | California Institute Of Technology | Mirna circuits for controlled gene expression |
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| EP3684937A1 (en) | 2020-07-29 |
| AU2018338188A1 (en) | 2020-04-02 |
| AU2018338188B2 (en) | 2025-02-20 |
| US12312587B2 (en) | 2025-05-27 |
| JP2025169472A (ja) | 2025-11-13 |
| JP2020535804A (ja) | 2020-12-10 |
| CN118006607A (zh) | 2024-05-10 |
| CN111448321A (zh) | 2020-07-24 |
| JP7717398B2 (ja) | 2025-08-04 |
| AU2025203314A1 (en) | 2025-05-29 |
| WO2019060686A1 (en) | 2019-03-28 |
| CA3075643A1 (en) | 2019-03-28 |
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