JP2024521750A5 - - Google Patents
Info
- Publication number
- JP2024521750A5 JP2024521750A5 JP2023572544A JP2023572544A JP2024521750A5 JP 2024521750 A5 JP2024521750 A5 JP 2024521750A5 JP 2023572544 A JP2023572544 A JP 2023572544A JP 2023572544 A JP2023572544 A JP 2023572544A JP 2024521750 A5 JP2024521750 A5 JP 2024521750A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- base editor
- polynucleotide
- intron
- domain
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163194431P | 2021-05-28 | 2021-05-28 | |
| US63/194,431 | 2021-05-28 | ||
| PCT/US2022/031419 WO2022251687A2 (en) | 2021-05-28 | 2022-05-27 | Compositions and methods for the self-inactivation of base editors |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024521750A JP2024521750A (ja) | 2024-06-04 |
| JP2024521750A5 true JP2024521750A5 (https=) | 2025-06-03 |
Family
ID=84230360
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023572544A Pending JP2024521750A (ja) | 2021-05-28 | 2022-05-27 | 塩基エディターの自己不活性化のための組成物及び方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20240132868A1 (https=) |
| EP (1) | EP4346840A4 (https=) |
| JP (1) | JP2024521750A (https=) |
| KR (1) | KR20240012377A (https=) |
| CN (1) | CN117729926A (https=) |
| AU (1) | AU2022280952A1 (https=) |
| CA (1) | CA3219628A1 (https=) |
| WO (1) | WO2022251687A2 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN118813611B (zh) * | 2023-04-19 | 2025-09-16 | 清华大学 | 一种基于rna核酶的dear核酸操纵系统及其应用 |
| WO2025111384A1 (en) * | 2023-11-20 | 2025-05-30 | Beam Therapeutics Inc. | Compositions and methods for altering complement activation |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9580727B1 (en) * | 2015-08-07 | 2017-02-28 | Caribou Biosciences, Inc. | Compositions and methods of engineered CRISPR-Cas9 systems using split-nexus Cas9-associated polynucleotides |
| CN110214183A (zh) * | 2016-08-03 | 2019-09-06 | 哈佛大学的校长及成员们 | 腺苷核碱基编辑器及其用途 |
| HUE070436T2 (hu) * | 2017-10-23 | 2025-06-28 | Stoke Therapeutics Inc | Antiszensz oligomerek nonszensz-mediált RNS-lebomláson alapuló állapotok és betegségek kezelésére |
| CA3084185A1 (en) * | 2017-12-06 | 2019-06-13 | Generation Bio Co. | Gene editing using a modified closed-ended dna (cedna) |
| KR20250133482A (ko) * | 2018-05-11 | 2025-09-05 | 빔 테라퓨틱스, 인크. | 프로그래밍가능한 염기 편집기 시스템을 이용하여 단일 뉴클레오티드 다형성을 편집하는 방법 |
-
2022
- 2022-05-27 CN CN202280036220.2A patent/CN117729926A/zh active Pending
- 2022-05-27 KR KR1020237039212A patent/KR20240012377A/ko active Pending
- 2022-05-27 AU AU2022280952A patent/AU2022280952A1/en active Pending
- 2022-05-27 WO PCT/US2022/031419 patent/WO2022251687A2/en not_active Ceased
- 2022-05-27 EP EP22812298.2A patent/EP4346840A4/en active Pending
- 2022-05-27 JP JP2023572544A patent/JP2024521750A/ja active Pending
- 2022-05-27 CA CA3219628A patent/CA3219628A1/en active Pending
-
2023
- 2023-11-27 US US18/519,954 patent/US20240132868A1/en active Pending
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