JP2022553309A5 - - Google Patents

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Publication number
JP2022553309A5
JP2022553309A5 JP2022523415A JP2022523415A JP2022553309A5 JP 2022553309 A5 JP2022553309 A5 JP 2022553309A5 JP 2022523415 A JP2022523415 A JP 2022523415A JP 2022523415 A JP2022523415 A JP 2022523415A JP 2022553309 A5 JP2022553309 A5 JP 2022553309A5
Authority
JP
Japan
Prior art keywords
nucleic acid
vector
seq
pharmaceutical composition
nucleotide sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022523415A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022553309A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/056862 external-priority patent/WO2021081203A1/en
Publication of JP2022553309A publication Critical patent/JP2022553309A/ja
Publication of JP2022553309A5 publication Critical patent/JP2022553309A5/ja
Pending legal-status Critical Current

Links

JP2022523415A 2019-10-22 2020-10-22 加齢黄斑変性ならびに他の眼疾患および障害の治療のためのアデノ随伴ウイルス(aav)ベクター Pending JP2022553309A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962924338P 2019-10-22 2019-10-22
US62/924,338 2019-10-22
PCT/US2020/056862 WO2021081203A1 (en) 2019-10-22 2020-10-22 Adeno-associated virus (aav)vectors for the treatment of age-related macular degeneration and other ocular diseases and disorders

Publications (2)

Publication Number Publication Date
JP2022553309A JP2022553309A (ja) 2022-12-22
JP2022553309A5 true JP2022553309A5 (https=) 2023-10-30

Family

ID=75586875

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022523415A Pending JP2022553309A (ja) 2019-10-22 2020-10-22 加齢黄斑変性ならびに他の眼疾患および障害の治療のためのアデノ随伴ウイルス(aav)ベクター

Country Status (10)

Country Link
US (1) US20210123076A1 (https=)
EP (1) EP4048321A4 (https=)
JP (1) JP2022553309A (https=)
KR (1) KR20230019062A (https=)
CN (1) CN115175706A (https=)
AU (1) AU2020371663A1 (https=)
CA (1) CA3158517A1 (https=)
IL (1) IL292379A (https=)
MX (1) MX2022004770A (https=)
WO (1) WO2021081203A1 (https=)

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7745389B2 (en) * 2005-02-14 2010-06-29 University Of Iowa Research Foundation Methods for treatment of age-related macular degeneration
CN101160412A (zh) * 2005-02-14 2008-04-09 爱荷华大学研究基金会 治疗和诊断年龄相关性黄斑变性的方法和试剂
WO2007127428A2 (en) * 2006-04-28 2007-11-08 University Of Florida Research Foundation, Inc. Double-stranded/self-complementary vectors with a truncated cba promoter and methods of gene delivery
EP2479284B1 (en) * 2006-07-13 2017-09-20 University of Iowa Research Foundation Methods and reagents for treatment and diagnosis of vascular disorders and age-related macular degeneration
CN108291216B (zh) * 2015-09-24 2022-09-16 宾夕法尼亚州大学信托人 用于治疗补体介导的疾病的组合物和方法
WO2017114401A1 (zh) * 2015-12-31 2017-07-06 江苏匡亚生物医药科技有限公司 具有补体调节活性的重组补体因子h-免疫球蛋白融合蛋白及其制备方法与应用
GB201706808D0 (en) * 2017-04-28 2017-06-14 Univ Newcastle Modified complement proteins and uses thereof
EP3697920A4 (en) * 2017-10-20 2022-03-02 Gemini Therapeutics, Inc. COMPOSITIONS AND METHODS FOR THE TREATMENT OF AGE-RELATED MACULAR DEGENERATION

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