JP7233149B2 - 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用 - Google Patents

眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用 Download PDF

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JP7233149B2
JP7233149B2 JP2019532105A JP2019532105A JP7233149B2 JP 7233149 B2 JP7233149 B2 JP 7233149B2 JP 2019532105 A JP2019532105 A JP 2019532105A JP 2019532105 A JP2019532105 A JP 2019532105A JP 7233149 B2 JP7233149 B2 JP 7233149B2
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ストリングス－ウフォムバー，ヴァネッサ
スーイ，デイヴィッド
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ベニテック アイピー ホールディングス インコーポレーテッド
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JP2019532105A 2016-12-14 2017-12-14 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用 Active JP7233149B2 (ja)

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JP2023023159A JP7431359B2 (ja) 2016-12-14 2023-02-17 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用

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US201662434312P 2016-12-14 2016-12-14
US62/434,312 2016-12-14
PCT/AU2017/051385 WO2018107228A1 (en) 2016-12-14 2017-12-14 Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

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JP2023023159A Active JP7431359B2 (ja) 2016-12-14 2023-02-17 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用

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US (2) US11142765B2 (https=)
EP (1) EP3555294A4 (https=)
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KR (2) KR102667867B1 (https=)
CN (2) CN110382698B (https=)
AU (2) AU2017377661B2 (https=)
CA (1) CA3047154A1 (https=)
IL (2) IL267353B2 (https=)
MX (2) MX2019007110A (https=)
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WO (1) WO2018107228A1 (https=)
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EP3555294A4 (en) * 2016-12-14 2020-08-26 Benitec Biopharma Limited REAGENTS FOR THE TREATMENT OF OCULOPHARYNGEAL MUSCLE DYSTROPHY (PDD) AND THEIR USE
CN112867511A (zh) * 2018-10-17 2021-05-28 贝尼泰克生物制药有限公司 用于治疗眼咽肌营养不良(opmd)的方法
US20220098614A1 (en) 2019-02-28 2022-03-31 Benitec IP Holdings Inc. Compositions and Methods for Treating Oculopharyngeal Muscular Dystrophy (OPMD)
CN114901822A (zh) * 2019-12-23 2022-08-12 维萨梅布有限公司 用于同时调节基因表达的组合物和方法
WO2026011009A1 (en) * 2024-07-02 2026-01-08 Kate Therapeutics, Inc. Compositions and methods for muscle disorders

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CA3020754C (en) * 2016-04-14 2023-07-25 Benitec Biopharma Limited Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof
EP3555294A4 (en) 2016-12-14 2020-08-26 Benitec Biopharma Limited REAGENTS FOR THE TREATMENT OF OCULOPHARYNGEAL MUSCLE DYSTROPHY (PDD) AND THEIR USE

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JP7431359B2 (ja) 2024-02-14
AU2023222827A1 (en) 2023-09-14
KR20230020586A (ko) 2023-02-10
IL267353B2 (en) 2023-12-01
WO2018107228A1 (en) 2018-06-21
JP2023062092A (ja) 2023-05-02
IL304674B1 (en) 2024-07-01
BR112019012312A8 (pt) 2023-02-28
CN118421624A (zh) 2024-08-02
JP2020503014A (ja) 2020-01-30
US20190330629A1 (en) 2019-10-31
RU2763319C2 (ru) 2021-12-28
RU2019121950A3 (https=) 2021-01-18
MX2024003643A (es) 2024-04-15
AU2017377661A1 (en) 2019-07-18
IL304674A (en) 2023-09-01
KR20190104151A (ko) 2019-09-06
CA3047154A1 (en) 2018-06-21
IL304674B2 (en) 2024-11-01
ZA202106827B (en) 2022-07-27
KR102495222B1 (ko) 2023-02-09
BR112019012312A2 (pt) 2020-02-11
KR102667867B1 (ko) 2024-05-29
EP3555294A4 (en) 2020-08-26
IL267353A (en) 2019-08-29
US20220056446A1 (en) 2022-02-24
CN110382698A (zh) 2019-10-25
US11142765B2 (en) 2021-10-12
MX2019007110A (es) 2019-12-05
AU2023222827B2 (en) 2025-02-27
CN110382698B (zh) 2024-05-10
RU2019121950A (ru) 2021-01-18
AU2017377661B2 (en) 2023-07-27
EP3555294A1 (en) 2019-10-23
US11932852B2 (en) 2024-03-19
IL267353B1 (en) 2023-08-01

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