JP2025509438A5 - - Google Patents

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Publication number
JP2025509438A5
JP2025509438A5 JP2024553854A JP2024553854A JP2025509438A5 JP 2025509438 A5 JP2025509438 A5 JP 2025509438A5 JP 2024553854 A JP2024553854 A JP 2024553854A JP 2024553854 A JP2024553854 A JP 2024553854A JP 2025509438 A5 JP2025509438 A5 JP 2025509438A5
Authority
JP
Japan
Prior art keywords
pharmaceutically acceptable
acceptable salt
antisense oligomer
oligomer conjugate
item
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024553854A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025509438A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/064513 external-priority patent/WO2023178230A1/en
Publication of JP2025509438A publication Critical patent/JP2025509438A/ja
Publication of JP2025509438A5 publication Critical patent/JP2025509438A5/ja
Pending legal-status Critical Current

Links

JP2024553854A 2022-03-17 2023-03-16 ホスホロジアミデートモルホリノオリゴマーコンジュゲート Pending JP2025509438A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263320773P 2022-03-17 2022-03-17
US63/320,773 2022-03-17
PCT/US2023/064513 WO2023178230A1 (en) 2022-03-17 2023-03-16 Phosphorodiamidate morpholino oligomer conjugates

Publications (2)

Publication Number Publication Date
JP2025509438A JP2025509438A (ja) 2025-04-11
JP2025509438A5 true JP2025509438A5 (https=) 2026-03-25

Family

ID=85979575

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024553854A Pending JP2025509438A (ja) 2022-03-17 2023-03-16 ホスホロジアミデートモルホリノオリゴマーコンジュゲート

Country Status (11)

Country Link
US (1) US20250195667A1 (https=)
EP (1) EP4493693A1 (https=)
JP (1) JP2025509438A (https=)
KR (1) KR20240155352A (https=)
CN (1) CN119013401A (https=)
AU (1) AU2023235302A1 (https=)
CA (1) CA3252177A1 (https=)
CO (1) CO2024012425A2 (https=)
IL (1) IL315280A (https=)
MX (1) MX2024011069A (https=)
WO (1) WO2023178230A1 (https=)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SG11202100928QA (en) 2018-08-02 2021-02-25 Dyne Therapeutics Inc Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
US12018087B2 (en) 2018-08-02 2024-06-25 Dyne Therapeutics, Inc. Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
US11168141B2 (en) 2018-08-02 2021-11-09 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
CA3108282A1 (en) 2018-08-02 2020-02-06 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
US11771776B2 (en) 2021-07-09 2023-10-03 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
US11969475B2 (en) 2021-07-09 2024-04-30 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy

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