CN117821458A - 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物 - Google Patents

用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物 Download PDF

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CN117821458A
CN117821458A CN202311860322.9A CN202311860322A CN117821458A CN 117821458 A CN117821458 A CN 117821458A CN 202311860322 A CN202311860322 A CN 202311860322A CN 117821458 A CN117821458 A CN 117821458A
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certain embodiments
cas9
nucleotides
complementary
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J·L·戈里
L·A·巴雷拉
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Editas Medicine Inc
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Editas Medicine Inc
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CN202311860322.9A 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物 Pending CN117821458A (zh)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201662308190P 2016-03-14 2016-03-14
US62/308,190 2016-03-14
US201762456615P 2017-02-08 2017-02-08
US62/456,615 2017-02-08
CN201780029929.9A CN109153994A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
PCT/US2017/022377 WO2017160890A1 (en) 2016-03-14 2017-03-14 Crispr/cas-related methods and compositions for treating beta hemoglobinopathies

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CN201780029929.9A Division CN109153994A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物

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CN117821458A true CN117821458A (zh) 2024-04-05

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CN202311860322.9A Pending CN117821458A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
CN202311860310.6A Pending CN117802102A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
CN202311860300.2A Pending CN118127006A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
CN201780029929.9A Pending CN109153994A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物

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CN202311860310.6A Pending CN117802102A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
CN202311860300.2A Pending CN118127006A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物
CN201780029929.9A Pending CN109153994A (zh) 2016-03-14 2017-03-14 用于治疗β-血红蛋白病的CRISPR/CAS相关方法和组合物

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US (2) US20200255857A1 (enExample)
EP (1) EP3430142A1 (enExample)
JP (2) JP2019508051A (enExample)
KR (2) KR102532663B1 (enExample)
CN (4) CN117821458A (enExample)
AU (2) AU2017235333B2 (enExample)
CA (1) CA3017956A1 (enExample)
IL (2) IL261714B2 (enExample)
MX (2) MX2018011114A (enExample)
SG (1) SG11201807859WA (enExample)
WO (1) WO2017160890A1 (enExample)

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