JP2024515344A5 - - Google Patents

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Publication number
JP2024515344A5
JP2024515344A5 JP2023564255A JP2023564255A JP2024515344A5 JP 2024515344 A5 JP2024515344 A5 JP 2024515344A5 JP 2023564255 A JP2023564255 A JP 2023564255A JP 2023564255 A JP2023564255 A JP 2023564255A JP 2024515344 A5 JP2024515344 A5 JP 2024515344A5
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JP
Japan
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JP2023564255A
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Japanese (ja)
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JPWO2022226127A5 (https=
JP2024515344A (ja
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Publication date
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Priority claimed from PCT/US2022/025648 external-priority patent/WO2022226127A1/en
Publication of JP2024515344A publication Critical patent/JP2024515344A/ja
Priority to JP2025066627A priority Critical patent/JP2025100729A/ja
Publication of JPWO2022226127A5 publication Critical patent/JPWO2022226127A5/ja
Publication of JP2024515344A5 publication Critical patent/JP2024515344A5/ja
Pending legal-status Critical Current

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JP2023564255A 2021-04-20 2022-04-20 補体成分3の発現を阻害するための組成物及び方法 Pending JP2024515344A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025066627A JP2025100729A (ja) 2021-04-20 2025-04-15 補体成分3の発現を阻害するための組成物及び方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163177254P 2021-04-20 2021-04-20
US63/177,254 2021-04-20
PCT/US2022/025648 WO2022226127A1 (en) 2021-04-20 2022-04-20 Compositions and methods for inhibiting complement component 3 expression

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025066627A Division JP2025100729A (ja) 2021-04-20 2025-04-15 補体成分3の発現を阻害するための組成物及び方法

Publications (3)

Publication Number Publication Date
JP2024515344A JP2024515344A (ja) 2024-04-09
JPWO2022226127A5 JPWO2022226127A5 (https=) 2025-04-23
JP2024515344A5 true JP2024515344A5 (https=) 2025-04-23

Family

ID=83723122

Family Applications (2)

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JP2023564255A Pending JP2024515344A (ja) 2021-04-20 2022-04-20 補体成分3の発現を阻害するための組成物及び方法
JP2025066627A Pending JP2025100729A (ja) 2021-04-20 2025-04-15 補体成分3の発現を阻害するための組成物及び方法

Family Applications After (1)

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JP2025066627A Pending JP2025100729A (ja) 2021-04-20 2025-04-15 補体成分3の発現を阻害するための組成物及び方法

Country Status (12)

Country Link
US (1) US20250002908A1 (https=)
EP (1) EP4326876A4 (https=)
JP (2) JP2024515344A (https=)
KR (1) KR20230173116A (https=)
CN (1) CN117295819A (https=)
AU (1) AU2022261922A1 (https=)
BR (1) BR112023021703A2 (https=)
CA (1) CA3177629A1 (https=)
CO (1) CO2023014681A2 (https=)
IL (1) IL307721A (https=)
MX (1) MX2023012385A (https=)
WO (1) WO2022226127A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
TWI868755B (zh) 2022-06-24 2025-01-01 丹麥商諾佛 儂迪克股份有限公司 抑制跨膜絲胺酸蛋白酶6(tmprss6)表現的組成物及方法
WO2024169907A1 (zh) * 2023-02-17 2024-08-22 苏州时安生物技术有限公司 一种调节补体C3表达的siRNA、其缀合物和药物组合物及用途
CN121488036A (zh) * 2023-07-21 2026-02-06 上海舶望制药有限公司 用于抑制补体成分3(c3)表达的组合物和方法
WO2025168134A1 (zh) * 2024-02-08 2025-08-14 北京安龙生物医药有限公司 靶向补体成分c3基因的寡核苷酸及其用途
CN121154665B (zh) * 2025-11-21 2026-02-27 天津医科大学第二医院 尿苷在防治糖尿病肾病药物开发过程中及药物中的应用

Family Cites Families (12)

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Publication number Priority date Publication date Assignee Title
EP2305812A3 (en) * 2002-11-14 2012-06-06 Dharmacon, Inc. Fuctional and hyperfunctional sirna
WO2007064846A2 (en) * 2005-11-30 2007-06-07 Intradigm Corporation COMPOSITIONS AND METHODS OF USING siRNA TO KNOCKDOWN GENE EXPRESSION AND TO IMPROVE SOLID ORGAN AND CELL TRANSPLANTATION
WO2010042755A2 (en) * 2008-10-08 2010-04-15 Chimeros Inc. Chimeric therapeutics, compositions, and methods for using same
SG10201804960RA (en) * 2013-12-12 2018-07-30 Alnylam Pharmaceuticals Inc Complement component irna compositions and methods of use thereof
RU2019113301A (ru) * 2016-10-17 2020-11-17 Апеллис Фармасьютикалс, Инк. Комбинированная терапия для ингибирования с3
AU2018360697A1 (en) * 2017-11-01 2020-05-14 Alnylam Pharmaceuticals, Inc. Complement component C3 iRNA compositions and methods of use thereof
CA3119234A1 (en) * 2018-11-23 2020-05-28 Silence Therapeutics Gmbh Nucleic acids for inhibiting expression of c3 in a cell
EP4022060A1 (en) * 2019-08-27 2022-07-06 Silence Therapeutics GmbH Nucleic acids for inhibiting expression of c3 in a cell
TW202134435A (zh) * 2019-10-22 2021-09-16 美商阿尼拉製藥公司 補體成分c3 irna組成物及其使用方法
CN115335524A (zh) * 2020-02-14 2022-11-11 阿佩利斯制药有限公司 用于补体抑制的rna
MX2023008469A (es) * 2021-01-22 2023-11-22 Alnylam Pharmaceuticals Inc Oligonucleotidos de doble hebra modificados.
WO2022251484A1 (en) * 2021-05-26 2022-12-01 Apellis Pharmaceuticals, Inc. Treatment of complement-mediated disorders

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