JP2021526505A5 - - Google Patents
Info
- Publication number
- JP2021526505A5 JP2021526505A5 JP2020558508A JP2020558508A JP2021526505A5 JP 2021526505 A5 JP2021526505 A5 JP 2021526505A5 JP 2020558508 A JP2020558508 A JP 2020558508A JP 2020558508 A JP2020558508 A JP 2020558508A JP 2021526505 A5 JP2021526505 A5 JP 2021526505A5
- Authority
- JP
- Japan
- Prior art keywords
- lnp
- lnp preparation
- preparation according
- mol
- therapeutic protein
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024060375A JP2024105237A (ja) | 2018-04-18 | 2024-04-03 | 治療用タンパク質の標的細胞に特異的な産生のための、および、標的細胞に関連する疾患、疾病、または障害の処置のための、融合性脂質ナノ粒子、および、融合性脂質ナノ粒子の製造方法と使用方法 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862659676P | 2018-04-18 | 2018-04-18 | |
| US62/659,676 | 2018-04-18 | ||
| US201962821084P | 2019-03-20 | 2019-03-20 | |
| US62/821,084 | 2019-03-20 | ||
| PCT/US2019/028207 WO2019204666A1 (en) | 2018-04-18 | 2019-04-18 | Fusogenic lipid nanoparticles and methods for the manufacture and use thereof for the target cell-specific production of a therapeutic protein and for the treatment of a disease, condition, or disorder associated with a target cell |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024060375A Division JP2024105237A (ja) | 2018-04-18 | 2024-04-03 | 治療用タンパク質の標的細胞に特異的な産生のための、および、標的細胞に関連する疾患、疾病、または障害の処置のための、融合性脂質ナノ粒子、および、融合性脂質ナノ粒子の製造方法と使用方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021526505A JP2021526505A (ja) | 2021-10-07 |
| JP2021526505A5 true JP2021526505A5 (enExample) | 2022-05-30 |
| JP7592493B2 JP7592493B2 (ja) | 2024-12-02 |
Family
ID=68239921
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020558508A Active JP7592493B2 (ja) | 2018-04-18 | 2019-04-18 | 治療用タンパク質の標的細胞に特異的な産生のための、および、標的細胞に関連する疾患、疾病、または障害の処置のための、融合性脂質ナノ粒子、および、融合性脂質ナノ粒子の製造方法と使用方法 |
| JP2024060375A Pending JP2024105237A (ja) | 2018-04-18 | 2024-04-03 | 治療用タンパク質の標的細胞に特異的な産生のための、および、標的細胞に関連する疾患、疾病、または障害の処置のための、融合性脂質ナノ粒子、および、融合性脂質ナノ粒子の製造方法と使用方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024060375A Pending JP2024105237A (ja) | 2018-04-18 | 2024-04-03 | 治療用タンパク質の標的細胞に特異的な産生のための、および、標的細胞に関連する疾患、疾病、または障害の処置のための、融合性脂質ナノ粒子、および、融合性脂質ナノ粒子の製造方法と使用方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (3) | US11603543B2 (enExample) |
| EP (1) | EP3784252A4 (enExample) |
| JP (2) | JP7592493B2 (enExample) |
| CN (2) | CN112312918A (enExample) |
| CA (1) | CA3097411A1 (enExample) |
| WO (1) | WO2019204666A1 (enExample) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2020503390A (ja) | 2017-01-09 | 2020-01-30 | オイシン バイオテクノロジーズ, インコーポレイテッド | 治療用タンパク質の標的細胞特異的な産生のため、および標的細胞に関連する疾患、状態、または障害の治療のための、膜融合性脂質ナノ粒子、ならびにその作製および使用のための方法 |
| CN112312918A (zh) | 2018-04-18 | 2021-02-02 | 奥依信生物技术公司 | 促融合脂质纳米粒和制备其的方法以及其用于靶细胞特异性产生治疗蛋白和治疗与靶细胞有关的疾病、病况或障碍的用途 |
| US20220008557A1 (en) * | 2018-11-14 | 2022-01-13 | Flagship Pioneering Innovations V, Inc. | Fusosome compositions for cns delivery |
| CN113631718A (zh) | 2018-11-14 | 2021-11-09 | 旗舰先锋创新V股份有限公司 | 用于特定隔室货物递送的组合物和方法 |
