JP2021500864A - Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 - Google Patents

Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 Download PDF

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JP2021500864A
JP2021500864A JP2020517500A JP2020517500A JP2021500864A JP 2021500864 A JP2021500864 A JP 2021500864A JP 2020517500 A JP2020517500 A JP 2020517500A JP 2020517500 A JP2020517500 A JP 2020517500A JP 2021500864 A JP2021500864 A JP 2021500864A
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composition according
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JP2021500864A5 (enExample
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マヘンドラ プラカシュ カンジョリア，アルティ
マヘンドラ プラカシュ カンジョリア，アルティ
オダテ，ショブ
リン サイツァー，ジェシカ
リン サイツァー，ジェシカ
マイケル レスカーボ，レイナルド
マイケル レスカーボ，レイナルド
ストラップス，ウォルター
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インテリア セラピューティクス，インコーポレイテッド
インテリア セラピューティクス，インコーポレイテッド
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Publication of JP2021500864A publication Critical patent/JP2021500864A/ja
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JP2020517500A 2017-09-29 2018-09-28 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法 Pending JP2021500864A (ja)

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JP2022194564A JP7707140B2 (ja) 2017-09-29 2022-12-06 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法
JP2025112164A JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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US201762566236P 2017-09-29 2017-09-29
US62/566,236 2017-09-29
US201862671902P 2018-05-15 2018-05-15
US62/671,902 2018-05-15
PCT/US2018/053382 WO2019067872A1 (en) 2017-09-29 2018-09-28 COMPOSITIONS AND METHODS FOR EDITING THE TTR GENE AND TREATING AMYLOID DOSE ATTR

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JP2022194564A Active JP7707140B2 (ja) 2017-09-29 2022-12-06 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法
JP2025112164A Pending JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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JP2025112164A Pending JP2025163016A (ja) 2017-09-29 2025-07-02 Ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスの治療用の組成物および方法

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KR (1) KR20200058509A (enExample)
CN (2) CN111417728A (enExample)
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BR (1) BR112020005287A2 (enExample)
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IL (3) IL311170B2 (enExample)
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JP2024519922A (ja) * 2021-05-21 2024-05-21 ビーム セラピューティクス インク． トランスサイレチン遺伝子の塩基編集
JP2024527525A (ja) * 2021-06-22 2024-07-25 インテリア セラピューティクス，インコーポレイテッド 肝遺伝子のインビボ編集のための方法

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WO2023028469A2 (en) * 2021-08-23 2023-03-02 The Board Of Trustees Of The Leland Stanford Junior University Targeted integration at beta-globin locus in human hematopoietic stem and progenitor cells
JP2024535888A (ja) 2021-09-20 2024-10-02 アルナイラム ファーマシューティカルズ， インコーポレイテッド インヒビンサブユニットベータｅ（ｉｎｈｂｅ）モジュレーター組成物およびその使用方法
CN116064598B (zh) * 2021-10-08 2024-03-12 苏州艾博生物科技有限公司 冠状病毒的核酸疫苗
CN118974256A (zh) * 2022-03-29 2024-11-15 锐正基因(苏州)有限公司 用于治疗转甲状腺素蛋白淀粉样变性的组合物和方法
WO2024003805A1 (en) * 2022-06-30 2024-01-04 Geneditbio Limited Methods and compositions for ttr gene editing and therapy using crispr system
WO2024003810A1 (en) * 2022-06-30 2024-01-04 Geneditbio Limited Guide rna with chemical modifications
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