JP2017509632A5 - - Google Patents

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Publication number
JP2017509632A5
JP2017509632A5 JP2016557218A JP2016557218A JP2017509632A5 JP 2017509632 A5 JP2017509632 A5 JP 2017509632A5 JP 2016557218 A JP2016557218 A JP 2016557218A JP 2016557218 A JP2016557218 A JP 2016557218A JP 2017509632 A5 JP2017509632 A5 JP 2017509632A5
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JP
Japan
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nucleic acid
raav
seq
acid encoding
mir
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JP2016557218A
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English (en)
Japanese (ja)
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JP2017509632A (ja
JP6669664B2 (ja
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Priority claimed from PCT/US2015/021896 external-priority patent/WO2015143418A2/en
Publication of JP2017509632A publication Critical patent/JP2017509632A/ja
Publication of JP2017509632A5 publication Critical patent/JP2017509632A5/ja
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Publication of JP6669664B2 publication Critical patent/JP6669664B2/ja
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JP2016557218A 2014-03-21 2015-03-20 網膜色素変性症のための遺伝子治療 Active JP6669664B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201461969027P 2014-03-21 2014-03-21
US61/969,027 2014-03-21
PCT/US2015/021896 WO2015143418A2 (en) 2014-03-21 2015-03-20 Gene therapy for retinitis pigmentosa

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2019224202A Division JP7048563B2 (ja) 2014-03-21 2019-12-12 網膜色素変性症のための遺伝子治療

Publications (3)

Publication Number Publication Date
JP2017509632A JP2017509632A (ja) 2017-04-06
JP2017509632A5 true JP2017509632A5 (OSRAM) 2018-04-26
JP6669664B2 JP6669664B2 (ja) 2020-03-18

Family

ID=52829343

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2016557218A Active JP6669664B2 (ja) 2014-03-21 2015-03-20 網膜色素変性症のための遺伝子治療
JP2019224202A Active JP7048563B2 (ja) 2014-03-21 2019-12-12 網膜色素変性症のための遺伝子治療
JP2022046280A Active JP7534348B2 (ja) 2014-03-21 2022-03-23 網膜色素変性症のための遺伝子治療

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2019224202A Active JP7048563B2 (ja) 2014-03-21 2019-12-12 網膜色素変性症のための遺伝子治療
JP2022046280A Active JP7534348B2 (ja) 2014-03-21 2022-03-23 網膜色素変性症のための遺伝子治療

Country Status (36)

Country Link
US (3) US10383953B2 (OSRAM)
EP (3) EP3628334B1 (OSRAM)
JP (3) JP6669664B2 (OSRAM)
KR (2) KR20230006039A (OSRAM)
CN (2) CN115252823A (OSRAM)
AR (1) AR099837A1 (OSRAM)
AU (3) AU2015230942B2 (OSRAM)
CA (2) CA2943185C (OSRAM)
CL (1) CL2016002333A1 (OSRAM)
CR (1) CR20160480A (OSRAM)
DK (2) DK3119437T3 (OSRAM)
DO (1) DOP2016000237A (OSRAM)
EA (1) EA201691891A1 (OSRAM)
EC (1) ECSP16083000A (OSRAM)
ES (2) ES2760263T3 (OSRAM)
FI (1) FI3628334T3 (OSRAM)
HR (2) HRP20192141T1 (OSRAM)
HU (2) HUE046454T2 (OSRAM)
IL (3) IL247543B (OSRAM)
LT (2) LT3119437T (OSRAM)
MA (1) MA39390B2 (OSRAM)
MX (2) MX376190B (OSRAM)
MY (2) MY190726A (OSRAM)
NZ (1) NZ724622A (OSRAM)
PE (1) PE20161252A1 (OSRAM)
PH (1) PH12016501684B1 (OSRAM)
PL (2) PL3119437T3 (OSRAM)
PT (2) PT3119437T (OSRAM)
RS (2) RS64611B1 (OSRAM)
SG (3) SG11201607005UA (OSRAM)
SI (2) SI3119437T1 (OSRAM)
TW (2) TWI780401B (OSRAM)
UA (1) UA120050C2 (OSRAM)
UY (1) UY36044A (OSRAM)
WO (1) WO2015143418A2 (OSRAM)
ZA (1) ZA201605924B (OSRAM)

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IL261014B2 (en) * 2016-03-01 2023-10-01 Univ Florida Aav vectors for treatment of dominant retinitis pigmentosa
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WO2018172961A1 (en) * 2017-03-21 2018-09-27 Ludwig-Maximilians-Universität München Gene therapy for the treatment of cngb1-linked retinitis pigmentosa
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TW202014181A (zh) 2018-04-04 2020-04-16 美商希吉隆醫療公司 可植入顆粒及相關方法
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CN111518813B (zh) * 2019-02-03 2023-04-28 武汉纽福斯生物科技有限公司 视紫红质的编码序列、其表达载体构建及其应用
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WO2021030745A1 (en) * 2019-08-15 2021-02-18 The Children's Hospital Of Philadelphia Combined transgene and intron-derived mirna therapy for treatment of sca1
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AU2021213786A1 (en) * 2020-01-29 2022-09-22 Genzyme Corporation Modified adeno-associated viral capsid proteins for ocular gene therapy and methods of use thereof
KR102396200B1 (ko) * 2020-07-24 2022-05-12 알지노믹스 주식회사 로돕신 전사체에 특이적인 트랜스-스플라이싱 라이보자임 및 이의 용도
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TWI832531B (zh) * 2022-11-02 2024-02-11 慈濟學校財團法人慈濟大學 Rip1抑制劑或mlkl抑制劑用於治療或預防遺傳性視網膜失養症的用途
CN117625619B (zh) * 2023-12-05 2024-11-12 云舟生物科技(广州)股份有限公司 核酸分子及其作为特异启动子的应用
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