JP2019508051A5 - - Google Patents

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Publication number
JP2019508051A5
JP2019508051A5 JP2018548318A JP2018548318A JP2019508051A5 JP 2019508051 A5 JP2019508051 A5 JP 2019508051A5 JP 2018548318 A JP2018548318 A JP 2018548318A JP 2018548318 A JP2018548318 A JP 2018548318A JP 2019508051 A5 JP2019508051 A5 JP 2019508051A5
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JP
Japan
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nucleotide sequence
cells
cell
grna
targeting domain
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JP2018548318A
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English (en)
Japanese (ja)
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JP2019508051A (ja
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Priority claimed from PCT/US2017/022377 external-priority patent/WO2017160890A1/en
Publication of JP2019508051A publication Critical patent/JP2019508051A/ja
Publication of JP2019508051A5 publication Critical patent/JP2019508051A5/ja
Priority to JP2023026918A priority Critical patent/JP2023075166A/ja
Priority to JP2025244943A priority patent/JP2026064992A/ja
Pending legal-status Critical Current

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JP2018548318A 2016-03-14 2017-03-14 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物 Pending JP2019508051A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023026918A JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物
JP2025244943A JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662308190P 2016-03-14 2016-03-14
US62/308,190 2016-03-14
US201762456615P 2017-02-08 2017-02-08
US62/456,615 2017-02-08
PCT/US2017/022377 WO2017160890A1 (en) 2016-03-14 2017-03-14 Crispr/cas-related methods and compositions for treating beta hemoglobinopathies

Related Child Applications (1)

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JP2023026918A Division JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Publications (2)

Publication Number Publication Date
JP2019508051A JP2019508051A (ja) 2019-03-28
JP2019508051A5 true JP2019508051A5 (https=) 2020-04-23

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ID=58413206

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Application Number Title Priority Date Filing Date
JP2018548318A Pending JP2019508051A (ja) 2016-03-14 2017-03-14 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物
JP2023026918A Pending JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物
JP2025244943A Pending JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2023026918A Pending JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物
JP2025244943A Pending JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Country Status (11)

Country Link
US (2) US20200255857A1 (https=)
EP (1) EP3430142A1 (https=)
JP (3) JP2019508051A (https=)
KR (2) KR102532663B1 (https=)
CN (4) CN109153994A (https=)
AU (2) AU2017235333B2 (https=)
CA (1) CA3017956A1 (https=)
IL (2) IL313038A (https=)
MX (2) MX2018011114A (https=)
SG (1) SG11201807859WA (https=)
WO (1) WO2017160890A1 (https=)

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