JP2025502064A5 - - Google Patents
Info
- Publication number
- JP2025502064A5 JP2025502064A5 JP2024540893A JP2024540893A JP2025502064A5 JP 2025502064 A5 JP2025502064 A5 JP 2025502064A5 JP 2024540893 A JP2024540893 A JP 2024540893A JP 2024540893 A JP2024540893 A JP 2024540893A JP 2025502064 A5 JP2025502064 A5 JP 2025502064A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutically acceptable
- acceptable salt
- compound
- compound according
- aforementioned
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263297090P | 2022-01-06 | 2022-01-06 | |
| US63/297,090 | 2022-01-06 | ||
| US202263382854P | 2022-11-08 | 2022-11-08 | |
| US63/382,854 | 2022-11-08 | ||
| PCT/US2023/010331 WO2023133284A2 (en) | 2022-01-06 | 2023-01-06 | Compounds and methods for treating friedreich's ataxia |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025502064A JP2025502064A (ja) | 2025-01-24 |
| JP2025502064A5 true JP2025502064A5 (https=) | 2026-01-06 |
Family
ID=87074158
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024540893A Pending JP2025502064A (ja) | 2022-01-06 | 2023-01-06 | フリードライヒ運動失調症を治療するための化合物及び方法 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20250109132A1 (https=) |
| EP (1) | EP4460302A4 (https=) |
| JP (1) | JP2025502064A (https=) |
| KR (1) | KR20240138079A (https=) |
| AU (1) | AU2023205889A1 (https=) |
| CA (1) | CA3246468A1 (https=) |
| CL (1) | CL2024002029A1 (https=) |
| CO (1) | CO2024010651A2 (https=) |
| CR (1) | CR20240321A (https=) |
| IL (1) | IL314006A (https=) |
| MX (1) | MX2024008474A (https=) |
| PE (1) | PE20241730A1 (https=) |
| TW (1) | TW202334148A (https=) |
| WO (1) | WO2023133284A2 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025076181A1 (en) * | 2023-10-03 | 2025-04-10 | Design Therapeutics, Inc. | Methods and compounds for modulating huntington's disease |
| WO2025076219A1 (en) * | 2023-10-03 | 2025-04-10 | Design Therapeutics, Inc. | Methods and compounds for modulating huntington's disease |
| WO2025076236A1 (en) * | 2023-10-03 | 2025-04-10 | Design Therapeutics, Inc. | Methods and compounds for modulating huntington's disease |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2013097052A1 (en) * | 2011-12-30 | 2013-07-04 | Abbott Laboratories | Bromodomain inhibitors |
| CN106068266A (zh) * | 2013-10-11 | 2016-11-02 | 千叶县 | 以癌症驱动基因的基因突变为靶点进行烷基化的新型烷基化剂 |
| US11759533B2 (en) * | 2017-03-29 | 2023-09-19 | Wisconsin Alumni Research Foundation | Methods and compositions for modulating gene expression |
| WO2020253711A1 (zh) * | 2019-06-17 | 2020-12-24 | 中国科学院上海药物研究所 | 一种吡咯并吡啶酮类化合物、其制备方法、其组合物和用途 |
| KR102677015B1 (ko) * | 2019-07-02 | 2024-06-19 | 누베이션 바이오 인크. | Bet 억제제로서의 헤테로시클릭 화합물 |
| JP2024502469A (ja) * | 2021-01-08 | 2024-01-19 | デザイン セラピューティクス,インク. | フリードライヒ運動失調症を治療するための方法及び化合物 |
-
2023
- 2023-01-06 JP JP2024540893A patent/JP2025502064A/ja active Pending
- 2023-01-06 US US18/726,567 patent/US20250109132A1/en active Pending
- 2023-01-06 TW TW112100613A patent/TW202334148A/zh unknown
- 2023-01-06 MX MX2024008474A patent/MX2024008474A/es unknown
- 2023-01-06 IL IL314006A patent/IL314006A/en unknown
- 2023-01-06 PE PE2024001532A patent/PE20241730A1/es unknown
- 2023-01-06 WO PCT/US2023/010331 patent/WO2023133284A2/en not_active Ceased
- 2023-01-06 AU AU2023205889A patent/AU2023205889A1/en active Pending
- 2023-01-06 KR KR1020247025794A patent/KR20240138079A/ko active Pending
- 2023-01-06 CA CA3246468A patent/CA3246468A1/en active Pending
- 2023-01-06 EP EP23737637.1A patent/EP4460302A4/en active Pending
- 2023-01-06 CR CR20240321A patent/CR20240321A/es unknown
-
2024
- 2024-07-03 CL CL2024002029A patent/CL2024002029A1/es unknown
- 2024-08-02 CO CONC2024/0010651A patent/CO2024010651A2/es unknown
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