JP2023536921A5 - - Google Patents

Info

Publication number
JP2023536921A5
JP2023536921A5 JP2023507620A JP2023507620A JP2023536921A5 JP 2023536921 A5 JP2023536921 A5 JP 2023536921A5 JP 2023507620 A JP2023507620 A JP 2023507620A JP 2023507620 A JP2023507620 A JP 2023507620A JP 2023536921 A5 JP2023536921 A5 JP 2023536921A5
Authority
JP
Japan
Prior art keywords
cardiomyopathy
seq
syndrome
nucleic acid
heart failure
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023507620A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023536921A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/044650 external-priority patent/WO2022031914A2/en
Publication of JP2023536921A publication Critical patent/JP2023536921A/ja
Publication of JP2023536921A5 publication Critical patent/JP2023536921A5/ja
Pending legal-status Critical Current

Links

JP2023507620A 2020-08-05 2021-08-05 心障害およびうっ血性心不全を処置する方法ならびにaavベクターを投与する方法 Pending JP2023536921A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063061342P 2020-08-05 2020-08-05
US63/061,342 2020-08-05
US202163214119P 2021-06-23 2021-06-23
US63/214,119 2021-06-23
PCT/US2021/044650 WO2022031914A2 (en) 2020-08-05 2021-08-05 Methods of treating cardiac disorders and congestive heart failure and administering aav vectors

Publications (2)

Publication Number Publication Date
JP2023536921A JP2023536921A (ja) 2023-08-30
JP2023536921A5 true JP2023536921A5 (https=) 2024-08-13

Family

ID=80120133

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023507620A Pending JP2023536921A (ja) 2020-08-05 2021-08-05 心障害およびうっ血性心不全を処置する方法ならびにaavベクターを投与する方法

Country Status (8)

Country Link
US (1) US20230340528A1 (https=)
EP (1) EP4192580A4 (https=)
JP (1) JP2023536921A (https=)
CN (1) CN116406297A (https=)
AU (1) AU2021320244A1 (https=)
CA (1) CA3188398A1 (https=)
IL (1) IL300367A (https=)
WO (1) WO2022031914A2 (https=)

Families Citing this family (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3947700A4 (en) 2019-04-01 2023-01-04 Tenaya Therapeutics, Inc. Adeno-associated virus with engineered capsid
BR112023006305A2 (pt) 2020-10-09 2023-05-09 Tenaya Therapeutics Inc Métodos e composições de terapia gênica com placofilina-2
AU2022297795A1 (en) * 2021-06-23 2024-01-04 AskBio Inc. Regulatory nucleic acid sequences
WO2023178338A2 (en) * 2022-03-18 2023-09-21 University Of Florida Research Foundation, Incorporated Methods and compositions for treating tmem43 related cardiomyopathy with a viral vector
JP2025512405A (ja) * 2022-04-11 2025-04-17 テナヤ セラピューティクス, インコーポレイテッド プラコフィリン2遺伝子治療の処置の方法
CN116256523B (zh) * 2023-02-02 2023-09-12 香港大学深圳医院 生物标志物在制备用于糖尿病患者HFpEF检测试剂中的应用
IL322735A (en) * 2023-02-13 2025-10-01 Astrazeneca Ireland Ltd Nucleic acids encoding BCL2-associated athenogen 3 (BAG3) for gene therapy
CN116644347B (zh) * 2023-05-23 2025-11-28 珠海市康利莱医疗器械有限公司 一种用于风湿性瓣膜病的血清差异多肽检测系统
EP4719440A1 (en) * 2023-06-01 2026-04-08 Alkahest, Inc. Compositions of blood plasma fractions and blood plasma subfractions and their use in treatment of disease
TW202525313A (zh) * 2023-09-06 2025-07-01 瑞士商迪納柯公司 用aav基因治療載體及治療調配物治療肥厚性心肌病之方法
WO2025259575A1 (en) * 2024-06-10 2025-12-18 Asklepios Biopharmaceutical, Inc. Methods and compositions for treatment of duchenne muscular dystrophy

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN101056539B (zh) * 2004-09-09 2012-12-12 综合医院公司 调节心脏细胞中的磷酸酶活性
BRPI0912559A2 (pt) * 2008-05-16 2015-10-13 Corthera Inc método de tratar insuficiência cardíaca crônica
EP4081643A1 (en) * 2019-12-24 2022-11-02 Asklepios Biopharmaceutical, Inc. Regulatory nucleic acid sequences

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