JP2018506530A5 - - Google Patents

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Publication number
JP2018506530A5
JP2018506530A5 JP2017540569A JP2017540569A JP2018506530A5 JP 2018506530 A5 JP2018506530 A5 JP 2018506530A5 JP 2017540569 A JP2017540569 A JP 2017540569A JP 2017540569 A JP2017540569 A JP 2017540569A JP 2018506530 A5 JP2018506530 A5 JP 2018506530A5
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JP
Japan
Prior art keywords
spinal
aav9
gfp
expression
buffy coat
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2017540569A
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English (en)
Japanese (ja)
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JP2018506530A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2015/065704 external-priority patent/WO2016122791A1/en
Publication of JP2018506530A publication Critical patent/JP2018506530A/ja
Publication of JP2018506530A5 publication Critical patent/JP2018506530A5/ja
Pending legal-status Critical Current

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JP2017540569A 2015-01-30 2015-12-15 脊柱軟膜下遺伝子送達システム Pending JP2018506530A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562110340P 2015-01-30 2015-01-30
US62/110,340 2015-01-30
PCT/US2015/065704 WO2016122791A1 (en) 2015-01-30 2015-12-15 Spinal subpial gene delivery system

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2019182624A Division JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム

Publications (2)

Publication Number Publication Date
JP2018506530A JP2018506530A (ja) 2018-03-08
JP2018506530A5 true JP2018506530A5 (enExample) 2019-02-14

Family

ID=56544138

Family Applications (5)

Application Number Title Priority Date Filing Date
JP2017540569A Pending JP2018506530A (ja) 2015-01-30 2015-12-15 脊柱軟膜下遺伝子送達システム
JP2019182624A Withdrawn JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム
JP2021124373A Pending JP2021181456A (ja) 2015-01-30 2021-07-29 脊髄軟膜下遺伝子送達システム
JP2023036473A Pending JP2023060308A (ja) 2015-01-30 2023-03-09 脊髄軟膜下遺伝子送達システム
JP2024199400A Pending JP2025015673A (ja) 2015-01-30 2024-11-15 脊髄軟膜下遺伝子送達システム

Family Applications After (4)

Application Number Title Priority Date Filing Date
JP2019182624A Withdrawn JP2020019796A (ja) 2015-01-30 2019-10-03 脊髄軟膜下遺伝子送達システム
JP2021124373A Pending JP2021181456A (ja) 2015-01-30 2021-07-29 脊髄軟膜下遺伝子送達システム
JP2023036473A Pending JP2023060308A (ja) 2015-01-30 2023-03-09 脊髄軟膜下遺伝子送達システム
JP2024199400A Pending JP2025015673A (ja) 2015-01-30 2024-11-15 脊髄軟膜下遺伝子送達システム

Country Status (6)

Country Link
US (1) US20180008727A1 (enExample)
EP (1) EP3250279B1 (enExample)
JP (5) JP2018506530A (enExample)
CN (1) CN107427666B (enExample)
CA (1) CA2975447C (enExample)
WO (1) WO2016122791A1 (enExample)

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KR102584655B1 (ko) 2014-11-14 2023-10-06 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
MX2017006216A (es) 2014-11-14 2018-08-29 Voyager Therapeutics Inc Composiciones y métodos para tratar la esclerosis lateral amiotrófica (ela).
US11697825B2 (en) 2014-12-12 2023-07-11 Voyager Therapeutics, Inc. Compositions and methods for the production of scAAV
US10688285B2 (en) 2015-01-30 2020-06-23 The Regents Of The University Of California Spinal subpial gene delivery system
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WO2017189964A2 (en) 2016-04-29 2017-11-02 Voyager Therapeutics, Inc. Compositions for the treatment of disease
US11326182B2 (en) 2016-04-29 2022-05-10 Voyager Therapeutics, Inc. Compositions for the treatment of disease
AU2017268382B2 (en) 2016-05-18 2023-09-28 Voyager Therapeutics, Inc. Compositions and methods of treating Huntington's disease
RU2758488C2 (ru) 2016-05-18 2021-10-28 Вояджер Терапьютикс, Инк. Модулирующие полинуклеотиды
JP2019531787A (ja) 2016-08-30 2019-11-07 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 生物医学的ターゲティング及びデリバリーの方法並びにそれを実行するための装置及びシステム
AU2018261790B2 (en) 2017-05-05 2024-10-03 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
WO2018204803A1 (en) 2017-05-05 2018-11-08 Voyager Therapeutics, Inc. Compositions and methods of treating huntington's disease
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
CN111132626B (zh) 2017-07-17 2024-01-30 沃雅戈治疗公司 轨迹阵列引导系统
EP3662060A2 (en) 2017-08-03 2020-06-10 Voyager Therapeutics, Inc. Compositions and methods for delivery of aav
AU2018327253B2 (en) * 2017-09-08 2024-05-16 The Regents Of The University Of California Method and composition for treating neuropathic pain
EP3687582A4 (en) 2017-09-29 2021-07-14 Voyager Therapeutics, Inc. RESCUE OF CENTRAL AND PERIPHERAL NEUROLOGICAL PHENOTYPE OF FRIEDREICH ATAXIA BY INTRAVENOUS ADMINISTRATION
US11434502B2 (en) 2017-10-16 2022-09-06 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (ALS)
EP4454654A3 (en) 2017-10-16 2025-02-19 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (als)
MX2020012077A (es) 2018-05-15 2021-03-09 Voyager Therapeutics Inc Composiciones y metodos para el tratamiento de la enfermedad de parkinson.
SG11202103151RA (en) 2018-09-28 2021-04-29 Voyager Therapeutics Inc Frataxin expression constructs having engineered promoters and methods of use thereof
JP7373226B2 (ja) * 2019-01-10 2023-11-02 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 軟膜下送達システムおよび使用方法
USD963164S1 (en) 2020-01-09 2022-09-06 The Regents Of The University Of California Surgical needle
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