JP2021526834A5 - - Google Patents

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Publication number
JP2021526834A5
JP2021526834A5 JP2020569147A JP2020569147A JP2021526834A5 JP 2021526834 A5 JP2021526834 A5 JP 2021526834A5 JP 2020569147 A JP2020569147 A JP 2020569147A JP 2020569147 A JP2020569147 A JP 2020569147A JP 2021526834 A5 JP2021526834 A5 JP 2021526834A5
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JP
Japan
Prior art keywords
sequence
sequence number
recombinant aav2
aav2 vector
vector according
Prior art date
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Application number
JP2020569147A
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English (en)
Japanese (ja)
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JP2021526834A (ja
JP7470057B2 (ja
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Priority claimed from PCT/US2019/036487 external-priority patent/WO2019241206A1/en
Publication of JP2021526834A publication Critical patent/JP2021526834A/ja
Publication of JP2021526834A5 publication Critical patent/JP2021526834A5/ja
Application granted granted Critical
Publication of JP7470057B2 publication Critical patent/JP7470057B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2020569147A 2018-06-11 2019-06-11 組み換えaavベクター及びその使用方法 Active JP7470057B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862683501P 2018-06-11 2018-06-11
US62/683,501 2018-06-11
PCT/US2019/036487 WO2019241206A1 (en) 2018-06-11 2019-06-11 Recombinant aav vectors and methods of using the same

Publications (3)

Publication Number Publication Date
JP2021526834A JP2021526834A (ja) 2021-10-11
JP2021526834A5 true JP2021526834A5 (https=) 2022-06-15
JP7470057B2 JP7470057B2 (ja) 2024-04-17

Family

ID=67138055

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020569147A Active JP7470057B2 (ja) 2018-06-11 2019-06-11 組み換えaavベクター及びその使用方法

Country Status (8)

Country Link
US (1) US20210189424A1 (https=)
EP (1) EP3802840A1 (https=)
JP (1) JP7470057B2 (https=)
KR (1) KR102946006B1 (https=)
CN (1) CN112384625A (https=)
AU (1) AU2019286386B2 (https=)
CA (1) CA3103231A1 (https=)
WO (1) WO2019241206A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN113528510A (zh) 2018-06-29 2021-10-22 武汉纽福斯生物科技有限公司 治疗遗传性视神经病变的组合物和方法
SG11202101032VA (en) * 2018-08-20 2021-02-25 Wuhan Neurophth Biotechnology Ltd Company Compositions and methods for treating leber's hereditary optic neuropathy
CN113025633B (zh) 2019-12-09 2024-08-27 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位1蛋白的核酸及其应用
CN115710585B (zh) * 2021-08-23 2025-03-28 纽福斯(苏州)生物科技有限公司 编码nd4的核酸及其用途

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6218117B1 (en) * 1998-06-15 2001-04-17 Mitokor Compositions and methods for identifying agents that quantitatively alter detectable extramitochondrial DNA:mitochondrial DNA ratios
PT1880008E (pt) * 2005-05-03 2015-08-27 Inserm Inst Nat De La Santé Et De La Rech Médicale Expressão de proteína mitocondrial através de uma abordagem alotópica melhorada
EP2121914B1 (en) * 2007-02-16 2014-08-20 John Guy Mitochondrial nucleic acid delivery systems
DE102010013829A1 (de) * 2010-03-26 2011-09-29 Carl Zeiss Microlmaging Gmbh Mikroskop und Verfahren zur Erfassung von Probenlicht
CN102634527B (zh) * 2012-04-11 2013-11-06 华中科技大学同济医学院附属同济医院 重组人nadh脱氢酶亚单位4基因及其表达载体构建方法
TWI698240B (zh) * 2012-05-15 2020-07-11 澳大利亞商艾佛蘭屈澳洲私營有限公司 使用腺相關病毒(aav)sflt-1治療老年性黃斑部退化(amd)
KR102244434B1 (ko) * 2014-08-11 2021-04-23 삼성전자주식회사 재조합 벡터 및 이를 이용한 목적 폴리펩타이드의 생산 방법
CN104450747B (zh) * 2014-09-23 2018-02-09 武汉纽福斯生物科技有限公司 用于治疗Leber遗传性视神经病变的重组腺相关病毒‑NADH脱氢酶亚单位4基因全长以及药剂

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