CN111356763B - 变体RNAi - Google Patents

变体RNAi Download PDF

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Publication number
CN111356763B
CN111356763B CN201880073881.6A CN201880073881A CN111356763B CN 111356763 B CN111356763 B CN 111356763B CN 201880073881 A CN201880073881 A CN 201880073881A CN 111356763 B CN111356763 B CN 111356763B
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vector
nucleic acid
aav
promoter
recombinant
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CN111356763A (zh
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C·R·奥里奥丹
A·巴勒莫
B·理查兹
L·M·斯坦尼克
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Genzyme Corp
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CN201880073881.6A 2017-09-22 2018-09-21 变体RNAi Active CN111356763B (zh)

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Application Number Priority Date Filing Date Title
US201762561843P 2017-09-22 2017-09-22
US62/561,843 2017-09-22
PCT/US2018/052221 WO2019060726A1 (en) 2017-09-22 2018-09-21 Variant rnai

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CN111356763A CN111356763A (zh) 2020-06-30
CN111356763B true CN111356763B (zh) 2024-03-12

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EP (1) EP3684932A1 (https=)
JP (1) JP7248658B2 (https=)
KR (1) KR102686857B1 (https=)
CN (1) CN111356763B (https=)
AR (1) AR113134A1 (https=)
AU (2) AU2018335410B2 (https=)
BR (1) BR112020005569A2 (https=)
CA (1) CA3076191A1 (https=)
CO (1) CO2020003187A2 (https=)
IL (1) IL273394B2 (https=)
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TW (1) TWI902656B (https=)
UY (1) UY37897A (https=)
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JP2020518259A (ja) 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． ハンチントン病治療組成物および方法
CN111356763B (zh) 2017-09-22 2024-03-12 建新公司 变体RNAi
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JP2020535803A (ja) 2020-12-10
AU2018335410A1 (en) 2020-05-07
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US12331296B2 (en) 2025-06-17
AR113134A1 (es) 2020-01-29
US20230392149A1 (en) 2023-12-07
CO2020003187A2 (es) 2020-04-13
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