JP2015522280A5 - - Google Patents

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Publication number
JP2015522280A5
JP2015522280A5 JP2015520166A JP2015520166A JP2015522280A5 JP 2015522280 A5 JP2015522280 A5 JP 2015522280A5 JP 2015520166 A JP2015520166 A JP 2015520166A JP 2015520166 A JP2015520166 A JP 2015520166A JP 2015522280 A5 JP2015522280 A5 JP 2015522280A5
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JP
Japan
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JP2015520166A
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Japanese (ja)
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JP6366581B2 (ja
JP2015522280A (ja
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Priority claimed from PCT/US2013/031644 external-priority patent/WO2014007858A1/en
Publication of JP2015522280A publication Critical patent/JP2015522280A/ja
Publication of JP2015522280A5 publication Critical patent/JP2015522280A5/ja
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JP2015520166A 2012-07-06 2013-03-14 改変されたアデノ随伴ウイルスベクター組成物 Active JP6366581B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261668839P 2012-07-06 2012-07-06
US61/668,839 2012-07-06
PCT/US2013/031644 WO2014007858A1 (en) 2012-07-06 2013-03-14 Modified adeno-associated virus vector compositions

Publications (3)

Publication Number Publication Date
JP2015522280A JP2015522280A (ja) 2015-08-06
JP2015522280A5 true JP2015522280A5 (cg-RX-API-DMAC10.html) 2016-01-21
JP6366581B2 JP6366581B2 (ja) 2018-08-08

Family

ID=49882407

Family Applications (1)

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JP2015520166A Active JP6366581B2 (ja) 2012-07-06 2013-03-14 改変されたアデノ随伴ウイルスベクター組成物

Country Status (12)

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US (2) US9540659B2 (cg-RX-API-DMAC10.html)
EP (1) EP2870237B1 (cg-RX-API-DMAC10.html)
JP (1) JP6366581B2 (cg-RX-API-DMAC10.html)
CN (1) CN104619832B (cg-RX-API-DMAC10.html)
AU (1) AU2013287261B2 (cg-RX-API-DMAC10.html)
BR (1) BR112015000161A2 (cg-RX-API-DMAC10.html)
CA (1) CA2878401C (cg-RX-API-DMAC10.html)
ES (1) ES2703177T3 (cg-RX-API-DMAC10.html)
HK (1) HK1210214A1 (cg-RX-API-DMAC10.html)
IN (1) IN2015KN00074A (cg-RX-API-DMAC10.html)
RU (1) RU2679843C2 (cg-RX-API-DMAC10.html)
WO (1) WO2014007858A1 (cg-RX-API-DMAC10.html)

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EP3448874A4 (en) 2016-04-29 2020-04-22 Voyager Therapeutics, Inc. COMPOSITIONS FOR TREATING A DISEASE
EP3448987A4 (en) 2016-04-29 2020-05-27 Voyager Therapeutics, Inc. COMPOSITIONS FOR TREATING A DISEASE
US10584337B2 (en) 2016-05-18 2020-03-10 Voyager Therapeutics, Inc. Modulatory polynucleotides
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EP3831281B1 (en) 2016-08-30 2026-02-25 The Regents of The University of California Devices and systems for biomedical targeting and delivery
MX2019013172A (es) 2017-05-05 2020-09-07 Voyager Therapeutics Inc Composiciones y metodos para tratar la enfermedad de huntington.
EP3618839A4 (en) 2017-05-05 2021-06-09 Voyager Therapeutics, Inc. COMPOSITIONS AND METHODS OF TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
CA3070087A1 (en) 2017-07-17 2019-01-24 Voyager Therapeutics, Inc. Trajectory array guide system
MX2020003042A (es) 2017-09-29 2020-11-18 Voyager Therapeutics Inc Rescate del fenotipo neurológico central y periférico de la ataxia de friedreich mediante administración intravenosa.
WO2019079242A1 (en) 2017-10-16 2019-04-25 Voyager Therapeutics, Inc. TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
AU2018383712B2 (en) * 2017-12-11 2025-09-04 Editas Medicine, Inc. Cpf1-related methods and compositions for gene editing
WO2019152841A1 (en) 2018-02-01 2019-08-08 Homology Medicines, Inc. Adeno-associated virus compositions for pah gene transfer and methods of use thereof
AU2019215152A1 (en) 2018-02-01 2020-08-20 Homology Medicines, Inc. Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof
US11306329B2 (en) 2018-02-19 2022-04-19 City Of Hope Adeno-associated virus compositions for restoring F8 gene function and methods of use thereof
BR112020020266A2 (pt) 2018-04-03 2021-01-19 Stridebio, Inc. Vetores de vírus com evasão de anticorpos
CA3095179A1 (en) 2018-04-03 2019-10-10 Stridebio, Inc. Antibody-evading virus vectors
MX2020010465A (es) 2018-04-03 2021-01-08 Vectores de virus para direccionamiento a tejidos oftalmicos.
CN112424359A (zh) 2018-05-15 2021-02-26 沃雅戈治疗公司 用于治疗帕金森氏病的组合物和方法
US20210254103A1 (en) * 2018-07-02 2021-08-19 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
US12281321B2 (en) 2018-09-28 2025-04-22 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
CN113727992A (zh) 2019-03-21 2021-11-30 斯特里迪比奥公司 重组腺相关病毒载体
MX2021013913A (es) 2019-05-14 2022-03-17 Univ Duke Composiciones y metodos para el tratamiento de enfermedades mediadas por atpasa.
WO2021011841A1 (en) * 2019-07-18 2021-01-21 Lysogene Compositions and methods for the treatment of sanfilippo disease and other disorders
CN114787180A (zh) 2019-10-17 2022-07-22 斯特里迪比奥公司 用于治疗c型尼曼-匹克病的腺相关病毒载体
MX2022004353A (es) 2019-10-17 2022-07-19 Casete de transferencia de aav.
TW202140791A (zh) 2020-01-13 2021-11-01 美商霍蒙拉奇醫藥公司 治療苯酮尿症之方法
WO2021231305A2 (en) * 2020-05-11 2021-11-18 Gordian Biotechnology, Inc. Viral delivery vehicle selection
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