JP2023509118A5 - - Google Patents
Info
- Publication number
- JP2023509118A5 JP2023509118A5 JP2022539145A JP2022539145A JP2023509118A5 JP 2023509118 A5 JP2023509118 A5 JP 2023509118A5 JP 2022539145 A JP2022539145 A JP 2022539145A JP 2022539145 A JP2022539145 A JP 2022539145A JP 2023509118 A5 JP2023509118 A5 JP 2023509118A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- crm
- functional variant
- sequence number
- cre0035
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GBGB1919269.9A GB201919269D0 (en) | 2019-12-24 | 2019-12-24 | Regulatory nucleic acid sequences |
| GB1919269.9 | 2019-12-24 | ||
| GBGB2012192.7A GB202012192D0 (en) | 2020-08-05 | 2020-08-05 | Regulatory nucleic acid sequences |
| GB2012192.7 | 2020-08-05 | ||
| PCT/GB2020/053371 WO2021130503A1 (en) | 2019-12-24 | 2020-12-24 | Regulatory nucleic acid sequences |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023509118A JP2023509118A (ja) | 2023-03-07 |
| JP2023509118A5 true JP2023509118A5 (https=) | 2024-01-05 |
Family
ID=74130280
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022539145A Pending JP2023509118A (ja) | 2019-12-24 | 2020-12-24 | 調節性核酸配列 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20230233710A1 (https=) |
| EP (1) | EP4081643A1 (https=) |
| JP (1) | JP2023509118A (https=) |
| KR (1) | KR20220119703A (https=) |
| CN (1) | CN115151646A (https=) |
| AU (1) | AU2020412375A1 (https=) |
| CA (1) | CA3161735A1 (https=) |
| IL (1) | IL294238A (https=) |
| WO (1) | WO2021130503A1 (https=) |
| ZA (1) | ZA202207849B (https=) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP4103214B1 (en) | 2020-02-13 | 2026-04-29 | Tenaya Therapeutics, Inc. | Gene therapy vectors for treating heart disease |
| EP4192580A4 (en) * | 2020-08-05 | 2025-06-18 | AskBio Inc. | Methods for treating heart disease and congestive heart failure and administration of AAV vectors |
| AU2022297795A1 (en) * | 2021-06-23 | 2024-01-04 | AskBio Inc. | Regulatory nucleic acid sequences |
| KR20250012749A (ko) * | 2022-04-22 | 2025-01-24 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 b-세포 림프종 2-관련 안타노겐 3(bag3) 유전자 요법 |
| CN115948403B (zh) * | 2022-12-30 | 2023-09-15 | 广州派真生物技术有限公司 | 在哺乳动物肌肉中特异性启动基因的启动子序列及其应用 |
| AU2024406119A1 (en) * | 2023-12-18 | 2026-04-02 | F. Hoffmann-La Roche Ag | Skeletal muscle-specific promoters |
Family Cites Families (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4683195A (en) | 1986-01-30 | 1987-07-28 | Cetus Corporation | Process for amplifying, detecting, and/or-cloning nucleic acid sequences |
| ES2261489T3 (es) | 2000-10-13 | 2006-11-16 | Chiron Corporation | Fragmentos de intron a de citomegalovirus. |
| US8106180B2 (en) | 2003-08-07 | 2012-01-31 | Whitehead Institute For Biomedical Research | Methods and products for expression of micro RNAs |
| US20050142581A1 (en) | 2003-09-04 | 2005-06-30 | Griffey Richard H. | Microrna as ligands and target molecules |
| WO2005056761A2 (en) | 2003-12-05 | 2005-06-23 | Massachusetts Institute Of Technology | REAGENTS AND METHODS FOR IDENTIFICATION OF RNAi PATHWAY GENES AND CHEMICAL MODULATORS OF RNAi |
| KR100614827B1 (ko) | 2004-05-06 | 2006-08-25 | 재단법인서울대학교산학협력재단 | 양방향 은닉 마코프 모델을 이용한 완숙한마이크로알엔에이 위치예측방법 및 이를 구현하기 위한컴퓨터 프로그램을 기록한 저장매체 |
| WO2011051450A1 (en) * | 2009-10-29 | 2011-05-05 | Vib Vzw | Cardiac-specific nucleic acid regulatory elements and methods and use thereof |
| CN103074373A (zh) * | 2011-10-26 | 2013-05-01 | 南京医科大学 | 肌肉组织特异性表达Follistatin以提高牛瘦肉率的转基因载体 |
| CN102747082B (zh) * | 2011-12-29 | 2014-06-18 | 华中农业大学 | 猪肌肉特异性itgb1bp2启动子及其应用 |
| US20190032079A1 (en) * | 2015-08-03 | 2019-01-31 | Myodopa Limited | Systemic synthesis and regulation of l-dopa |
| CN105063079A (zh) * | 2015-08-15 | 2015-11-18 | 内蒙古大学 | 一种三顺反子肌肉特异双向共表达基因转移体及制备方法 |
| US20170253927A1 (en) * | 2016-03-01 | 2017-09-07 | Washington State University | Heritable epigenetic modifications as markers of chemotherapy exposure |
| CN108018311A (zh) * | 2016-11-04 | 2018-05-11 | 中国科学院上海生命科学研究院 | 通过基因编辑特异靶向肌肉组织mstn治疗恶病质 |
| EP3596112A2 (en) * | 2017-03-17 | 2020-01-22 | Newcastle University | Adeno-associated virus vector delivery of a fragment of micro-dystrophin to treat muscular dystrophy |
-
2020
- 2020-12-24 EP EP20838277.0A patent/EP4081643A1/en active Pending
- 2020-12-24 US US17/788,679 patent/US20230233710A1/en active Pending
- 2020-12-24 WO PCT/GB2020/053371 patent/WO2021130503A1/en not_active Ceased
- 2020-12-24 CA CA3161735A patent/CA3161735A1/en active Pending
- 2020-12-24 JP JP2022539145A patent/JP2023509118A/ja active Pending
- 2020-12-24 IL IL294238A patent/IL294238A/en unknown
- 2020-12-24 KR KR1020227025726A patent/KR20220119703A/ko active Pending
- 2020-12-24 CN CN202080097425.2A patent/CN115151646A/zh active Pending
- 2020-12-24 AU AU2020412375A patent/AU2020412375A1/en active Pending
-
2022
- 2022-07-14 ZA ZA2022/07849A patent/ZA202207849B/en unknown
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