JP2025506419A5 - - Google Patents

Info

Publication number
JP2025506419A5
JP2025506419A5 JP2024546193A JP2024546193A JP2025506419A5 JP 2025506419 A5 JP2025506419 A5 JP 2025506419A5 JP 2024546193 A JP2024546193 A JP 2024546193A JP 2024546193 A JP2024546193 A JP 2024546193A JP 2025506419 A5 JP2025506419 A5 JP 2025506419A5
Authority
JP
Japan
Prior art keywords
gjb2
polynucleotide
nucleic acid
acid vector
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024546193A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025506419A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/061953 external-priority patent/WO2023150689A2/en
Publication of JP2025506419A publication Critical patent/JP2025506419A/ja
Publication of JP2025506419A5 publication Critical patent/JP2025506419A5/ja
Pending legal-status Critical Current

Links

JP2024546193A 2022-02-04 2023-02-03 Gjb2調節エレメント及びその使用 Pending JP2025506419A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263306941P 2022-02-04 2022-02-04
US202263306928P 2022-02-04 2022-02-04
US63/306,941 2022-02-04
US63/306,928 2022-02-04
PCT/US2023/061953 WO2023150689A2 (en) 2022-02-04 2023-02-03 Gjb2 regulatory elements and uses thereof

Publications (2)

Publication Number Publication Date
JP2025506419A JP2025506419A (ja) 2025-03-11
JP2025506419A5 true JP2025506419A5 (https=) 2026-02-04

Family

ID=87552983

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024546193A Pending JP2025506419A (ja) 2022-02-04 2023-02-03 Gjb2調節エレメント及びその使用

Country Status (11)

Country Link
US (1) US20250127928A1 (https=)
EP (1) EP4473005A4 (https=)
JP (1) JP2025506419A (https=)
KR (1) KR20240156606A (https=)
AU (1) AU2023214481A1 (https=)
CA (1) CA3250345A1 (https=)
CL (1) CL2024002306A1 (https=)
CO (1) CO2024012057A2 (https=)
IL (1) IL314705A (https=)
MX (1) MX2024009520A (https=)
WO (1) WO2023150689A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20260027327A1 (en) 2024-07-26 2026-01-29 Regeneron Pharmaceuticals, Inc. Otic drug delivery system and methods

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR20220130093A (ko) * 2019-10-30 2022-09-26 데시벨 테라퓨틱스, 인크. 오토펄린 듀얼 벡터 시스템을 사용한 감각신경성 난청을 치료하기 위한 조성물 및 방법
WO2021231808A2 (en) * 2020-05-13 2021-11-18 Akouos, Inc. Compositions and methods for treating gjb2-associated hearing loss

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