JP2024514160A5 - - Google Patents

Info

Publication number
JP2024514160A5
JP2024514160A5 JP2023562865A JP2023562865A JP2024514160A5 JP 2024514160 A5 JP2024514160 A5 JP 2024514160A5 JP 2023562865 A JP2023562865 A JP 2023562865A JP 2023562865 A JP2023562865 A JP 2023562865A JP 2024514160 A5 JP2024514160 A5 JP 2024514160A5
Authority
JP
Japan
Application number
JP2023562865A
Other languages
Japanese (ja)
Other versions
JP2024514160A (ja
JPWO2022221574A5 (https=
Filing date
Publication date
Priority claimed from US17/231,963 external-priority patent/US12275941B2/en
Application filed filed Critical
Publication of JP2024514160A publication Critical patent/JP2024514160A/ja
Publication of JP2024514160A5 publication Critical patent/JP2024514160A5/ja
Publication of JPWO2022221574A5 publication Critical patent/JPWO2022221574A5/ja
Pending legal-status Critical Current

Links

JP2023562865A 2021-04-15 2022-04-14 ダイナミン1バリアントの発現の阻害のための産物及び方法 Pending JP2024514160A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US17/231,963 2021-04-15
US17/231,963 US12275941B2 (en) 2021-04-15 2021-04-15 Products and methods for inhibition of expression of dynamin-1 variants
PCT/US2022/024885 WO2022221574A2 (en) 2021-04-15 2022-04-14 Products and methods for inhibition of expression of dynamin-1 variants

Publications (3)

Publication Number Publication Date
JP2024514160A JP2024514160A (ja) 2024-03-28
JP2024514160A5 true JP2024514160A5 (https=) 2025-04-04
JPWO2022221574A5 JPWO2022221574A5 (https=) 2025-04-04

Family

ID=83602203

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023562865A Pending JP2024514160A (ja) 2021-04-15 2022-04-14 ダイナミン1バリアントの発現の阻害のための産物及び方法

Country Status (4)

Country Link
US (2) US12275941B2 (https=)
EP (1) EP4322964A4 (https=)
JP (1) JP2024514160A (https=)
WO (1) WO2022221574A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025226343A1 (en) 2024-04-26 2025-10-30 Research Institute At Nationwide Children's Hospital Products and methods to inhibit expression of dynamin-1 variants and replace dynamin-1

Family Cites Families (26)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5173414A (en) 1990-10-30 1992-12-22 Applied Immune Sciences, Inc. Production of recombinant adeno-associated virus vectors
PT733103E (pt) 1993-11-09 2004-07-30 Targeted Genetics Corp Criacao de elevados titulos de vectores de aav recombinantes
PT728214E (pt) 1993-11-09 2004-11-30 Ohio Med College Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado
US5658785A (en) 1994-06-06 1997-08-19 Children's Hospital, Inc. Adeno-associated virus materials and methods
US5856152A (en) 1994-10-28 1999-01-05 The Trustees Of The University Of Pennsylvania Hybrid adenovirus-AAV vector and methods of use therefor
AU707866B2 (en) 1994-12-06 1999-07-22 Targeted Genetics Corporation Packaging cell lines for generation of high titers of recombinant AAV vectors
FR2737730B1 (fr) 1995-08-10 1997-09-05 Pasteur Merieux Serums Vacc Procede de purification de virus par chromatographie
AU722196B2 (en) 1995-08-30 2000-07-27 Genzyme Corporation Chromatographic purification of adenovirus and AAV
EP1983057A3 (en) 1995-09-08 2009-01-07 Genzyme Corporation Improved AAV vectors for gene therapy
US5910434A (en) 1995-12-15 1999-06-08 Systemix, Inc. Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant
EP0932418B1 (en) 1996-09-06 2007-12-05 The Trustees Of The University Of Pennsylvania Method for recombinant adeno-associated virus-directed gene therapy
US6566118B1 (en) 1997-09-05 2003-05-20 Targeted Genetics Corporation Methods for generating high titer helper-free preparations of released recombinant AAV vectors
JP2001514845A (ja) 1997-09-05 2001-09-18 ターゲティッド ジェネティクス コーポレイション 組換えaavベクターの高力価ヘルパーなし調製物を生成するための方法
US6258595B1 (en) 1999-03-18 2001-07-10 The Trustees Of The University Of Pennsylvania Compositions and methods for helper-free production of recombinant adeno-associated viruses
CA2406743A1 (en) 2000-04-28 2001-11-08 The Trustees Of The University Of Pennsylvania Recombinant aav vectors with aav5 capsids and aav5 vectors pseudotyped in heterologous capsids
AU2002248297A1 (en) 2001-01-05 2002-07-16 Children's Hospital, Inc. Aav2 vectors and methods
US20070225363A1 (en) * 2003-11-21 2007-09-27 The University Of Newcastle Research Associates Ltd. Methods and Agents for Inhibiting Dynamin-Dependent Endocytosis
WO2007056435A2 (en) 2005-11-08 2007-05-18 The General Hospital Corporation Dynamin mediated diseases and associated methods and products
US20080306007A1 (en) * 2007-04-30 2008-12-11 Newcastle Innovation Limited Agents for prophylaxis or treatment of neurological related diseases and conditions
US20110081362A1 (en) * 2008-01-31 2011-04-07 The Brigham And Women's Hospital, Inc. Treatment of cancer
US9434928B2 (en) 2011-11-23 2016-09-06 Nationwide Children's Hospital, Inc. Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides
BR112018070249A2 (pt) * 2016-04-02 2019-01-29 Research Institute At Nationwide Children's Hospital sistema promotor de u6 modificada para expressão específica de tecido
US10947540B2 (en) 2016-11-29 2021-03-16 Association Institut De Myologie Allele-specific silencing therapy for Dynamin 2-related diseases
EP3610016A1 (en) 2017-04-10 2020-02-19 Genethon Antisense targeting dynamin 2 and use for the treatment of centronuclear myopathies and neuropathies
WO2018200674A1 (en) 2017-04-26 2018-11-01 Mitobridge, Inc. Dynamin-1-like protein inhibitors
BR112020014425A2 (pt) 2018-01-15 2020-12-29 Ionis Pharmaceuticals, Inc. Moduladores de expressão de dnm2

Similar Documents

Publication Publication Date Title
JP2024514160A5 (https=)
CL2025003982A1 (es) Pieza de molde y estación de moldeo
BR102023014872A2 (https=)
BR202022009269U2 (https=)
BR202022005961U2 (https=)
BR202022001779U2 (https=)
BR202022000931U2 (https=)
BY13167U (https=)
BY13162U (https=)
CN307049103S (https=)
CN307048383S (https=)
CN307047452S (https=)
CN307045783S (https=)
CN307044229S (https=)
BY23965C1 (https=)
BY23963C1 (https=)
BY13176U (https=)
BY13175U (https=)
BY13143U (https=)
BY13172U (https=)
BY13170U (https=)
BY13142U (https=)
BY13169U (https=)
BY13168U (https=)
CN307049275S (https=)