| CA3094859A1 (en) * | 2020-10-01 | 2022-04-01 | Entos Pharmaceuticals Inc. | Proteolipid vesicles formulated with fusion associated small transmembrane proteins |
| CN114540416A (zh) * | 2022-02-18 | 2022-05-27 | 上海交通大学 | 一种表达载体、脂质纳米粒、抗肿瘤药物及其制备方法和用途 |
| WO2024036148A1 (en) * | 2022-08-08 | 2024-02-15 | A2 Biotherapeutics, Inc. | Compositions and methods for treating blood cancers |
| CN116712406B (zh) * | 2023-04-23 | 2026-03-31 | 深圳复生命生物医药有限公司 | 一种病毒样纳米粒子核酸药物递送系统、制备方法及应用 |
Family Cites Families (33)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE69132032T2 (de) | 1990-11-23 | 2000-12-21 | Peptech Ltd., North Ryde | Verzögerung, verhinderung und/oder rückgängigmachen von zellalterung |
| US5869337A (en) | 1993-02-12 | 1999-02-09 | President And Fellows Of Harvard College | Regulated transcription of targeted genes and other biological events |
| AU733310C (en) | 1997-05-14 | 2001-11-29 | University Of British Columbia, The | High efficiency encapsulation of charged therapeutic agents in lipid vesicles |
| AU7936898A (en) | 1997-08-20 | 1999-03-08 | Dnavec Research Inc. | Vectors for treating cancer |
| AU1137699A (en) | 1997-11-07 | 1999-05-31 | Dalhousie University | Novel reovirus-derived proteins, nucleic acids encoding same, and uses therefor |
| US6899870B1 (en) * | 1998-03-11 | 2005-05-31 | Board Of Regents, The University Of Texas System | Induction of apoptic or cytotoxic gene expression by adenoviral mediated gene codelivery |
| US6403765B1 (en) * | 1998-06-16 | 2002-06-11 | Thomas Jefferson University | Truncated Apaf-1 and methods of use thereof |
| JP2002530436A (ja) | 1998-11-25 | 2002-09-17 | ジェネティカ インコーポレイテッド | 増殖能を増強しかつ複製老化を防止する方法及び試薬 |
| CA2325088A1 (en) | 2000-12-01 | 2002-06-01 | Fusogenix Inc. | Novel membrane fusion proteins derived from poikilothermic reovirus |
| JP2005504520A (ja) | 2001-06-13 | 2005-02-17 | イースタン ヴァージニア メディカル スクール | 治療用核酸の標的化発現の方法 |
| CN100361710C (zh) | 2004-06-07 | 2008-01-16 | 成都康弘生物科技有限公司 | 肿瘤细胞专一表达免疫调节因子gm-csf的溶瘤性腺病毒重组体的构建及其应用 |
| JPWO2006043354A1 (ja) | 2004-10-20 | 2008-05-22 | 独立行政法人放射線医学総合研究所 | 組込型の低線量放射線誘導性ベクター |
| JP2010531638A (ja) | 2007-06-12 | 2010-09-30 | ケース ウエスタン リザーブ ユニバーシティ | 標的化された細胞死 |
| RU2553225C2 (ru) | 2008-05-23 | 2015-06-10 | Сива Корпорейшн | Способ облегчения регенерации |
| EP3318248B1 (en) | 2009-12-01 | 2019-04-10 | Translate Bio, Inc. | Delivery of mrna for the augmentation of proteins and enzymes in human genetic diseases |
| US9089520B2 (en) | 2010-05-21 | 2015-07-28 | Baylor College Of Medicine | Methods for inducing selective apoptosis |
| EP2600871A2 (en) | 2010-08-04 | 2013-06-12 | The Ohio State University | Methods for impairing the p53/hdm2 auto-regulatory loop in multiple myeloma development using mir-192, mir-194 and mir-215 |
| CA2813300A1 (en) | 2010-09-29 | 2012-04-05 | Innovascreen Inc. | Recombinant polypeptides for membrane fusion and uses thereof |
