JP2024534502A5 - - Google Patents

Info

Publication number
JP2024534502A5
JP2024534502A5 JP2024517430A JP2024517430A JP2024534502A5 JP 2024534502 A5 JP2024534502 A5 JP 2024534502A5 JP 2024517430 A JP2024517430 A JP 2024517430A JP 2024517430 A JP2024517430 A JP 2024517430A JP 2024534502 A5 JP2024534502 A5 JP 2024534502A5
Authority
JP
Japan
Prior art keywords
halogens
optionally substituted
alkyl group
group optionally
halogen
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024517430A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024534502A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/044377 external-priority patent/WO2023049258A1/en
Publication of JP2024534502A publication Critical patent/JP2024534502A/ja
Publication of JP2024534502A5 publication Critical patent/JP2024534502A5/ja
Pending legal-status Critical Current

Links

JP2024517430A 2021-09-22 2022-09-22 オリゴヌクレオチドのインビボ送達に使用するための2’-アルキル又は3’-アルキル修飾リボース誘導体 Pending JP2024534502A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163246870P 2021-09-22 2021-09-22
US63/246,870 2021-09-22
PCT/US2022/044377 WO2023049258A1 (en) 2021-09-22 2022-09-22 2'-alkyl or 3'- alkyl modified ribose derivatives for use in the in-vivo delivery of oligonucleotides

Publications (2)

Publication Number Publication Date
JP2024534502A JP2024534502A (ja) 2024-09-20
JP2024534502A5 true JP2024534502A5 (https=) 2025-09-30

Family

ID=84053050

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024517430A Pending JP2024534502A (ja) 2021-09-22 2022-09-22 オリゴヌクレオチドのインビボ送達に使用するための2’-アルキル又は3’-アルキル修飾リボース誘導体

Country Status (9)

Country Link
US (1) US20230241224A1 (https=)
EP (1) EP4405368A1 (https=)
JP (1) JP2024534502A (https=)
KR (1) KR20240082361A (https=)
CN (1) CN118076619A (https=)
AU (1) AU2022352676A1 (https=)
CA (1) CA3233113A1 (https=)
IL (1) IL311486A (https=)
WO (1) WO2023049258A1 (https=)

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MX2025013094A (es) * 2023-05-03 2026-02-03 Sanegene Bio Usa Inc Conjugados basados en lipidos para la administracion sistemica en el sistema nervioso central, el sistema nervioso periferico y ocular
US20250064939A1 (en) * 2023-07-24 2025-02-27 Sanegene Bio Usa Inc. Lipid-based enhancement agent for rna delivery and therapy
CN116854754B (zh) 2023-09-01 2023-12-12 北京悦康科创医药科技股份有限公司 一种含有核糖环或其衍生结构的GalNAc化合物及其寡核苷酸缀合物
WO2025144872A2 (en) * 2023-12-29 2025-07-03 Adarx Pharmaceuticals, Inc. Nucleoside-derived lipids for drug delivery
WO2026041067A2 (en) 2024-08-20 2026-02-26 Sanegene Bio Usa Inc. Small interfering rna targeting myostatin (mstn) and uses thereof
WO2026046411A1 (en) 2024-09-02 2026-03-05 Sanegene Bio Usa Inc. Small interfering rna targeting plasminogen (plg) and uses thereof

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