JP7073264B2 - 遺伝子構築物 - Google Patents

遺伝子構築物 Download PDF

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JP7073264B2
JP7073264B2 JP2018540229A JP2018540229A JP7073264B2 JP 7073264 B2 JP7073264 B2 JP 7073264B2 JP 2018540229 A JP2018540229 A JP 2018540229A JP 2018540229 A JP2018540229 A JP 2018540229A JP 7073264 B2 JP7073264 B2 JP 7073264B2
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recombinant vector
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variant
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JP2018535696A5 (OSRAM
JP2018535696A (ja
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ウィドーソン，ピーター
マーティン，キース
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Quethera Ltd
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Quethera Ltd
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JP2018540229A 2015-10-26 2016-10-25 遺伝子構築物 Active JP7073264B2 (ja)

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JP2022078299A JP7503590B2 (ja) 2015-10-26 2022-05-11 遺伝子構築物

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Application Number Priority Date Filing Date Title
GB1518911.1 2015-10-26
GB1518911.1A GB2547179A (en) 2015-10-26 2015-10-26 Genetic construct
PCT/GB2016/053319 WO2017072498A1 (en) 2015-10-26 2016-10-25 Genetic construct

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JP2018535696A JP2018535696A (ja) 2018-12-06
JP2018535696A5 JP2018535696A5 (OSRAM) 2019-11-21
JP7073264B2 true JP7073264B2 (ja) 2022-05-23

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US (2) US10342880B2 (OSRAM)
EP (2) EP3985119A1 (OSRAM)
JP (2) JP7073264B2 (OSRAM)
KR (1) KR102819739B1 (OSRAM)
CN (1) CN108350467B (OSRAM)
AU (1) AU2016344508B2 (OSRAM)
CY (1) CY1124588T1 (OSRAM)
DK (1) DK3368678T3 (OSRAM)
ES (1) ES2886009T3 (OSRAM)
GB (1) GB2547179A (OSRAM)
HR (1) HRP20211407T1 (OSRAM)
HU (1) HUE056911T2 (OSRAM)
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MX (1) MX2018005286A (OSRAM)
PL (1) PL3368678T3 (OSRAM)
PT (1) PT3368678T (OSRAM)
RS (1) RS62460B1 (OSRAM)
RU (1) RU2734678C2 (OSRAM)
SI (1) SI3368678T1 (OSRAM)
SM (1) SMT202100520T1 (OSRAM)
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WO2017058926A1 (en) 2015-10-01 2017-04-06 Goleini Inc. Targeted expression of chloride channels and methods of use thereof
GB201705484D0 (en) * 2017-04-05 2017-05-17 Quethera Ltd Genetic construct
CN111372612A (zh) * 2017-09-27 2020-07-03 西吉隆医疗股份有限公司 包含活性细胞的方法、组合物和可植入元件
IL321310A (en) 2017-10-20 2025-08-01 Res Inst Nationwide Childrens Hospital Methods and materials for NT-3 gene therapy
EP3720460A1 (en) * 2017-12-05 2020-10-14 University of Washington Compositions and methods for enhancing functional expression of therapeutic genes in photoreceptors
CN108250288A (zh) * 2018-01-17 2018-07-06 吉林省农业科学院 一种叶绿体表达的脑源性神经营养因子hBDNFb蛋白及其制备方法
CN109022487A (zh) * 2018-08-15 2018-12-18 上海市第人民医院 一种表达p65的基因载体及其用于治疗视网膜神经节细胞变性的基因治疗药物
WO2020077295A1 (en) * 2018-10-11 2020-04-16 Decibel Therapeutics, Inc. Aav1 vectors and uses thereof for treatment of otic indications
SG11202105267VA (en) * 2018-12-19 2021-07-29 Versameb Ag Rna encoding a protein
CN113557301B (zh) * 2019-03-04 2025-03-07 公益财团法人东京都医学综合研究所 编码Trk片段的核酸构建体及其利用
MA55223A (fr) * 2019-03-06 2022-01-12 Generation Bio Co Adn à extrémité fermée (cedna) et composés de modulation immunitaire
US20230123802A1 (en) * 2019-03-27 2023-04-20 Sigilon Therapeutics, Inc. Compositions, devices, and methods for factor vii therapy
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