JP2025514978A5 - - Google Patents
Info
- Publication number
- JP2025514978A5 JP2025514978A5 JP2024563648A JP2024563648A JP2025514978A5 JP 2025514978 A5 JP2025514978 A5 JP 2025514978A5 JP 2024563648 A JP2024563648 A JP 2024563648A JP 2024563648 A JP2024563648 A JP 2024563648A JP 2025514978 A5 JP2025514978 A5 JP 2025514978A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- amino acid
- acid sequence
- seq
- use according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (9)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263364188P | 2022-05-04 | 2022-05-04 | |
| US63/364,188 | 2022-05-04 | ||
| US202263366447P | 2022-06-15 | 2022-06-15 | |
| US63/366,447 | 2022-06-15 | ||
| US202263366662P | 2022-06-20 | 2022-06-20 | |
| US63/366,662 | 2022-06-20 | ||
| US202263378987P | 2022-10-10 | 2022-10-10 | |
| US63/378,987 | 2022-10-10 | ||
| PCT/US2023/020843 WO2023215384A2 (en) | 2022-05-04 | 2023-05-03 | Use of myostatin inhibitor for treating spinal muscular atrophy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025514978A JP2025514978A (ja) | 2025-05-13 |
| JP2025514978A5 true JP2025514978A5 (enExample) | 2026-05-11 |
Family
ID=86732326
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024563648A Pending JP2025514978A (ja) | 2022-05-04 | 2023-05-03 | 脊髄性筋萎縮症を治療するためのミオスタチン阻害薬の使用 |
Country Status (20)
| Country | Link |
|---|---|
| US (1) | US20250326827A1 (enExample) |
| EP (2) | EP4518970B1 (enExample) |
| JP (1) | JP2025514978A (enExample) |
| KR (1) | KR20250021401A (enExample) |
| CN (1) | CN119451696A (enExample) |
| AU (1) | AU2023265846A1 (enExample) |
| CA (1) | CA3251441A1 (enExample) |
| DK (1) | DK4518970T3 (enExample) |
| ES (1) | ES3072446T3 (enExample) |
| FI (1) | FI4518970T3 (enExample) |
| HR (1) | HRP20260506T1 (enExample) |
| IL (1) | IL316463A (enExample) |
| LT (1) | LT4518970T (enExample) |
| MX (1) | MX2024013313A (enExample) |
| PL (1) | PL4518970T3 (enExample) |
| PT (1) | PT4518970T (enExample) |
| RS (1) | RS68105B1 (enExample) |
| SI (1) | SI4518970T1 (enExample) |
| SM (1) | SMT202600209T1 (enExample) |
| WO (1) | WO2023215384A2 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2016073853A1 (en) | 2014-11-06 | 2016-05-12 | Scholar Rock, Inc. | Anti-pro/latent-myostatin antibodies and uses thereof |
| EA038146B1 (ru) | 2015-09-15 | 2021-07-13 | Сколар Рок, Инк. | Антитела к про-/латентному миостатину и их применения |
| CN120677175A (zh) | 2022-12-22 | 2025-09-19 | 供石公司 | 肌生成抑制蛋白活化的选择性和强效抑制剂 |
| WO2026076383A1 (en) * | 2024-10-06 | 2026-04-09 | Scholar Rock, Inc. | Use of myostatin inhibitor for treating spinal muscular atrophy |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20040044063A1 (en) | 2002-05-31 | 2004-03-04 | Brent Stockwell | SMA therapy and cell based assay for identifying therapies |
| EP2144614A1 (en) | 2007-04-12 | 2010-01-20 | Paratek Pharmaceuticals, Inc. | Methods for treating spinal muscular atrophy using tetracycline compounds |
| MX2017005774A (es) | 2014-12-19 | 2017-07-28 | Chugai Pharmaceutical Co Ltd | Anticuerpos antimiostatina, polipeptidos que contienen regiones fc variantes, y metodos de uso. |
| EA038146B1 (ru) | 2015-09-15 | 2021-07-13 | Сколар Рок, Инк. | Антитела к про-/латентному миостатину и их применения |
| PL4218804T3 (pl) * | 2016-06-13 | 2026-05-25 | Scholar Rock, Inc. | Stosowanie inhibitorów miostatyny i terapii skojarzonych |
| EP4232151B1 (en) | 2020-10-26 | 2025-10-22 | Scholar Rock, Inc. | Use of anti-pro/latent myostatin antibody for treating spinal muscular atrophy |
| CN117545842A (zh) | 2021-01-29 | 2024-02-09 | 拜奥卡德联合股份公司 | SMN1和miR-23a在治疗脊髓性肌萎缩中的协同效应 |
-
2023
- 2023-05-03 LT LTEPPCT/US2023/020843T patent/LT4518970T/lt unknown
- 2023-05-03 PT PT237295399T patent/PT4518970T/pt unknown
- 2023-05-03 HR HRP20260506TT patent/HRP20260506T1/hr unknown
- 2023-05-03 EP EP23729539.9A patent/EP4518970B1/en active Active
- 2023-05-03 WO PCT/US2023/020843 patent/WO2023215384A2/en not_active Ceased
- 2023-05-03 US US18/862,079 patent/US20250326827A1/en active Pending
- 2023-05-03 AU AU2023265846A patent/AU2023265846A1/en active Pending
- 2023-05-03 CN CN202380045672.1A patent/CN119451696A/zh active Pending
- 2023-05-03 JP JP2024563648A patent/JP2025514978A/ja active Pending
- 2023-05-03 FI FIEP23729539.9T patent/FI4518970T3/fi active
- 2023-05-03 IL IL316463A patent/IL316463A/en unknown
- 2023-05-03 PL PL23729539.9T patent/PL4518970T3/pl unknown
- 2023-05-03 RS RS20260510A patent/RS68105B1/sr unknown
- 2023-05-03 SI SI202330091T patent/SI4518970T1/sl unknown
- 2023-05-03 KR KR1020247040101A patent/KR20250021401A/ko active Pending
- 2023-05-03 SM SM20260209T patent/SMT202600209T1/it unknown
- 2023-05-03 DK DK23729539.9T patent/DK4518970T3/da active
- 2023-05-03 ES ES23729539T patent/ES3072446T3/es active Active
- 2023-05-03 CA CA3251441A patent/CA3251441A1/en active Pending
- 2023-05-03 EP EP26167260.4A patent/EP4778536A2/en active Pending
-
2024
- 2024-10-28 MX MX2024013313A patent/MX2024013313A/es unknown
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