HK1202049A1 - 編碼視杆細胞來源的視錐細胞活力因子的載體 - Google Patents

編碼視杆細胞來源的視錐細胞活力因子的載體

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Publication number
HK1202049A1
HK1202049A1 HK15102471.7A HK15102471A HK1202049A1 HK 1202049 A1 HK1202049 A1 HK 1202049A1 HK 15102471 A HK15102471 A HK 15102471A HK 1202049 A1 HK1202049 A1 HK 1202049A1
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HK
Hong Kong
Prior art keywords
vectors encoding
viability factor
cone viability
derived cone
encoding rod
Prior art date
Application number
HK15102471.7A
Other languages
English (en)
Inventor
Tianci Luo
Original Assignee
Wellstat Ophthalmics Corp
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Wellstat Ophthalmics Corp filed Critical Wellstat Ophthalmics Corp
Publication of HK1202049A1 publication Critical patent/HK1202049A1/zh

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HK15102471.7A 2011-10-27 2015-03-10 編碼視杆細胞來源的視錐細胞活力因子的載體 HK1202049A1 (zh)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201161552155P 2011-10-27 2011-10-27
PCT/US2012/062106 WO2013063383A2 (en) 2011-10-27 2012-10-26 Vectors encoding rod-derived cone viability factor

Publications (1)

Publication Number Publication Date
HK1202049A1 true HK1202049A1 (zh) 2015-09-18

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HK15102471.7A HK1202049A1 (zh) 2011-10-27 2015-03-10 編碼視杆細胞來源的視錐細胞活力因子的載體

Country Status (15)

Country Link
US (2) US9265813B2 (zh)
EP (1) EP2797613B1 (zh)
JP (1) JP6293664B2 (zh)
KR (1) KR102000141B1 (zh)
CN (2) CN110777124A (zh)
AU (1) AU2012321102C1 (zh)
BR (1) BR112014010091B1 (zh)
CA (1) CA2853379C (zh)
DK (1) DK2797613T3 (zh)
ES (1) ES2774779T3 (zh)
HK (1) HK1202049A1 (zh)
MX (1) MX354516B (zh)
PL (1) PL2797613T3 (zh)
RU (1) RU2664673C2 (zh)
WO (1) WO2013063383A2 (zh)

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EP2909232B1 (en) 2012-10-17 2020-03-11 Institut National de la Sante et de la Recherche Medicale (INSERM) Methods and pharmaceutical compositions for the treatment of age-related macular degeneration (amd)
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US10857240B2 (en) 2016-01-05 2020-12-08 The Trustees Of The University Of Pennsylvania Methods and compositions for treatment of ocular disorders and blinding diseases
CN106148528B (zh) * 2016-07-11 2019-10-01 赵晨 一种遗传性Usher综合征的致病突变及其检测试剂
CA3025977A1 (en) 2016-10-11 2018-04-19 Wellstat Ophthalmics Corporation Fusion protein between short form rod-derived cone viability factor and a hydrophilic peptide
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CN108504685A (zh) * 2018-03-27 2018-09-07 宜明细胞生物科技有限公司 一种利用CRISPR/Cas9系统同源重组修复IL-2RG缺陷基因的方法
BR112021009370A2 (pt) * 2018-11-14 2021-08-17 Regenxbio Inc. método de tratamento da doença de batten cln2, composição farmacêutica e kit
MA54503A (fr) * 2018-12-19 2021-10-27 Versameb Ag Arn codant pour une protéine
US20220332780A1 (en) 2019-09-10 2022-10-20 Obsidian Therapeutics, Inc. Ca2-il15 fusion proteins for tunable regulation
EP4268895A3 (en) * 2019-12-09 2024-01-10 Chigenovo Co., Ltd. Uses of cyp4v2 and rdcvf in preparation of drugs
CN111733174B (zh) * 2020-08-07 2021-02-09 北京大学第三医院（北京大学第三临床医学院） 一种分离的核酸分子及其用途
WO2024206928A1 (en) 2023-03-30 2024-10-03 Pharma Cinq, Llc VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IgK SIGNAL SEQUENCE

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WO2013063383A3 (en) 2013-06-20
ES2774779T3 (es) 2020-07-22
KR102000141B1 (ko) 2019-07-15
MX2014004949A (es) 2014-09-12
CA2853379A1 (en) 2013-05-02
CN104321069A (zh) 2015-01-28
DK2797613T3 (da) 2020-03-02
BR112014010091B1 (pt) 2022-11-08
CN110777124A (zh) 2020-02-11
US9265813B2 (en) 2016-02-23
JP6293664B2 (ja) 2018-03-14
WO2013063383A2 (en) 2013-05-02
AU2012321102B2 (en) 2016-07-14
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EP2797613B1 (en) 2019-12-04
EP2797613A2 (en) 2014-11-05
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BR112014010091A2 (pt) 2020-10-27
CA2853379C (en) 2020-11-24
KR20140092320A (ko) 2014-07-23
JP2015501156A (ja) 2015-01-15
MX354516B (es) 2018-03-08
US10040835B2 (en) 2018-08-07
US20160108099A1 (en) 2016-04-21
RU2664673C2 (ru) 2018-08-21
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US20140328821A1 (en) 2014-11-06
AU2012321102A1 (en) 2013-05-16

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