JP2021512896A5 - - Google Patents

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Publication number
JP2021512896A5
JP2021512896A5 JP2020542569A JP2020542569A JP2021512896A5 JP 2021512896 A5 JP2021512896 A5 JP 2021512896A5 JP 2020542569 A JP2020542569 A JP 2020542569A JP 2020542569 A JP2020542569 A JP 2020542569A JP 2021512896 A5 JP2021512896 A5 JP 2021512896A5
Authority
JP
Japan
Prior art keywords
formulation
migalastat
use according
salt
effective amount
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2020542569A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021512896A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/016853 external-priority patent/WO2019157056A1/en
Publication of JP2021512896A publication Critical patent/JP2021512896A/ja
Publication of JP2021512896A5 publication Critical patent/JP2021512896A5/ja
Priority to JP2023192942A priority Critical patent/JP2024026080A/ja
Withdrawn legal-status Critical Current

Links

JP2020542569A 2018-02-06 2019-02-06 古典型ファブリー病患者の治療 Withdrawn JP2021512896A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023192942A JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862626992P 2018-02-06 2018-02-06
US62/626,992 2018-02-06
PCT/US2019/016853 WO2019157056A1 (en) 2018-02-06 2019-02-06 Treatment of patients with classic fabry disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023192942A Division JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Publications (2)

Publication Number Publication Date
JP2021512896A JP2021512896A (ja) 2021-05-20
JP2021512896A5 true JP2021512896A5 (https=) 2023-06-06

Family

ID=65494622

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020542569A Withdrawn JP2021512896A (ja) 2018-02-06 2019-02-06 古典型ファブリー病患者の治療
JP2023192942A Pending JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023192942A Pending JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Country Status (20)

Country Link
US (1) US20210038579A1 (https=)
EP (2) EP3749308B1 (https=)
JP (2) JP2021512896A (https=)
KR (1) KR20200128675A (https=)
CN (1) CN112203657A (https=)
AR (1) AR114392A1 (https=)
AU (2) AU2019217603A1 (https=)
DK (1) DK3749308T3 (https=)
ES (1) ES2969263T3 (https=)
FI (1) FI3749308T3 (https=)
HR (1) HRP20240025T1 (https=)
HU (1) HUE064761T2 (https=)
LT (1) LT3749308T (https=)
PL (1) PL3749308T3 (https=)
PT (1) PT3749308T (https=)
RS (1) RS65103B1 (https=)
SI (1) SI3749308T1 (https=)
SM (1) SMT202400027T1 (https=)
TW (2) TWI869336B (https=)
WO (1) WO2019157056A1 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL2533050T6 (pl) 2006-05-16 2016-05-31 Amicus Therapeutics Inc Możliwości leczenia choroby Fabry'ego
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
CA3224546C (en) 2017-05-30 2026-02-24 Amicus Therapeutics, Inc. Use of migalastat in the treatment of fabry patients
KR20200128676A (ko) 2018-02-06 2020-11-16 아미쿠스 세라퓨틱스, 인코포레이티드 임신 환자의 파브리병 치료를 위한 미갈라스타트의 용도
US12594268B2 (en) 2018-08-20 2026-04-07 Amicus Therapeutics, Inc. Methods of treating Fabry disease in patients having a mutation in the GLA gene
KR20220044560A (ko) 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) * 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
PL2533050T6 (pl) * 2006-05-16 2016-05-31 Amicus Therapeutics Inc Możliwości leczenia choroby Fabry'ego
MX2009010557A (es) 2007-03-30 2009-11-19 Amicus Therapeutics Inc Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas.
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
KR20190087673A (ko) * 2016-03-22 2019-07-24 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 g9331a 돌연변이를 갖는 환자에서 파브리 질병의 치료 방법
TW202408513A (zh) * 2016-07-19 2024-03-01 美商阿米庫斯醫療股份有限公司 治療ert初治的和已經歷ert的患者中之法布瑞氏症
SG11202000423XA (en) * 2017-07-19 2020-02-27 Amicus Therapeutics Inc Treatment of fabry disease in ert-naïve and ert-experienced patients

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