JP2024529108A5 - - Google Patents
Info
- Publication number
- JP2024529108A5 JP2024529108A5 JP2024508332A JP2024508332A JP2024529108A5 JP 2024529108 A5 JP2024529108 A5 JP 2024529108A5 JP 2024508332 A JP2024508332 A JP 2024508332A JP 2024508332 A JP2024508332 A JP 2024508332A JP 2024529108 A5 JP2024529108 A5 JP 2024529108A5
- Authority
- JP
- Japan
- Prior art keywords
- editing system
- gene editing
- sequence
- gene
- nucleic acid
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163231784P | 2021-08-11 | 2021-08-11 | |
| US63/231,784 | 2021-08-11 | ||
| US202263322002P | 2022-03-21 | 2022-03-21 | |
| US63/322,002 | 2022-03-21 | ||
| PCT/US2022/040042 WO2023018858A1 (en) | 2021-08-11 | 2022-08-11 | Gene editing systems comprising an rna guide targeting stathmin 2 (stmn2) and uses thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024529108A JP2024529108A (ja) | 2024-08-01 |
| JP2024529108A5 true JP2024529108A5 (https=) | 2025-08-19 |
Family
ID=83193363
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024508332A Pending JP2024529108A (ja) | 2021-08-11 | 2022-08-11 | スタスミン2(stmn2)を標的とするrnaガイドを含む遺伝子編集システム及びその使用 |
Country Status (10)
| Country | Link |
|---|---|
| US (2) | US20230203539A1 (https=) |
| EP (1) | EP4384618A1 (https=) |
| JP (1) | JP2024529108A (https=) |
| KR (1) | KR20240052763A (https=) |
| AU (1) | AU2022328401A1 (https=) |
| CA (1) | CA3228487A1 (https=) |
| CO (1) | CO2024002315A2 (https=) |
| IL (1) | IL310616A (https=) |
| MX (1) | MX2024001878A (https=) |
| WO (1) | WO2023018858A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2023205844A1 (en) * | 2022-04-26 | 2023-11-02 | Peter Maccallum Cancer Institute | Nucleic acids and uses thereof |
| KR20250151430A (ko) * | 2023-02-15 | 2025-10-21 | 아버 바이오테크놀로지스, 인크. | 스타스민 2(stmn2) 전사체에서 비정상적인 스플라이싱을 억제하는 유전자 편집 방법 |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2019178427A1 (en) | 2018-03-14 | 2019-09-19 | Arbor Biotechnologies, Inc. | Novel crispr dna targeting enzymes and systems |
| CA3126918A1 (en) * | 2019-01-14 | 2020-07-23 | President And Fellows Of Harvard College | Methods and compositions for restoring stmn2 levels |
| EP3976010A4 (en) * | 2019-06-03 | 2023-08-02 | Quralis Corporation | Oligonucleotides and methods of use for treating neurological diseases |
| CN121380024A (zh) | 2020-03-31 | 2026-01-23 | 阿伯生物技术公司 | 包含Cas12i2变体多肽的组合物及其用途 |
| CN115851665B (zh) * | 2021-05-27 | 2025-01-24 | 中国科学院动物研究所 | 工程化的Cas12i核酸酶及其效应蛋白以及用途 |
-
2022
- 2022-08-11 US US17/885,876 patent/US20230203539A1/en not_active Abandoned
- 2022-08-11 CA CA3228487A patent/CA3228487A1/en active Pending
- 2022-08-11 AU AU2022328401A patent/AU2022328401A1/en active Pending
- 2022-08-11 KR KR1020247007547A patent/KR20240052763A/ko active Pending
- 2022-08-11 EP EP22765309.4A patent/EP4384618A1/en active Pending
- 2022-08-11 WO PCT/US2022/040042 patent/WO2023018858A1/en not_active Ceased
- 2022-08-11 MX MX2024001878A patent/MX2024001878A/es unknown
- 2022-08-11 US US18/682,643 patent/US20250127924A1/en active Pending
- 2022-08-11 IL IL310616A patent/IL310616A/en unknown
- 2022-08-11 JP JP2024508332A patent/JP2024529108A/ja active Pending
-
2024
- 2024-02-27 CO CONC2024/0002315A patent/CO2024002315A2/es unknown
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