JP2019537446A5 - - Google Patents

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Publication number
JP2019537446A5
JP2019537446A5 JP2019524226A JP2019524226A JP2019537446A5 JP 2019537446 A5 JP2019537446 A5 JP 2019537446A5 JP 2019524226 A JP2019524226 A JP 2019524226A JP 2019524226 A JP2019524226 A JP 2019524226A JP 2019537446 A5 JP2019537446 A5 JP 2019537446A5
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JP
Japan
Prior art keywords
nucleic acid
sequence
composition
pharmaceutical composition
domain
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JP2019524226A
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English (en)
Japanese (ja)
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JP2019537446A (ja
JP7338937B2 (ja
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Priority claimed from PCT/KR2017/010897 external-priority patent/WO2018088694A2/ko
Publication of JP2019537446A publication Critical patent/JP2019537446A/ja
Publication of JP2019537446A5 publication Critical patent/JP2019537446A5/ja
Application granted granted Critical
Publication of JP7338937B2 publication Critical patent/JP7338937B2/ja
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JP2019524226A 2016-11-14 2017-09-28 人工的に操作されたsc機能制御システム Active JP7338937B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662421516P 2016-11-14 2016-11-14
US62/421,516 2016-11-14
PCT/KR2017/010897 WO2018088694A2 (ko) 2016-11-14 2017-09-28 인위적으로 조작된 sc 기능 조절 시스템

Publications (3)

Publication Number Publication Date
JP2019537446A JP2019537446A (ja) 2019-12-26
JP2019537446A5 true JP2019537446A5 (enExample) 2020-11-12
JP7338937B2 JP7338937B2 (ja) 2023-09-05

Family

ID=62109586

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2019524226A Active JP7338937B2 (ja) 2016-11-14 2017-09-28 人工的に操作されたsc機能制御システム

Country Status (9)

Country Link
US (1) US12331086B2 (enExample)
EP (2) EP3539980A4 (enExample)
JP (1) JP7338937B2 (enExample)
KR (2) KR102437228B1 (enExample)
CN (1) CN110248957B (enExample)
AU (1) AU2017358122B2 (enExample)
BR (1) BR112019009725A2 (enExample)
RU (2) RU2768043C2 (enExample)
WO (1) WO2018088694A2 (enExample)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11572574B2 (en) 2017-09-28 2023-02-07 Toolgen Incorporated Artificial genome manipulation for gene expression regulation
AU2018339164B2 (en) * 2017-09-28 2022-06-16 Toolgen Incorporated Artificial genome manipulation for gene expression regulation
EP3851528A4 (en) * 2018-09-12 2023-12-06 Institute for Basic Science COMPOSITION FOR INDUCATING DEATH OF CELLS HAVING MUTATED GENE AND METHOD FOR INDUCATING DEATH OF CELLS HAVING MODIFIED GENE USING THE COMPOSITION
GB201907882D0 (en) 2019-06-03 2019-07-17 Cyprus Foundation For Muscular Dystrophy Res Methods
EP3798301A1 (en) * 2019-09-25 2021-03-31 KWS SAAT SE & Co. KGaA Promoter repression
WO2021184021A1 (en) * 2020-03-13 2021-09-16 Codiak Biosciences, Inc. Extracellular vesicle-aso constructs targeting pmp22
CN114621922A (zh) * 2022-02-15 2022-06-14 中山大学附属第五医院 一种大鼠海绵体神经来源施旺细胞的提取纯化和培养方法
WO2025079278A1 (ja) * 2023-10-10 2025-04-17 国立大学法人 東京医科歯科大学 シャルコー・マリー・トゥース病の処置剤

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR100613038B1 (ko) * 2004-07-07 2006-08-16 공주대학교 산학협력단 염색체 17p11.2-p12 지역의 중복을 제외한 유전자돌연변이를 발병 원인으로 하는 CMT 질환의 진단방법및 진단키트
JP2010531638A (ja) * 2007-06-12 2010-09-30 ケース ウエスタン リザーブ ユニバーシティ 標的化された細胞死
PL4397760T3 (pl) 2012-10-23 2026-03-30 Toolgen Incorporated Kompozycja do rozszczepiania docelowego dna zawierająca prowadzące rna specyficzne dla docelowego dna i kwas nukleinowy kodujący białko cas lub białko cas oraz jej zastosowanie
IL239317B (en) 2012-12-12 2022-07-01 Broad Inst Inc Providing, engineering and optimizing systems, methods and compositions for sequence manipulation and therapeutic applications
WO2014204724A1 (en) * 2013-06-17 2014-12-24 The Broad Institute Inc. Delivery, engineering and optimization of tandem guide systems, methods and compositions for sequence manipulation
WO2015048577A2 (en) * 2013-09-27 2015-04-02 Editas Medicine, Inc. Crispr-related methods and compositions
KR20160102056A (ko) * 2013-12-26 2016-08-26 더 제너럴 하스피탈 코포레이션 멀티플렉스 가이드 rna
EP3151846A4 (en) * 2014-06-05 2017-12-27 Sangamo BioSciences, Inc. Methods and compositions for nuclease design
WO2016021973A1 (ko) 2014-08-06 2016-02-11 주식회사 툴젠 캄필로박터 제주니 crispr/cas 시스템 유래 rgen을 이용한 유전체 교정
SG10202104041PA (en) 2015-10-23 2021-06-29 Harvard College Nucleobase editors and uses thereof

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