CA3077251A1 - Compositions and methods for ttr gene editing and treating attr amyloidosis - Google Patents
Compositions and methods for ttr gene editing and treating attr amyloidosis Download PDFInfo
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| CA3224995A1 (en) | 2021-06-22 | 2022-12-29 | Intellia Therapeutics, Inc. | Methods for in vivo editing of a liver gene |
| WO2023028469A2 (en) * | 2021-08-23 | 2023-03-02 | The Board Of Trustees Of The Leland Stanford Junior University | Targeted integration at beta-globin locus in human hematopoietic stem and progenitor cells |
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