| RU2013154295A (ru) * | 2011-06-08 | 2015-07-20 | Шир Хьюман Дженетик Терапис, Инк. | КОМПОЗИЦИИ ЛИПИДНЫХ НАНОЧАСТИЦ И СПОСОБЫ ДЛЯ ДОСТАВКИ мРНК |
| WO2012177927A1 (en) | 2011-06-21 | 2012-12-27 | Mayo Foundation For Medical Education And Research | Transgenic animals capable of being induced to delete senescent cells |
| EP2765997A4 (en) * | 2011-10-14 | 2015-06-24 | Stc Unm | POROUS NANOPARTICLE-SUPPORTED LIPID DOUBLE LAYERS (PROTOCOLS) FOR THE TARGETED RELEASE BY TRANSDERMAL RELEASE AND USE METHOD THEREFOR |
| US20150064137A1 (en) | 2012-04-17 | 2015-03-05 | Kythera Biopharmaceuticals, Inc. | Use of engineered viruses to specifically kill senescent cells |
| EP2852380A4 (en) * | 2012-05-23 | 2016-01-20 | Univ Ohio State | LIPID-COATED ALBUMIN NANOPARTICLE COMPOSITIONS AND METHOD FOR THE PREPARATION AND METHOD OF USE THEREOF |
| WO2014089239A1 (en) * | 2012-12-07 | 2014-06-12 | Alnylam Pharmaceuticals, Inc. | Improved nucleic acid lipid particle formulations |
| CN105142614A (zh) | 2013-03-14 | 2015-12-09 | 迪克纳制药公司 | 用于配制阴离子试剂的方法 |
| EP3388834B1 (en) * | 2013-03-15 | 2020-04-15 | Translate Bio, Inc. | Synergistic enhancement of the delivery of nucleic acids via blended formulations |
| BR112015024605A2 (pt) | 2013-03-24 | 2017-07-18 | Oisin Biotechnologies | sistemas e métodos para a produção visada de proteína terapêutica dentro de célula alvo |
| EP3234144B1 (en) * | 2014-12-15 | 2020-08-26 | Bellicum Pharmaceuticals, Inc. | Methods for controlled elimination of therapeutic cells |
| GB201503133D0 (en) | 2015-02-24 | 2015-04-08 | Ucl Business Plc And Syncona Partners Llp | Chimeric protein |
| WO2016185481A2 (en) | 2015-05-20 | 2016-11-24 | Yeda Research And Development Co. Ltd. | Method of targeting senescent cells |
| JP2020503390A (ja) | 2017-01-09 | 2020-01-30 | オイシン バイオテクノロジーズ, インコーポレイテッド | 治療用タンパク質の標的細胞特異的な産生のため、および標的細胞に関連する疾患、状態、または障害の治療のための、膜融合性脂質ナノ粒子、ならびにその作製および使用のための方法 |
| CN112312918A (zh) | 2018-04-18 | 2021-02-02 | 奥依信生物技术公司 | 促融合脂质纳米粒和制备其的方法以及其用于靶细胞特异性产生治疗蛋白和治疗与靶细胞有关的疾病、病况或障碍的用途 |
| EP3920888A4 (en) | 2019-02-04 | 2023-11-01 | Oisin Biotechnologies, Inc. | FUSOGENIC LIPID NANOPARTICLES FOR TARGET CELL-SPECIFIC PRODUCTION OF RAPAMYCIN-INDUCIBLE THERAPEUTIC PROTEINS |
-
2019
- 2019-04-18 CN CN201980041436.6A patent/CN112312918A/zh active Pending
- 2019-04-18 US US16/388,775 patent/US11603543B2/en active Active
- 2019-04-18 CA CA3097411A patent/CA3097411A1/en active Pending
- 2019-04-18 EP EP19789049.4A patent/EP3784252A4/en active Pending
- 2019-04-18 WO PCT/US2019/028207 patent/WO2019204666A1/en not_active Ceased
- 2019-04-18 CN CN202511703583.9A patent/CN121775163A/zh active Pending
- 2019-04-18 JP JP2020558508A patent/JP7592493B2/ja active Active
-
2022
- 2022-11-30 US US18/060,292 patent/US20230348937A1/en not_active Abandoned
-
2024
- 2024-04-03 JP JP2024060375A patent/JP2024105237A/ja active Pending
-
2025
- 2025-01-16 US US19/025,917 patent/US20250346925A1/en active Pending
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