CN108463211B - 用于治疗肌联蛋白类肌病和其它肌联蛋白病变的材料和方法 - Google Patents

用于治疗肌联蛋白类肌病和其它肌联蛋白病变的材料和方法 Download PDF

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CN108463211B
CN108463211B CN201680078207.8A CN201680078207A CN108463211B CN 108463211 B CN108463211 B CN 108463211B CN 201680078207 A CN201680078207 A CN 201680078207A CN 108463211 B CN108463211 B CN 108463211B
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titin
nucleic acid
gene
dna
sequence
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CN108463211A (zh
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L·罗迪诺-卡拉巴
R·波特
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Nationwide Childrens Hospital Inc
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CN201680078207.8A 2015-11-16 2016-11-15 用于治疗肌联蛋白类肌病和其它肌联蛋白病变的材料和方法 Active CN108463211B (zh)

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US201562255887P 2015-11-16 2015-11-16
US62/255,887 2015-11-16
PCT/US2016/062052 WO2017087395A1 (en) 2015-11-16 2016-11-15 Materials and methods for treatment of titin-based myopathies and other titinopaties

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CN (1) CN108463211B (https=)
AU (1) AU2016358172B2 (https=)
CA (1) CA3005633C (https=)
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