JP2018506530A5 - - Google Patents

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Publication number
JP2018506530A5
JP2018506530A5 JP2017540569A JP2017540569A JP2018506530A5 JP 2018506530 A5 JP2018506530 A5 JP 2018506530A5 JP 2017540569 A JP2017540569 A JP 2017540569A JP 2017540569 A JP2017540569 A JP 2017540569A JP 2018506530 A5 JP2018506530 A5 JP 2018506530A5
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JP
Japan
Prior art keywords
spinal
aav9
gfp
expression
buffy coat
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2017540569A
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English (en)
Japanese (ja)
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JP2018506530A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2015/065704 external-priority patent/WO2016122791A1/en
Publication of JP2018506530A publication Critical patent/JP2018506530A/ja
Publication of JP2018506530A5 publication Critical patent/JP2018506530A5/ja
Pending legal-status Critical Current

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JP2017540569A 2015-01-30 2015-12-15 脊柱軟膜下遺伝子送達システム Pending JP2018506530A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562110340P 2015-01-30 2015-01-30
US62/110,340 2015-01-30
PCT/US2015/065704 WO2016122791A1 (en) 2015-01-30 2015-12-15 Spinal subpial gene delivery system

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2019182624A Division JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム

Publications (2)

Publication Number Publication Date
JP2018506530A JP2018506530A (ja) 2018-03-08
JP2018506530A5 true JP2018506530A5 (https=) 2019-02-14

Family

ID=56544138

Family Applications (5)

Application Number Title Priority Date Filing Date
JP2017540569A Pending JP2018506530A (ja) 2015-01-30 2015-12-15 脊柱軟膜下遺伝子送達システム
JP2019182624A Withdrawn JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム
JP2021124373A Pending JP2021181456A (ja) 2015-01-30 2021-07-29 脊髄軟膜下遺伝子送達システム
JP2023036473A Pending JP2023060308A (ja) 2015-01-30 2023-03-09 脊髄軟膜下遺伝子送達システム
JP2024199400A Pending JP2025015673A (ja) 2015-01-30 2024-11-15 脊髄軟膜下遺伝子送達システム

Family Applications After (4)

Application Number Title Priority Date Filing Date
JP2019182624A Withdrawn JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム
JP2021124373A Pending JP2021181456A (ja) 2015-01-30 2021-07-29 脊髄軟膜下遺伝子送達システム
JP2023036473A Pending JP2023060308A (ja) 2015-01-30 2023-03-09 脊髄軟膜下遺伝子送達システム
JP2024199400A Pending JP2025015673A (ja) 2015-01-30 2024-11-15 脊髄軟膜下遺伝子送達システム

Country Status (6)

Country Link
US (1) US20180008727A1 (https=)
EP (1) EP3250279B1 (https=)
JP (5) JP2018506530A (https=)
CN (1) CN107427666B (https=)
CA (1) CA2975447C (https=)
WO (1) WO2016122791A1 (https=)

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CA3193811A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
CN119876138A (zh) 2014-11-14 2025-04-25 沃雅戈治疗公司 调节性多核苷酸
HK1245326A1 (zh) 2014-12-12 2018-08-24 Voyager Therapeutics, Inc. 用於生产scaav的组合物和方法
US10688285B2 (en) * 2015-01-30 2020-06-23 The Regents Of The University Of California Spinal subpial gene delivery system
AU2017241534A1 (en) 2016-03-28 2018-10-04 The Regents Of The University Of California Method and composition for treating neuronal hyper-excitability
EP3448987A4 (en) 2016-04-29 2020-05-27 Voyager Therapeutics, Inc. COMPOSITIONS FOR TREATING A DISEASE
EP3448874A4 (en) 2016-04-29 2020-04-22 Voyager Therapeutics, Inc. COMPOSITIONS FOR TREATING A DISEASE
CA3024449A1 (en) 2016-05-18 2017-11-23 Voyager Therapeutics, Inc. Compositions and methods of treating huntington's disease
CA3024448C (en) 2016-05-18 2025-09-09 Voyager Therapeutics, Inc. MODULATING POLYNUCLEOTIDES
WO2018044933A1 (en) 2016-08-30 2018-03-08 The Regents Of The University Of California Methods for biomedical targeting and delivery and devices and systems for practicing the same
EP3618839A4 (en) 2017-05-05 2021-06-09 Voyager Therapeutics, Inc. COMPOSITIONS AND METHODS OF TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
JP2020518259A (ja) 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． ハンチントン病治療組成物および方法
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
JP7229989B2 (ja) 2017-07-17 2023-02-28 ボイジャー セラピューティクス インコーポレイテッド 軌道アレイガイドシステム
JP7221275B2 (ja) 2017-08-03 2023-02-13 ボイジャー セラピューティクス インコーポレイテッド Ａａｖを送達するための組成物および方法
JP7291125B2 (ja) * 2017-09-08 2023-06-14 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 神経障害性疼痛を処置するための方法および組成物
US20200263199A1 (en) 2017-09-29 2020-08-20 Voyager Therapeutics, Inc. Rescue of central and peripheral neurological phenotype of friedreich's ataxia by intravenous delivery
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
WO2019079242A1 (en) 2017-10-16 2019-04-25 Voyager Therapeutics, Inc. TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
SG11202011296VA (en) 2018-05-15 2020-12-30 Voyager Therapeutics Inc Compositions and methods for the treatment of parkinson's disease
US12281321B2 (en) 2018-09-28 2025-04-22 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
EP3908198B1 (en) * 2019-01-10 2024-12-11 The Regents of the University of California Subpial delivery system
USD963164S1 (en) 2020-01-09 2022-09-06 The Regents Of The University Of California Surgical needle
WO2024120772A1 (en) 2022-12-05 2024-06-13 Eg 427 Viral vector encoding gad for treating spasticity

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