JP2023510590A5 - - Google Patents

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Publication number
JP2023510590A5
JP2023510590A5 JP2022543381A JP2022543381A JP2023510590A5 JP 2023510590 A5 JP2023510590 A5 JP 2023510590A5 JP 2022543381 A JP2022543381 A JP 2022543381A JP 2022543381 A JP2022543381 A JP 2022543381A JP 2023510590 A5 JP2023510590 A5 JP 2023510590A5
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JP
Japan
Application number
JP2022543381A
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Japanese (ja)
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JP2023510590A (ja
JP7846625B2 (ja
JPWO2021146591A5 (https=
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Priority claimed from PCT/US2021/013689 external-priority patent/WO2021146591A2/en
Publication of JP2023510590A publication Critical patent/JP2023510590A/ja
Publication of JPWO2021146591A5 publication Critical patent/JPWO2021146591A5/ja
Publication of JP2023510590A5 publication Critical patent/JP2023510590A5/ja
Priority to JP2025195186A priority Critical patent/JP2026032042A/ja
Application granted granted Critical
Publication of JP7846625B2 publication Critical patent/JP7846625B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2022543381A 2020-01-17 2021-01-15 組換えaavの産生 Active JP7846625B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025195186A JP2026032042A (ja) 2020-01-17 2025-11-14 組換えaavの産生

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062962911P 2020-01-17 2020-01-17
US62/962,911 2020-01-17
PCT/US2021/013689 WO2021146591A2 (en) 2020-01-17 2021-01-15 Recombinant aav production

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025195186A Division JP2026032042A (ja) 2020-01-17 2025-11-14 組換えaavの産生

Publications (4)

Publication Number Publication Date
JP2023510590A JP2023510590A (ja) 2023-03-14
JPWO2021146591A5 JPWO2021146591A5 (https=) 2024-01-23
JP2023510590A5 true JP2023510590A5 (https=) 2024-01-23
JP7846625B2 JP7846625B2 (ja) 2026-04-15

Family

ID=76864730

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022543381A Active JP7846625B2 (ja) 2020-01-17 2021-01-15 組換えaavの産生
JP2025195186A Pending JP2026032042A (ja) 2020-01-17 2025-11-14 組換えaavの産生

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025195186A Pending JP2026032042A (ja) 2020-01-17 2025-11-14 組換えaavの産生

Country Status (8)

Country Link
US (1) US20230048994A1 (https=)
EP (1) EP4090750A4 (https=)
JP (2) JP7846625B2 (https=)
CN (1) CN115315518A (https=)
AU (1) AU2021207683A1 (https=)
CA (1) CA3162520A1 (https=)
IL (1) IL294775A (https=)
WO (1) WO2021146591A2 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4189077A1 (en) 2020-07-30 2023-06-07 Shape Therapeutics Inc. Stable cell lines for inducible production of raav virions
AU2022373653A1 (en) 2021-10-18 2024-05-02 Regeneron Pharmaceuticals, Inc. Eukaryotic cells comprising adenovirus-associated virus polynucleotides
WO2024129882A1 (en) * 2022-12-14 2024-06-20 Astellas Gene Therapies, Inc. Compositions and methods for improved production of adeno-associated viral particles
AU2024223271A1 (en) * 2023-02-17 2025-09-18 Synplogen Co., Ltd. Itr-rep gene complex
EP4527938A1 (en) * 2023-09-22 2025-03-26 LenioBio GmbH Method for cell-free polypeptide synthesis

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6995006B2 (en) * 1997-09-05 2006-02-07 Targeted Genetics Corporation Methods for generating high titer helper-free preparations of released recombinant AAV vectors
EP2848253A1 (en) * 2006-06-19 2015-03-18 Asklepios Biopharmaceutical, Inc. Modified factor VIII and factor IX genes and vectors for gene therapy
WO2008105931A2 (en) * 2006-09-15 2008-09-04 Medimmune Vaccines, Inc. Mdck cell lines supporting viral growth to high titers and bioreactor process using the same
GB0901593D0 (en) * 2009-01-30 2009-03-11 Touchlight Genetics Ltd Production of closed linear DNA
US9441206B2 (en) * 2011-10-28 2016-09-13 The University Of North Carolina At Chapel Hill Cell line for production of adeno-associated virus
EP3039129B1 (en) * 2013-08-30 2018-06-27 Amgen Inc. High titer recombinant aav vector production in adherent and suspension cells
AU2016362317B2 (en) * 2015-12-01 2023-03-16 Spark Therapeutics, Inc. Scalable methods for producing recombinant Adeno-Associated Viral (AAV) vector in serum-free suspension cell culture system suitable for clinical use
EP3810782A2 (en) * 2018-06-22 2021-04-28 Asklepios Biopharmaceutical, Inc. Vectors for gene delivery that persist within cells

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