EA023938B1 - Вектор гена - Google Patents
Вектор гена Download PDFInfo
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- EA023938B1 EA023938B1 EA201171335A EA201171335A EA023938B1 EA 023938 B1 EA023938 B1 EA 023938B1 EA 201171335 A EA201171335 A EA 201171335A EA 201171335 A EA201171335 A EA 201171335A EA 023938 B1 EA023938 B1 EA 023938B1
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- cell
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- mirna
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| RU2749971C2 (ru) * | 2016-09-22 | 2021-06-21 | Юниверсити Оф Массачусетс | Средство лечения болезни гентингтона на основе aav |
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| WO2011143653A2 (en) | 2010-05-14 | 2011-11-17 | Oregon Health & Science University | Recombinant hcmv and rhcmv vectors and uses thereof |
| CA2804791C (en) * | 2010-07-08 | 2019-07-30 | Duke University | Direct reprogramming of cells to cardiac myocyte fate |
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| WO2013176772A1 (en) | 2012-05-25 | 2013-11-28 | The Regents Of The University Of California | Methods and compositions for rna-directed target dna modification and for rna-directed modulation of transcription |
| EP2872154B1 (en) | 2012-07-11 | 2017-05-31 | Sangamo BioSciences, Inc. | Methods and compositions for delivery of biologics |
| LT3138910T (lt) | 2012-12-06 | 2017-11-10 | Sigma-Aldrich Co. Llc | Crispr pagrįstas genomo modifikavimas ir reguliavimas |
| SI2956477T2 (sl) | 2013-02-15 | 2024-05-31 | Bioverativ Therapeutics Inc. | Optimiran gen dejavnika VIII |
| NZ712727A (en) | 2013-03-14 | 2017-05-26 | Caribou Biosciences Inc | Compositions and methods of nucleic acid-targeting nucleic acids |
| SG11201603166UA (en) | 2013-10-24 | 2016-05-30 | Ospedale San Raffaele Srl | Method |
| US11008561B2 (en) | 2014-06-30 | 2021-05-18 | Bioverativ Therapeutics Inc. | Optimized factor IX gene |
| EP3318630B1 (en) * | 2015-04-22 | 2020-11-04 | iPS Academia Japan, Inc. | Method for sorting tissue cells |
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| US10188750B1 (en) | 2015-10-23 | 2019-01-29 | University Of South Florida | Self-replicating cell selective gene delivery compositions, methods, and uses thereof |
| PT3411478T (pt) | 2016-02-01 | 2022-09-13 | Bioverativ Therapeutics Inc | Genes do fator viii otimizados |
| GB201612214D0 (en) | 2016-07-14 | 2016-08-31 | Univ Oxford Innovation Ltd | Method |
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| CN106566838B (zh) * | 2016-11-14 | 2019-11-01 | 上海伯豪生物技术有限公司 | 一种基于CRISPR-Cas9技术的miR-126全长基因敲除试剂盒及其应用 |
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| IT201700086403A1 (it) * | 2017-07-27 | 2019-01-27 | Univ Del Piemonte Orientale | Endothelial-specific promoter sequences and uses thereof |
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| AU2022332276A1 (en) | 2021-08-23 | 2024-04-04 | Bioverativ Therapeutics Inc. | Optimized factor viii genes |
| JP2024534123A (ja) | 2021-08-23 | 2024-09-18 | バイオベラティブ セラピューティクス インコーポレイテッド | バキュロウイルス発現システム |
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| KR20240067122A (ko) | 2021-09-30 | 2024-05-16 | 바이오버라티브 테라퓨틱스 인크. | 감소된 면역원성을 갖는 인자 viii 폴리펩타이드를 암호화하는 핵산 |
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| US11046957B2 (en) | 2016-09-22 | 2021-06-29 | University Of Massachusetts | AAV treatment of Huntington's disease |
| US11773392B2 (en) | 2016-09-22 | 2023-10-03 | University Of Massachusetts | AAV treatment of Huntington's disease |
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