JP2022516515A5 - - Google Patents

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Publication number
JP2022516515A5
JP2022516515A5 JP2021538230A JP2021538230A JP2022516515A5 JP 2022516515 A5 JP2022516515 A5 JP 2022516515A5 JP 2021538230 A JP2021538230 A JP 2021538230A JP 2021538230 A JP2021538230 A JP 2021538230A JP 2022516515 A5 JP2022516515 A5 JP 2022516515A5
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JP
Japan
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JP2021538230A
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Japanese (ja)
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JP2022516515A (ja
JPWO2020142479A5 (https=
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Priority claimed from PCT/US2019/069048 external-priority patent/WO2020142479A1/en
Publication of JP2022516515A publication Critical patent/JP2022516515A/ja
Publication of JP2022516515A5 publication Critical patent/JP2022516515A5/ja
Publication of JPWO2020142479A5 publication Critical patent/JPWO2020142479A5/ja
Priority to JP2024219757A priority Critical patent/JP2025032342A/ja
Pending legal-status Critical Current

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JP2021538230A 2018-12-31 2019-12-31 Rna標的化crispr-cas13bを使用するdux4 rna発現停止 Pending JP2022516515A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024219757A JP2025032342A (ja) 2018-12-31 2024-12-16 Rna標的化crispr-cas13bを使用するdux4 rna発現停止

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862786670P 2018-12-31 2018-12-31
US62/786,670 2018-12-31
PCT/US2019/069048 WO2020142479A1 (en) 2018-12-31 2019-12-31 Dux4 rna silencing using rna targeting crispr-cas13b

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024219757A Division JP2025032342A (ja) 2018-12-31 2024-12-16 Rna標的化crispr-cas13bを使用するdux4 rna発現停止

Publications (3)

Publication Number Publication Date
JP2022516515A JP2022516515A (ja) 2022-02-28
JP2022516515A5 true JP2022516515A5 (https=) 2023-01-05
JPWO2020142479A5 JPWO2020142479A5 (https=) 2023-01-05

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ID=69376003

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021538230A Pending JP2022516515A (ja) 2018-12-31 2019-12-31 Rna標的化crispr-cas13bを使用するdux4 rna発現停止
JP2024219757A Pending JP2025032342A (ja) 2018-12-31 2024-12-16 Rna標的化crispr-cas13bを使用するdux4 rna発現停止

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024219757A Pending JP2025032342A (ja) 2018-12-31 2024-12-16 Rna標的化crispr-cas13bを使用するdux4 rna発現停止

Country Status (8)

Country Link
US (1) US12545909B2 (https=)
EP (1) EP3906308A1 (https=)
JP (2) JP2022516515A (https=)
KR (1) KR20210110345A (https=)
AU (1) AU2019419494B2 (https=)
CA (1) CA3124963A1 (https=)
IL (1) IL284447B2 (https=)
WO (1) WO2020142479A1 (https=)

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US20220193250A1 (en) 2018-08-02 2022-06-23 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
US12018087B2 (en) 2018-08-02 2024-06-25 Dyne Therapeutics, Inc. Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
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