JP7389040B2 - 遺伝子治療のための修飾ｒＡＡＶキャプシドタンパク質 - Google Patents

遺伝子治療のための修飾ｒＡＡＶキャプシドタンパク質 Download PDF

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JP7389040B2
JP7389040B2 JP2020539801A JP2020539801A JP7389040B2 JP 7389040 B2 JP7389040 B2 JP 7389040B2 JP 2020539801 A JP2020539801 A JP 2020539801A JP 2020539801 A JP2020539801 A JP 2020539801A JP 7389040 B2 JP7389040 B2 JP 7389040B2
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ジョナサン・ダグラス・フィン
ディルク・グリム
キャスリーン・ベルナー
スサンネ・アンナ・スヌーク
ニールス・ブルクストラ
サビーネ・マリア・ヘルトルーデ・ファン・デル・サンデン
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メイラジーティーエックス・ユーケー・ザ・セカンド・リミテッド
ウニヴェルシテート ハイデルベルク
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JP2020539801A 2018-01-17 2019-01-17 遺伝子治療のための修飾ｒＡＡＶキャプシドタンパク質 Active JP7389040B2 (ja)

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EP18152133 2018-01-17
EP18152133.7 2018-01-17
PCT/EP2019/051128 WO2019141765A1 (en) 2018-01-17 2019-01-17 A modified raav capsid protein for gene therapy

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JP2007504219A (ja) 2003-09-01 2007-03-01 アカデミッシュ メディッシュ セントラム 関節リウマチのインビボ遺伝子治療のためのａａｖベクター
WO2013174760A1 (en) 2012-05-25 2013-11-28 Deutsches Krebsforschungszentrum Optimized aav-vectors for high transduction rates in dendritic cells
JP2017531652A (ja) 2014-10-06 2017-10-26 アルスロジェン ビー．ブイ．Ａｒｔｈｒｏｇｅｎ Ｂ．Ｖ． Ａａｖに基づく遺伝子治療
JP2018500311A (ja) 2014-12-16 2018-01-11 ボード オブ リージェンツ オブ ザ ユニバーシティ オブ ネブラスカ 若年型バッテン病のための遺伝子療法

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PH12020551096A1 (en) 2021-06-21
AU2019209595A1 (en) 2020-09-03
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ZA202004980B (en) 2025-07-30
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EP3740222B1 (en) 2023-06-28
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CA3087910A1 (en) 2019-07-25
CN112004544A (zh) 2020-11-27
US20200354744A1 (en) 2020-11-12
IL275838B1 (en) 2024-07-01
MX2020006764A (es) 2021-01-08
RS64499B1 (sr) 2023-09-29
IL275838B2 (en) 2024-11-01
DK3740222T3 (da) 2023-07-31
SMT202300284T1 (it) 2023-11-13
NZ767106A (en) 2023-10-27
US12480138B2 (en) 2025-11-25
HUE062774T2 (hu) 2023-12-28
BR112020014625A2 (pt) 2020-12-08
KR20200135768A (ko) 2020-12-03
SI3740222T1 (sl) 2023-11-30
LT3740222T (lt) 2023-09-11
MY202252A (en) 2024-04-19
AU2019209595B2 (en) 2023-04-27

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