JP2016163571A5 - - Google Patents

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Publication number
JP2016163571A5
JP2016163571A5 JP2016039171A JP2016039171A JP2016163571A5 JP 2016163571 A5 JP2016163571 A5 JP 2016163571A5 JP 2016039171 A JP2016039171 A JP 2016039171A JP 2016039171 A JP2016039171 A JP 2016039171A JP 2016163571 A5 JP2016163571 A5 JP 2016163571A5
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JP
Japan
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pharmaceutical composition
galactosidase
specific pharmacological
pharmacological chaperone
gala
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JP2016039171A
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English (en)
Japanese (ja)
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JP2016163571A (ja
JP6672013B2 (ja
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Publication of JP2016163571A5 publication Critical patent/JP2016163571A5/ja
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JP2016039171A 2008-02-12 2016-03-01 疾病の薬理シャペロン治療に対する応答性を予測する方法 Active JP6672013B2 (ja)

Applications Claiming Priority (8)

Application Number Priority Date Filing Date Title
US2814108P 2008-02-12 2008-02-12
US61/028,141 2008-02-12
US3568408P 2008-03-11 2008-03-11
US61/035,684 2008-03-11
US9363108P 2008-09-02 2008-09-02
US61/093,631 2008-09-02
US11349608P 2008-11-11 2008-11-11
US61/113,496 2008-11-11

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
JP2014244283A Division JP2015091239A (ja) 2008-02-12 2014-12-02 疾病の薬理シャペロン治療に対する応答性を予測する方法

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2018245609A Division JP6837469B2 (ja) 2008-02-12 2018-12-27 疾病の薬理シャペロン治療に対する応答性を予測する方法

Publications (3)

Publication Number Publication Date
JP2016163571A JP2016163571A (ja) 2016-09-08
JP2016163571A5 true JP2016163571A5 (https=) 2016-12-01
JP6672013B2 JP6672013B2 (ja) 2020-03-25

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ID=40957500

Family Applications (7)

Application Number Title Priority Date Filing Date
JP2010546901A Active JP5844045B2 (ja) 2008-02-12 2009-02-12 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2014244283A Pending JP2015091239A (ja) 2008-02-12 2014-12-02 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2016039171A Active JP6672013B2 (ja) 2008-02-12 2016-03-01 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2018245609A Active JP6837469B2 (ja) 2008-02-12 2018-12-27 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2021019383A Active JP7277493B2 (ja) 2008-02-12 2021-02-09 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2023076515A Withdrawn JP2023109807A (ja) 2008-02-12 2023-05-08 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2025097940A Pending JP2025148351A (ja) 2008-02-12 2025-06-11 疾病の薬理シャペロン治療に対する応答性を予測する方法

Family Applications Before (2)

Application Number Title Priority Date Filing Date
JP2010546901A Active JP5844045B2 (ja) 2008-02-12 2009-02-12 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2014244283A Pending JP2015091239A (ja) 2008-02-12 2014-12-02 疾病の薬理シャペロン治療に対する応答性を予測する方法

Family Applications After (4)

Application Number Title Priority Date Filing Date
JP2018245609A Active JP6837469B2 (ja) 2008-02-12 2018-12-27 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2021019383A Active JP7277493B2 (ja) 2008-02-12 2021-02-09 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2023076515A Withdrawn JP2023109807A (ja) 2008-02-12 2023-05-08 疾病の薬理シャペロン治療に対する応答性を予測する方法
JP2025097940A Pending JP2025148351A (ja) 2008-02-12 2025-06-11 疾病の薬理シャペロン治療に対する応答性を予測する方法

Country Status (16)

Country Link
US (8) US8592362B2 (https=)
EP (4) EP2946785B1 (https=)
JP (7) JP5844045B2 (https=)
AU (7) AU2009214648B2 (https=)
CA (1) CA2715407C (https=)
CY (3) CY1116466T1 (https=)
DK (3) DK3470077T3 (https=)
ES (3) ES2541933T3 (https=)
HR (3) HRP20150728T1 (https=)
HU (3) HUE042882T2 (https=)
LT (2) LT2946785T (https=)
MX (1) MX2010008835A (https=)
PL (3) PL2252313T3 (https=)
PT (3) PT2252313E (https=)
SI (3) SI2252313T1 (https=)
WO (1) WO2009102895A2 (https=)

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SG11202000423XA (en) 2017-07-19 2020-02-27 Amicus Therapeutics Inc Treatment of fabry disease in ert-naïve and ert-experienced patients
US20200222377A1 (en) 2017-08-28 2020-07-16 Amicus Therapeutics, Inc. Methods Of Enhancing And/Or Stabilizing Cardiac Function In Patients With Fabry Disease
KR20200128676A (ko) 2018-02-06 2020-11-16 아미쿠스 세라퓨틱스, 인코포레이티드 임신 환자의 파브리병 치료를 위한 미갈라스타트의 용도
PT3749308T (pt) 2018-02-06 2024-01-25 Amicus Therapeutics Inc Tratamento de pacientes com doença de fabry clássica com migalastato
US12594268B2 (en) 2018-08-20 2026-04-07 Amicus Therapeutics, Inc. Methods of treating Fabry disease in patients having a mutation in the GLA gene
MX2021015352A (es) 2019-06-11 2022-04-06 Amicus Therapeutics Inc Métodos para tratar la enfermedad de fabry en pacientes que tienen insuficiencia renal.
KR20220044560A (ko) 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법

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