JP2022552940A5 - - Google Patents

Info

Publication number
JP2022552940A5
JP2022552940A5 JP2022517729A JP2022517729A JP2022552940A5 JP 2022552940 A5 JP2022552940 A5 JP 2022552940A5 JP 2022517729 A JP2022517729 A JP 2022517729A JP 2022517729 A JP2022517729 A JP 2022517729A JP 2022552940 A5 JP2022552940 A5 JP 2022552940A5
Authority
JP
Japan
Prior art keywords
nucleic acid
small molecule
thrombocytopenia
modification
molecule
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022517729A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022552940A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/CN2020/116227 external-priority patent/WO2021052470A1/zh
Publication of JP2022552940A publication Critical patent/JP2022552940A/ja
Publication of JP2022552940A5 publication Critical patent/JP2022552940A5/ja
Pending legal-status Critical Current

Links

JP2022517729A 2019-09-20 2020-09-18 血小板減少症を治療するための核酸分子及びその応用 Pending JP2022552940A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
CN201910891508.8 2019-09-20
CN201910891508 2019-09-20
PCT/CN2020/116227 WO2021052470A1 (zh) 2019-09-20 2020-09-18 用于治疗血小板减少症的核酸分子及其应用

Publications (2)

Publication Number Publication Date
JP2022552940A JP2022552940A (ja) 2022-12-21
JP2022552940A5 true JP2022552940A5 (cg-RX-API-DMAC10.html) 2023-09-25

Family

ID=74883124

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022517729A Pending JP2022552940A (ja) 2019-09-20 2020-09-18 血小板減少症を治療するための核酸分子及びその応用

Country Status (12)

Country Link
US (1) US20230212565A1 (cg-RX-API-DMAC10.html)
EP (1) EP4036232A4 (cg-RX-API-DMAC10.html)
JP (1) JP2022552940A (cg-RX-API-DMAC10.html)
KR (1) KR20220070206A (cg-RX-API-DMAC10.html)
CN (1) CN114585738A (cg-RX-API-DMAC10.html)
AU (1) AU2020349991A1 (cg-RX-API-DMAC10.html)
BR (1) BR112022005028A2 (cg-RX-API-DMAC10.html)
CA (1) CA3148158A1 (cg-RX-API-DMAC10.html)
CO (1) CO2022004857A2 (cg-RX-API-DMAC10.html)
PE (1) PE20220604A1 (cg-RX-API-DMAC10.html)
TW (1) TW202126808A (cg-RX-API-DMAC10.html)
WO (1) WO2021052470A1 (cg-RX-API-DMAC10.html)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN111849968A (zh) 2019-04-30 2020-10-30 中美瑞康核酸技术(南通)研究院有限公司 寡核苷酸分子及其在急性间歇性卟啉症治疗中的应用
AU2024255186A1 (en) * 2023-04-12 2025-10-30 Alnylam Pharmaceuticals, Inc. Formulations for oligonucleotide delivery

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6270989B1 (en) * 1991-11-05 2001-08-07 Transkaryotic Therapies, Inc. Protein production and delivery
GB2285446B (en) * 1994-01-03 1999-07-28 Genentech Inc Thrombopoietin
JP5362350B2 (ja) * 2005-04-15 2013-12-11 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 小分子活性化rna分子及び使用方法
CA2629664A1 (en) * 2005-11-17 2007-08-02 Board Of Regents, The University Of Texas System Modulation of gene expression by oligomers targeted to chromosomal dna
KR20220038506A (ko) 2009-06-10 2022-03-28 알닐람 파마슈티칼스 인코포레이티드 향상된 지질 조성물
GB201010557D0 (en) * 2010-06-23 2010-08-11 Mina Therapeutics Ltd RNA molecules and uses thereof
WO2012175958A1 (en) * 2011-06-21 2012-12-27 Mina Therapeutics Limited Albumin production and cell proliferation
CN106032532A (zh) * 2015-03-17 2016-10-19 中国医学科学院北京协和医院 一种小激活rna及其制备方法和应用
CN108291228A (zh) * 2015-04-22 2018-07-17 米纳治疗有限公司 C/EBPαSARNA组合物和使用方法
EP3286318A2 (en) * 2015-04-22 2018-02-28 Mina Therapeutics Limited Sarna compositions and methods of use
WO2017106283A1 (en) * 2015-12-14 2017-06-22 Cold Spring Harbor Laboratory Compositions and methods for treatment of liver diseases
CN106480028B (zh) * 2016-10-12 2019-04-05 上海市第七人民医院 TPO基因的saRNA分子及其应用

Similar Documents

Publication Publication Date Title
ES2204913T3 (es) Metodo para formacion de oligonucleotidos.
Lu et al. Multifunctional DNA origami nanoplatforms for drug delivery
JP2007503474A5 (cg-RX-API-DMAC10.html)
JP2005517438A5 (cg-RX-API-DMAC10.html)
JP2006502694A5 (cg-RX-API-DMAC10.html)
JP2014527401A5 (cg-RX-API-DMAC10.html)
JP2005517433A5 (cg-RX-API-DMAC10.html)
JP2005517436A5 (cg-RX-API-DMAC10.html)
JP2005517432A5 (cg-RX-API-DMAC10.html)
JP2007529224A5 (cg-RX-API-DMAC10.html)
SK6042002A3 (en) High order nucleic acid based structures
WO2025157271A1 (zh) 一种抑制f11基因表达的核酸分子
JP2023521042A (ja) 操作されたオリゴヌクレオチドを使用する標的化された阻害
WO2015099122A1 (ja) 遺伝子発現制御のための人工ミミックmiRNAおよびその用途
CN112996913A (zh) 寡聚核酸分子及其应用
KR100929699B1 (ko) 다수 표적 유전자들을 제어하는 간섭 유도 rna들 및그들의 제조방법
CN113249380A (zh) 靶向covid-19新冠病毒的反义寡核苷酸、natac嵌合分子及其应用
JP2022536945A5 (cg-RX-API-DMAC10.html)
CN104919059B (zh) 旋转性隔离的翻译元件
ES2421314T3 (es) Constructos de ADN para la inhibición específica de la expresión génica mediante interferencia de ARN
TWI606058B (zh) Nucleic acid complex and nucleic acid polysaccharide complex
CN102876658A (zh) 一种大规模合成长链核酸分子的方法
CN118460655B (zh) 抑制FXI基因表达的siRNA的制备方法
CN118460649B (zh) 一种Vutrisiran的制备方法
EP4036232A1 (en) Nucleic acid molecule for treating immune thrombocytopenia and application thereof